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SAR113945

Phase 1

Osteoarthritis | Small molecule | Musculoskeletal |Sanofi|Last Updated: Mar 23, 2011

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment40
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01113333Safety, Tolerability and Pharmacokinetics of SAR113945 Following Intra-articular Administration in Patients With Knee OsteoarthritisPHASE1 COMPLETED 40Apr 1, 2010Feb 1, 2011Mar 23, 20111 Germany
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Study Endpoints
Primary Endpoints
Standard safety investigations (Physical examinations, 12 lead ECGs, vital signs (Blood pressure, heart rate, body temperature) and laboratory tests (hematology/coagulation, biochemistry, quantitative urinalysis))
4 weeks up to a maximum of 12 weeks
Examination of skin/soft tissue of injected knee
4 weeks up to a maximum of 12 weeks

Any reaction is classified as erythema, oedema, pain, papulae, haematoma and graded none, mild, moderate or severe.

Examination of knee joint of injected knee
4 weeks up to a maximum of 12 weeks

Any reaction is classified as effusion/worsening of effusion, warm and pain.

Secondary Endpoints
Pharmacokinetic parameters for SAR113945 and potential metabolites(s) from plasma concentration (i.e. AUC, Cmax, tmax, t1/2)
4 weeks up to a maximum of 16 weeks
Pharmacodynamic parameters (WOMAC Index, biomarkers relating to inflammation and cartilage/bone turnover)
4 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
SAR113945EXPERIMENTALSAR113945, single dose according to dose escalation design
PlaceboPLACEBO_COMPARATOR0.9% saline solution, single dose
Interventions
NameTypeDescription
placeboDRUGPharmaceutical form:injection Route of administration: intra-articular
SAR113945DRUGPharmaceutical form:injection Route of administration: intra-articular
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Eligibility Criteria
Age Range40 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion criteria: * Male patients or female patients of non child-bearing potential, aged at least 40 years with primary knee osteoarthritis having: * X-ray or Magnetic Resonance Imaging (MRI) evidence for Kellgren Lawrence Grades II./III joint space narrowing and osteophyte formation, * Wes...

Countries:Germany
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