Recent Updates
Recently added Catalysts

Ixo-vec

Phase 3

Neovascular Age-Related Macular Degeneration (nAMD) | Gene therapy | Ophthalmology |Adverum Biotechnologies, Inc.|Last Updated: May 22, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
RandomizedDouble-BlindACTIVE_CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment595
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07482176Efficacy and Safety Study of Ixoberogene Soroparvovec (Ixo-vec) in Participants With Neovascular Age-related Macular Degeneration (AQUARIUS)PHASE3 RECRUITING 284Mar 16, 2026Oct 20, 2031May 20, 202646 United States
NCT06856577Efficacy and Safety Study of Ixoberogene Soroparvovec (Ixo-vec) in Participants With Neovascular Age-Related Macular DegenerationPHASE3 ACTIVE NOT_RECRUITING 311Feb 28, 2025Nov 23, 2030May 22, 202675 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Mean Change from Baseline in BCVA Based on an Average at Weeks 52 and 56
Baseline, Week 52 and Week 56

BCVA will be measured using an Early Treatment Diabetic Retinopathy Study (ETDRS) visual acuity chart.

Mean change from Baseline in Best-Corrected Visual Acuity (BCVA) based on an average at Weeks 52 and 56
Baseline, Week 52 and Week 56

BCVA will be measured using an Early Treatment Diabetic Retinopathy Study (ETDRS) visual acuity chart.

Secondary Endpoints
Mean Number of Aflibercept IVT Injections Received
Week 4 through Week 56
Percentage of Participants with Worsened BCVA
Through Week 56
Percentage of Participants with Improved BCVA
Through Week 56
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Ixo-vecEXPERIMENTALParticipants will receive 3 monthly loading doses of aflibercept 2 mg IVT, a single IVT injection of Ixo-vec 6 x 10\^10 vg/eye at Week 1, and sham injections every 8 weeks.
AfliberceptACTIVE_COMPARATORParticipants will receive 3 monthly loading doses of aflibercept 2 mg IVT, a sham injection at Week 1, and aflibercept 2 mg IVT every 8 weeks.
Interventions
NameTypeDescription
Ixo-vecGENETICIxo-vec will be administered intravitreally.
AfliberceptDRUGAflibercept will be administered intravitreally.
Unlock Study Design Details
Eligibility Criteria
Age Range50 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites46

Inclusion Criteria: 1. Able and willing to provide informed consent (or have a legally authorized representative who is able and willing to provide informed consent) prior to any study assessments and procedures and comply with the study requirements and visits. 2. Male or female with a diagnosis o...

Countries:United States
Unlock Eligibility Criteria
Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT07482176primaryCompletionDate: changed
MEDIUMMay 26, 2026NCT06856577Status: RECRUITING → ACTIVE_NOT_RECRUITING
LOWMay 24, 2026NCT07482176studyFirstPostDate: changed
LOWMay 24, 2026NCT06856577studyFirstPostDate: changed