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VIT-2763 once a day

Phase 2

Beta-Thalassemia | Small molecule | Hematology |Labcorp Holdings Inc.|Last Updated: Dec 14, 2023

Success Probability

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment35

FDA Designations

No designations recorded

Clinical trial landscape

VIT-2763 once a day · 1 trial · 2 indications

Phase 2 1
NCT04364269Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemiaBeta-Thalassemia
COMPLETED35 Analytics
PHASE2COMPLETED
Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemia
Beta-ThalassemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants With Treatment-Emergent Adverse Events (TEAEs)
From baseline to Week 16

Please note that in this section we are presenting just the overview of the adverse events experienced by the trial participants, in particular, the number of participants with at least one TEAE. Please refer to the detailed tables included on the Adverse Event Module for specifics.

Changes in the Systolic Blood Pressure (SBP) and Diastolic Blood Pressure (DBP)
From baseline to Week 12

Summary of the values by visit from baseline and changes from baseline by post-baseline visit.

Changes in the Heart Rate
From baseline to Week 12

Summary of the values by visit from baseline and changes from baseline by post-baseline visit.

Changes in 12-lead Electrocardiogram (ECG) Parameters
From baseline to Week 12

Values by visit from baseline and changes from baseline by post-baseline visit. The following ECG parameters were recorded: PR interval, QRS duration, QT interval, RR interval and QTcF interval. PR interval represents the time from the onset of the P wave to the start of the QRS complex. QRS duration represents the time required for a stimulus to spread through the ventricles (ventricular depolarization). QT interval represents the time from the start of the Q wave to the end of the T wave. RR interval represents the time from the onset of one R wave to the onset of the next one, one complete cardiac cycle. QT corrected for heart rate (QTc) interval reflects ventricular repolarization.

Secondary Endpoints

Change From Baseline in Total Serum Iron
From baseline to Week 12
Change From Baseline in Serum Ferritin
From baseline to Week 12
Change From Baseline in Serum Transferrin
From baseline to Week 12
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
VIT-2763 Once a day (QD)EXPERIMENTALParticipants will be assigned to receive VIT-2763 once a day (QD) in a total daily dose of 60 mg or 120 mg depending on their body weight. The study medication (VIT-2763 and/or matching placebo) will be administered for all participants twice a day to maintain the blind.
VIT-2763 Twice a day (BID)EXPERIMENTALParticipants will be assigned to receive VIT-2763 Twice a day (BID) in a total daily dose of 60 mg or 120 mg depending on their body weight.
PlaceboPLACEBO_COMPARATORParticipants will be assigned to receive Placebo, Twice a day.

Interventions

NameTypeDescription
VIT-2763 once a day (QD)DRUGParticipants will receive VIT-2763 QD at a dose of 60 mg if their body weight is between 40 kg to 59 kg or at a dose of 120 mg if their body weight is between 60 kg and 100 kg, during 12 weeks.
VIT-2763 twice a day (BID)DRUGParticipants will receive VIT-2763 BID at a dose of 60 mg if their body weight is between 40 kg to 59 kg or at a dose of 120 mg if their body weight is between 60 kg and 100 kg, during 12 weeks.
PlaceboDRUGParticipants will receive hard capsules of Placebo, twice a day.
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Eligibility Criteria

Age Range12 Years to 65 Years
SexALL
Healthy VolunteersNo
Study Sites16

Inclusion Criteria: * Documented diagnosis of NTDT, including a β-thalassemia intermedia-phenotype. * NTDT is defined as subjects having received less than 5 units of red blood cells (RBCs) during the 24-week period prior to randomisation/first drug administration of VIT-2763 or placebo (Day 1; 1 u...

Countries:GreeceIsraelItalyLebanonThailand
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Frequently asked questions about VIT-2763 once a day

What is VIT-2763 used for?

VIT-2763 is an investigational small molecule being developed for the treatment of Beta-Thalassemia, a blood disorder. It is currently in Phase 2 clinical development and has been studied in patients with non-transfusion-dependent thalassemia. The drug is administered once a day.

Who makes VIT-2763?

VIT-2763 is being developed by Labcorp Holdings Inc., a company traded on the stock exchange under the ticker symbol LH. The drug is currently in Phase 2 clinical trials for the treatment of Beta-Thalassemia.

What phase is VIT-2763 in?

VIT-2763 is in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory authorities. A Phase 2 clinical trial has been completed to evaluate its safety, tolerability, and preliminary efficacy in patients with Beta-Thalassemia.

What clinical trials is VIT-2763 in?

VIT-2763 has been studied in a Phase 2 clinical trial with the identifier NCT04364269. This trial, titled 'Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemia,' has been completed. The trial enrolled 35 participants and was conducted in Greece, Israel, Italy, Lebanon, and Thailand.

Is VIT-2763 the same as VIT-2763 once a day?

Yes, VIT-2763 once a day refers to the same drug as VIT-2763. The once-a-day designation indicates the dosing frequency used in clinical studies. The drug is being developed for the treatment of Beta-Thalassemia and is currently in Phase 2 clinical development.