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Verteporfin photodynamic therapy

Phase 3

Macular Degeneration | Small molecule | Ophthalmology |Novartis AG|Last Updated: Mar 31, 2016

Success Probability

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLED
Total Trials2
Total Enrollment432

FDA Designations

No designations recorded

Clinical trial landscape

Verteporfin photodynamic therapy · 2 trials · 2 indications

Phase 3 2
NCT00436553Efficacy/Safety of Verteporfin Photodynamic Therapy and Ranibizumab Compared With Ranibizumab in Patients With Subfoveal Choroidal NeovascularizationMacular Degeneration
COMPLETED321 Analytics
NCT00242580A Safety and Efficacy Study Comparing the Combination Treatments of Verteporfin Therapy Plus One of Two Different Doses of Intravitreal Triamcinolone Acetonide and the Verteporfin Therapy Plus Intravitreal PegaptanibMacular Degeneration
COMPLETED111 Analytics
PHASE3COMPLETED
Efficacy/Safety of Verteporfin Photodynamic Therapy and Ranibizumab Compared With Ranibizumab in Patients With Subfoveal Choroidal Neovascularization
Macular DegenerationUnlock trial analytics
PHASE3COMPLETED
A Safety and Efficacy Study Comparing the Combination Treatments of Verteporfin Therapy Plus One of Two Different Doses of Intravitreal Triamcinolone Acetonide and the Verteporfin Therapy Plus Intravitreal Pegaptanib
Macular DegenerationUnlock trial analytics

Study Endpoints

Primary Endpoints

Mean Change From Baseline in Best-corrected Visual Acuity (BCVA) of the Study Eye at Month 12
Baseline and Month 12

BCVA score was based on the number of letters read correctly on the Early Treatment Diabetic Retinopathy Study (ETDRS) visual acuity chart assessed at a starting distance of 4 meters. An ETDRS visual acuity score of 85 is approximately 20/20. An increase in the VA score indicates improvement in visual acuity.

Percent of Patients With a Treatment-free Interval of at Least 3 Months Following the Month 2 Visit
Month 2 up to Month 11

The number of patients with a ranibizumab treatment-free interval, ie, no active ranibizumab treatments for at least 3 months duration (at least 2 consecutive monthly visits), anytime following the Month 2 ranibizumab treatment. Only active ranibizumab treatments were considered.

Percentage of Participants Who Lose Less Than 15 Letters of Best Corrected Visual Acuity (BCVA) at 12 Months From Baseline.
Baseline to Month 12

BCVA score was based on the number of letters read correctly on the Early Treatment Diabetic Retinopathy Study (ETDRS) visual acuity chart assessed at a starting distance of 4 meters. An ETDRS visual acuity score of 85 is approximately 20/20. A decrease in score indicates worsening of vision. This outcome assessed the percentage of participants who lost less than 15 letters of visual acuity at 12 months as compared with baseline.

Secondary Endpoints

Change From Baseline in Total Area of Leakage of the Study Eye at Month 12
Baseline and Month 12
Percentage of Patients With Fluorescein Leakage in the Study Eye at Month 12
Month 12
Change From Baseline in Central Retinal Thickness at Month 12
Baseline and Month 12
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Verteporfin With Standard Fluence Rate Plus RanibizumabEXPERIMENTALPatients received three consecutive monthly ranibizumab injections on Day 1 and at Months 1 and 2, and thereafter as needed at intervals of at least 30 days based on retreatment criteria. These patients also received verteporfin photodynamic therapy (PDT) with standard fluence (SF) rate on Day 1 and then as needed from Month 3 at intervals of at least 90 days based on the retreatment criteria. From month 3 onward, retreatments were determined based on study-specific retreatment criteria that included retinal thickness by Optical Coherence Tomography (OCT), sub-retinal hemorrhage evaluated by ophthalmoscopic examination, visual acuity assessed using Early treatment Diabetic Retinopathy Study (ETDRS) visual acuity chart and choroidal neovascularization (CNV) leakage assessed by fluorescein angiography (FA). Patients received sham intravitreal injections for the first 12 months if retreatment with ranibizumab was not warranted based on the retreatment criteria.
Ranibizumab MonotherapyACTIVE_COMPARATORPatients received monthly ranibizumab injections for 12 months and thereafter as needed based on the retreatment criteria. These patients were also administered verteporfin placebo infusion with sham PDT on Day 1 and then as needed from Month 3 at intervals of at least 90 days based on the retreatment criteria. Retreatments were determined based on study specific retreatment criteria that included retinal thickness by Optical Coherence Tomography (OCT), sub-retinal hemorrhage evaluated by ophthalmoscopic examination, visual acuity assessed using Early treatment Diabetic Retinopathy Study (ETDRS) visual acuity chart and choroidal neovascularization (CNV) leakage assessed by fluorescein angiography (FA).
Verteporfin With Reduced Fluence Rate Plus RanibizumabEXPERIMENTALPatients received three consecutive monthly ranibizumab injections on Day 1 and at Months 1 and 2, and thereafter as needed at intervals of at least 30 days based on retreatment criteria. These patients also received verteporfin PDT with reduced fluence (RF) rate on Day 1 and then as needed from Month 3 at intervals of at least 90 days based on the retreatment criteria. From month 3 onward, retreatments were determined based on study-specific retreatment criteria that included retinal thickness by Optical Coherence Tomography (OCT), sub-retinal hemorrhage evaluated by ophthalmoscopic examination, visual acuity assessed using Early treatment Diabetic Retinopathy Study (ETDRS) visual acuity chart and choroidal neovascularization (CNV) leakage assessed by fluorescein angiography (FA). Patients received sham intravitreal injections for the first 12 months if retreatment with ranibizumab was not warranted based on the retreatment criteria.
Verteporfin and Triamcinolone 1 mgEXPERIMENTALParticipants received Verteporfin photodynamic therapy and 1 mg triamcinolone acetonide intravitreal injection at the baseline visit. After the baseline visit, these participants received Verteporfin and triamcinolone acetonide 1 mg at every 3 month visit up to Month 9 only if leakage was detected on the fluorescein angiogram. At the 1.5, 4.5, 7.5 and 10.5 month follow-up visits participants received a sham injection. Starting from Month 12, if patients experienced ≥ 10 letters vision loss from the previous visit, they were treated at the investigators' discretion with available standard of care therapy.
Verteporfin and Triamcinolone 4 mgEXPERIMENTALParticipants received Verteporfin photodynamic therapy and 4 mg triamcinolone acetonide intravitreal injection at the baseline visit. After the baseline visit, these participants received Verteporfin and triamcinolone acetonide 4 mg at every 3 month visit up to Month 9 only if leakage was detected on the fluorescein angiogram. At the 1.5, 4.5, 7.5 and 10.5 month follow-up visits participants received a sham injection. Starting from Month 12, if patients experienced ≥ 10 letters vision loss from the previous visit, they were treated at the investigators' discretion with available standard of care therapy.
Verteporfin and PegaptanibACTIVE_COMPARATORParticipants received Verteporfin photodynamic therapy and 0.3 mg Pegaptanib at the baseline visit. After the baseline visit, these participants received pegaptanib every 1.5 months up until and including the 10.5 month visit. After the baseline visit, these participants also received verteporfin at every 3 month visit up to Month 9 only if leakage was detected on the fluorescein angiogram. Starting from Month 12, if participants experienced ≥ 10 letters vision loss from the previous visit, they were treated at the investigator's discretion with available standard of care therapy.

Interventions

NameTypeDescription
Verteporfin Photodynamic TherapyDRUGAfter a 10-minute intravenous infusion of verteporfin at a dose of 6 mg/m\^2 body surface area, verteporfin was activated by light application of 50 J/cm\^2 (Standard Fluence rate) or 25 J/cm\^2 (Reduced Fluence rate) to the study eye, begun 15 minutes after the start of the infusion.
RanibizumabDRUGRanibizumab 0.5 mg administered as an intravitreal injection.
Verteporfin PlaceboDRUGTo maintain masking, as a placebo for verteporfin photodynamic therapy, patients were administered a 10-minute intravenous infusion of 5% dextrose solution, followed by light application of 50 J/cm\^2 to the study eye, begun 15 minutes after the start of infusion.
Ranibizumab PlaceboDRUGTo maintain masking, patients in the combination groups received sham intravitreal injections whenever retreatment with active Ranibizumab was not warranted based on the retreatment algorithm.
PegaptanibDRUGPegaptanib sodium 0.3 mg administered by intravitreal injection.
Triamcinolone acetonideDRUGTriamcinolone acetonide administered by intravitreal injection.
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Eligibility Criteria

Age Range50 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites43

Inclusion Criteria: * Subjects of either gender age 50 years or older * Subfoveal choroidal neovascularization (CNV) due to age-related macular degeneration (AMD) Exclusion Criteria: * Choroidal neovascularization due to causes other than AMD * Prior treatment for neovascular AMD in the study eye...

Countries:United StatesCanada
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Frequently asked questions about Verteporfin photodynamic therapy

What is Verteporfin photodynamic therapy used for?

Verteporfin photodynamic therapy is used for macular degeneration, specifically for choroidal neovascularization, a condition involving abnormal blood vessel growth under the retina. It is an ophthalmology treatment being developed by Novartis AG (NVS) and is currently in Phase 3 clinical development.

What does Verteporfin photodynamic therapy target?

Verteporfin photodynamic therapy is a small molecule modality that works through photodynamic therapy, where the drug is activated by light to target abnormal blood vessels in the eye. It is being studied for the treatment of macular degeneration with choroidal neovascularization.

Who makes Verteporfin photodynamic therapy?

Verteporfin photodynamic therapy is developed by Novartis AG, a pharmaceutical company traded on the New York Stock Exchange under the ticker NVS. The therapy is currently in Phase 3 clinical trials for macular degeneration.

What phase is Verteporfin photodynamic therapy in?

Verteporfin photodynamic therapy is in Phase 3 clinical development. It is an investigational therapy for macular degeneration and is not yet approved. Two Phase 3 trials have been completed, with a total enrollment of 432 patients.

What clinical trials is Verteporfin photodynamic therapy in?

Verteporfin photodynamic therapy has two completed Phase 3 trials. NCT00242580 studied it in combination with triamcinolone acetonide or pegaptanib in 111 patients. NCT00436553 compared it with ranibizumab in 321 patients. Both trials involved patients with subfoveal choroidal neovascularization.

Is Verteporfin photodynamic therapy the same as Visudyne?

Verteporfin photodynamic therapy is a treatment that uses the drug verteporfin, which is also known by the brand name Visudyne. The therapy involves light activation of the drug to treat macular degeneration with choroidal neovascularization.