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Lapaquistat

Phase 3

Dyslipidemia | Small molecule | Metabolic |Takeda Pharmaceutical Company Limited|Last Updated: May 24, 2012

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindACTIVE_CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment2,491
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00143663Effect of Lapaquistat Acetate on Blood Cholesterol Levels in Subjects With Elevated CholesterolPHASE3 COMPLETED 361Sep 1, 2005Apr 1, 2006May 24, 201247 United States
NCT00487994Safety and Efficacy of Lapaquistat Acetate Taken Alone and With Atorvastatin in Subjects With Primary DyslipidemiaPHASE3 COMPLETED 2,130Nov 1, 2004May 1, 2007May 24, 2012128 United States, Argentina +15
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Study Endpoints
Primary Endpoints
Change from Baseline in Low-Density Lipoprotein cholesterol
Week 12 or Final Visit
Lens Opacity Classification System findings
Weeks 24, 48, 72, and 96 or Final Visit
Best corrected visual acuity
Weeks 24, 48, 72, and 96 or Final Visit
Adverse Events
Weeks 4, 8, 12, 24, 36, 48, 60, 72, 84, 96 or Final Visit
Clinical Laboratory Tests
Weeks 4, 8, 12, 24, 36, 48, 60, 72, 84, 96 or Final Visit
Vital signs (blood pressure and pulse rate) and weight
Weeks 4, 8, 12, 24, 36, 48, 60, 72, 84, 96 or Final Visit
12-lead Electrocardiogram
Weeks 48 and 96 or Final Visit
Physical Examination
Weeks 48 and 96 or Final Visit
Secondary Endpoints
Change from Baseline in Calculated Low-Density Lipoprotein cholesterol
Week 12 or Final Visit
Change from Baseline in High-Density Lipoprotein cholesterol
Week 12 or Final Visit
Change from Baseline in the ratio of Low-Density Lipoprotein cholesterol/ High-Density Lipoprotein cholesterol
Week 12 or Final Visit
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Lapaquistat Acetate 100 mg QDEXPERIMENTAL -
Placebo QDPLACEBO_COMPARATOR -
Lapaquistat Acetate 100 mg QD + Atorvastatin 10 mg QDEXPERIMENTAL -
Atorvastatin 10 mg QDACTIVE_COMPARATOR -
Interventions
NameTypeDescription
Lapaquistat AcetateDRUGLapaquistat acetate 100 mg, tablets, orally, once daily for up to 12 weeks
PlaceboDRUGLapaquistat acetate placebo-matching tablets, orally, once daily for up to 12 weeks
Lapaquistat acetate and atorvastatinDRUGLapaquistat acetate 100 mg, tablets, orally, once daily and Atorvastatin 10 mg, capsules, orally, once daily for up to 96 weeks.
AtorvastatinDRUGLapaquistat acetate placebo-matching tablets, orally, once daily and Atorvastatin 10 mg, capsules, orally, once daily for up to 96 weeks.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites47

Inclusion Criteria: * Female participants of childbearing potential cannot be been pregnant, lactating and are not planning on becoming pregnant and agrees to use acceptable forms of contraception throughout the course of this study. * Must have a mean low-density lipoprotein cholesterol values bet...

Countries:United StatesArgentinaChileCzechiaEstoniaGermanyHungaryLatviaLithuaniaMexicoNetherlandsPeruPolandRussiaSlovakiaSouth AfricaUnited Kingdom
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