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PIPE-307

Phase 1

Multiple Sclerosis | Small molecule | Immunology |Contineum Therapeutics, Inc.|Last Updated: Oct 5, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment76
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04941781PET Study to Determine the Relationship Between Plasma Concentrations and Muscarinic Type 1 Receptor (M1AChR) Occupancy of PIPE-307 in Healthy VolunteersPHASE1 COMPLETED 6Sep 1, 2021Nov 10, 2021Oct 5, 20221 United Kingdom
NCT04725175Phase I Study Evaluating Safety and Tolerability of Escalating Single and Multiple Doses of of PIPE-307 and Food Effect in Healthy VolunteersPHASE1 COMPLETED 70Feb 26, 2021Sep 1, 2021Nov 3, 20211 Australia
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Study Endpoints
Primary Endpoints
M1AChR receptor occupancy as determined by regional total volume of distribution (VT) of [11C] PIPE-307 at 24 hours
24 hours
Safety: Treatment-Emergent Adverse Events (TEAE)
From baseline to 7 days post dosing for SAD cohorts and 21 days post dosing for MAD cohorts

Number of participants with TEAEs

Secondary Endpoints
Safety: Cardiac repolarization using Fridericia-corrected QT interval (QTcF)
From baseline to 14 days post dose for SAD cohorts and 21 days post last dose for MAD cohorts
Pharmacokinetics (PK): Blood concentration levels of PIPE-307
From baseline to 14 days post dose for SAD cohorts and 21 days post last dose for MAD cohorts
PK: Urine concentration levels of PIPE-307
From baseline on day 1 through day 2 for SAD cohorts, and from baseline on day 1 though day 7 for the MAD cohorts
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
PIPE-307EXPERIMENTALSubjects will receive an oral dose of PIPE-307 and 3 intravenous injections of \[11C\] PIPE- 307.
PlaceboPLACEBO_COMPARATOR -
Interventions
NameTypeDescription
PIPE-307DRUGEach dose cohort will receive a single oral dose of PIPE-307. Doses to be tested in subsequent cohorts will be determined by the analysis of the exposure from PK data and the PET scans with \[11C\] PIPE-307. Subjects will receive an intravenous dose of the radioligand \[11C\] PIPE-307 prior to PET imaging.
Placebo oral tabletDRUGSingle and multiple ascending oral doses of matching Placebo tablets
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Eligibility Criteria
Age Range25 Years — 65 Years
SexALL
Healthy VolunteersYes
Study Sites1

Key Criteria: * Normotensive male or female volunteers between 25-65 years old * Deemed healthy on the basis of a clinical history, physical examination, ECG, vital signs, and laboratory tests of blood and urine Key Exclusion Criteria: * Clinically relevant abnormal findings at the screening asse...

Countries:United KingdomAustralia
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