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CD34-positive cells

Phase 1

Peripheral Artery Disease | Monoclonal antibody | Cardiovascular |Baxter International Inc.|Last Updated: Jul 25, 2011

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment28
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00616980Injection of Autologous CD34-Positive Cells for Critical Limb IschemiaPHASE1 COMPLETED 28Dec 1, 2007Aug 1, 2010Jul 25, 201112 United States
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Study Endpoints
Primary Endpoints
Safety of Intramuscular Injection of CD34-positive cells
6 months and 1 year
Change in Rest Pain
6 months
Ulcer Healing
6 months
Functional Improvement
6 months
Limb Salvage
6 months
Secondary Endpoints
Disease Severity
6 months
Assessment of Co-morbidity
6 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Low DoseACTIVE_COMPARATOR -
High DoseACTIVE_COMPARATOR -
SalinePLACEBO_COMPARATOR -
Interventions
NameTypeDescription
CD34-positive cellsBIOLOGICAL -
Saline and 5% autologous plasmaBIOLOGICAL -
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Eligibility Criteria
Age Range21 Years — 80 Years
SexALL
Healthy VolunteersNo
Study Sites12

Inclusion Criteria: * 21-80 years of age * moderate or high-risk Critical Limb Ischemia (Rutherford Clinical Severity Score 4 or 5) * unsuitable for conventional revascularization Exclusion Criteria: * advanced CLI (Rutherford Clinical Severity Score 6) characterized by extensive tissue loss or g...

Countries:United States
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