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Intravitreal anti-VEGF

Phase 1

Wet Age-related Macular Degeneration | Small molecule | Ophthalmology |Johnson & Johnson|Last Updated: Mar 30, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment25
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03585556AAVCAGsCD59 for the Treatment of Wet AMDPHASE1 COMPLETED 25Sep 13, 2018Jan 18, 2022Mar 30, 20252 United States
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Study Endpoints
Primary Endpoints
Number of intravitreal anti-VEGF injections
12 months

Measure the number of intravitreal anti VEGF injections from Month 1 through Month 12 following an intravitreal injection of AAVCAGsCD59 at Day 7

Secondary Endpoints
Number of patients with change in vision of ≥ 15 letters
12 months
Number of patients with inflammation, endophthalmitis, IOP>30, retinal detachment, cataract, and systemic adverse events
24 months
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
AAVCAGsCD59 Treated ArmEXPERIMENTALAn anti-VEGF injection will be given at Day 0 followed by an intravitreal injection of AAVCAGsCD59 at Day 7. All eyes will then be treated with intravitreal anti-VEGF monthly as needed based on disease activity.
Interventions
NameTypeDescription
Intravitreal anti-VEGFDRUGIntravitreal injection of anti-VEGF at Day 0 then monthly as needed
Intravitreal AAVCAGsCD59BIOLOGICALAn intravitreal injection of AAVCAGsCD59 will occur at Day 7 once
Oral prednisoloneDRUGA 7 day tapering dose of oral prednisone will be taken at Day 30 by all patients
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Eligibility Criteria
Age Range50 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites2

Inclusion Criteria: 1. Men or women 50 years of age or older. 2. Treatment naive Wet AMD with no evidence of subretinal fibrosis under the fovea. 3. Presence of intraretinal and/or subretinal fluid on OCT. 4. Best corrected visual acuity (BCVA) Snellen equivalent 20/25 to 20/400 in the study eye us...

Countries:United States
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