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Lepodisiran

Phase 3

Atherosclerosis | Small molecule | Cardiovascular |Eli Lilly and Company|Last Updated: Aug 24, 2026

Target and mechanism

Target class-Siran (Sirna)
ModalitySmall molecule

Also known as Lepodisiran Sodium

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment252

FDA Designations

No designations recorded

Clinical trial landscape

Lepodisiran · 3 trials · 7 indications

Phase 3 2Phase 1 1
NCT07613294A Study to See if Lepodisiran Can Reduce Plaque in Coronary Arteries of Adults With Elevated Lp(a) Who Have Had Heart Events or Are at High RiskAtherosclerosis
RECRUITING252 Analytics
NCT06292013A Study to Investigate the Effect of Lepodisiran on the Reduction of Major Adverse Cardiovascular Events in Adults With Elevated Lipoprotein(a) - ACCLAIM-Lp(a)Atherosclerotic Cardiovascular Disease (ASCVD)
ACTIVE NOT_RECRUITING17,300 Analytics
PHASE3RECRUITING
A Study to See if Lepodisiran Can Reduce Plaque in Coronary Arteries of Adults With Elevated Lp(a) Who Have Had Heart Events or Are at High Risk
AtherosclerosisUnlock trial analytics
PHASE3ACTIVE NOT_RECRUITING
A Study to Investigate the Effect of Lepodisiran on the Reduction of Major Adverse Cardiovascular Events in Adults With Elevated Lipoprotein(a) - ACCLAIM-Lp(a)
Atherosclerotic Cardiovascular Disease (ASCVD)Unlock trial analytics

Study Endpoints

Primary Endpoints

Percent Change from Baseline in Noncalcified Plaque (NCP) Volume
Baseline, Week 104
Time to First Occurrence of Any Component of the Major Adverse Cardiac Event (MACE)-4 Composite Endpoint
Baseline up to End of Study (About 4.5 Years)

Time to first event in a MACE-4 composite endpoint, comprised of cardiovascular death, nonfatal myocardial infarction, nonfatal ischemic stroke, and urgent coronary revascularization.

Pharmacokinetics (PK): Area Under the Concentration Versus Time Curve (AUC) of Lepodisiran
Baseline Up to 9 weeks

PK: AUC of Lepodisiran

PK: Maximum Concentration (Cmax) of Lepodisiran
Baseline Up to 9 weeks

PK: Cmax of Lepodisiran

Secondary Endpoints

Percent Change from Baseline in Mean Fat Attenuation Index (FAI) Score
Baseline, Week 104
Percent Change from Baseline in Lp(a) Level
Baseline through Week 104
Percentage of Participants Reporting Strongly Agree or Agree on the Subcutaneous Administration Assessment Questionnaire (SQAAQ) Version 3.0 Items
Week 26, Week 78
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
LepodisiranEXPERIMENTALParticipants will receive lepodisiran subcutaneously (SC)
PlaceboPLACEBO_COMPARATORParticipants will receive placebo SC
Lepodisiran SodiumEXPERIMENTALLepodisiran sodium administered subcutaneously (SC).
Lepodisiran Group 1EXPERIMENTALLepodisiran administered subcutaneously (SC)
Lepodisiran Group 2EXPERIMENTALLepodisiran administered SC
Lepodisiran Group 3EXPERIMENTALLepodisiran administered SC
Lepodisiran Group 4EXPERIMENTALLepodisiran administered SC

Interventions

NameTypeDescription
LepodisiranDRUGAdministered SC
PlaceboDRUGAdministered SC
Lepodisiran SodiumDRUGAdministered SC
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Eligibility Criteria

Age Range45 Years to 80 Years
SexALL
Healthy VolunteersNo
Study Sites58

Inclusion Criteria: * Have an Lp(a) ≥175 nmol/L * Have established cardiovascular (CV) disease or are at risk for a first CV event * Have angiographic evidence of coronary artery disease on screening CCTA * If taking lipid-lowering medications, inclusive of statins or prescription strength niacin a...

Countries:United StatesAustraliaCzechiaHungaryNetherlandsSpainUnited KingdomArgentinaAustriaBelgiumBrazilCanadaChinaDenmarkFranceGermanyGreeceIndiaIsraelItalyJapanMexicoPolandPuerto RicoRomaniaSlovakiaSouth KoreaTaiwan
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Recent Changes (Last 90 Days)

LOWAug 24, 2026NCT06292013lastUpdatePostDate: changed
LOWAug 24, 2026NCT06292013lastUpdatePostDate: changed
LOWAug 21, 2026NCT07613294lastUpdatePostDate: changed
LOWAug 21, 2026NCT07613294lastUpdatePostDate: changed
HIGHAug 20, 2026NCT06916078Status: ACTIVE_NOT_RECRUITING → COMPLETED
HIGHAug 20, 2026NCT06916078Status: ACTIVE_NOT_RECRUITING → COMPLETED
HIGHAug 20, 2026NCT06916078Status: ACTIVE_NOT_RECRUITING → COMPLETED
HIGHAug 20, 2026NCT06916078Status: ACTIVE_NOT_RECRUITING → COMPLETED
LOWAug 7, 2026NCT07613294lastUpdatePostDate: changed
LOWAug 7, 2026NCT07613294lastUpdatePostDate: changed
MEDIUMJul 28, 2026NCT07613294primaryCompletionDate: changed
MEDIUMJul 28, 2026NCT07613294primaryCompletionDate: changed
LOWJul 20, 2026NCT06292013lastUpdatePostDate: changed
LOWJul 20, 2026NCT06292013lastUpdatePostDate: changed
LOWJul 17, 2026NCT07613294startDate: changed
LOWJul 17, 2026NCT07613294startDate: changed
LOWJun 29, 2026NCT07613294lastUpdatePostDate: changed
LOWJun 29, 2026NCT07613294lastUpdatePostDate: changed
LOWJun 18, 2026NCT07613294Status: NOT_YET_RECRUITING → RECRUITING
LOWJun 18, 2026NCT06292013lastUpdatePostDate: changed

Frequently asked questions about Lepodisiran

What is Lepodisiran used for?

Lepodisiran is an investigational small molecule being studied for cardiovascular conditions including atherosclerotic cardiovascular disease (ASCVD), atherosclerosis, and elevated lipoprotein(a). It is also being evaluated in a liver function study. The drug is in Phase 3 clinical development and is not yet approved by regulatory authorities.

What does Lepodisiran target?

Lepodisiran is a small interfering RNA (siRNA) agent, as indicated by its '-siran' suffix. It is designed to target and reduce elevated lipoprotein(a) levels, which are associated with increased cardiovascular risk. The drug is being investigated for its potential to lower Lp(a) and reduce major adverse cardiovascular events.

Who makes Lepodisiran?

Lepodisiran is being developed by Eli Lilly and Company, a pharmaceutical company traded on the New York Stock Exchange under the ticker symbol LLY. The company is conducting clinical trials to evaluate the drug's safety and efficacy for cardiovascular indications.

What phase is Lepodisiran in?

Lepodisiran is currently in Phase 3 clinical development. It is being studied in two Phase 3 trials, including the ACCLAIM-Lp(a) trial and a coronary plaque reduction study. The drug is investigational and has not received FDA approval.

What clinical trials is Lepodisiran in?

Lepodisiran is being evaluated in three clinical trials. The Phase 3 ACCLAIM-Lp(a) trial (NCT06292013) enrolls 17,300 adults with ASCVD and elevated Lp(a). A second Phase 3 trial (NCT07613294) studies plaque reduction in 252 adults. A completed Phase 1 trial (NCT06916078) assessed liver function effects.

Is Lepodisiran the same as Lepodisiran Sodium?

Yes, Lepodisiran is also known as Lepodisiran Sodium. Both names refer to the same investigational drug being developed by Eli Lilly and Company for cardiovascular conditions associated with elevated lipoprotein(a).