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sc2Wear Furosemide

Phase 3

Heart Failure | Small molecule | Cardiovascular |MannKind Corporation|Last Updated: Jun 27, 2018

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials2
Total Enrollment101
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02804282Product Design Clinical Performance Study of sc2Wear Furosemide Combination ProductPHASE3 COMPLETED 74Jul 1, 2016Nov 1, 2016Jun 27, 2018 -
NCT02804035Pilot Study for First Clinical Use of sc2Wear Furosemide Combination ProductPHASE2 COMPLETED 27Jul 1, 2016Aug 1, 2016Oct 16, 2017 -
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Study Endpoints
Primary Endpoints
Absence of Major Product Failure
1-5 hours

Freedom from failures leading to infusion errors.

Secondary Endpoints
Local Pain Tolerance
1-5 hours
Local Skin Tolerance
1-8 days
Incidence of treatment-emergent Adverse Events and Serious Adverse Events
1-8 days
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
sc2Wear Furosemide Combination ProductEXPERIMENTALDrug-device combination product of buffered furosemide injection, (Furosemide Injection Solution), 8 mg/mL, and patch pump (sc2Wear Furosemide Pump) for subcutaneous administration of 80 mg dose delivered over 5 hours.
Interventions
NameTypeDescription
sc2Wear FurosemideCOMBINATION_PRODUCTDrug-device combination product of buffered furosemide injection, (Furosemide Injection Solution), 8 mg/mL, and patch pump (sc2Wear Furosemide Pump)
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo

Inclusion Criteria: 1. An Institutional Review Board (IRB) approved informed consent is signed and dated prior to any study-related activities. 2. Male and female Subjects ≥18 years of age 3. New York Heart Association (NYHA) Class II-IV Heart Failure. 4. In the opinion of the Investigator, able to...

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