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avutometinib

Phase 2

Low Grade Ovarian Serous Adenocarcinoma | Small molecule | Oncology |Verastem, Inc.|Last Updated: Jan 29, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDBiomarker
Total Trials1
Total Enrollment225
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04625270A Study of Avutometinib (VS-6766) v. Avutometinib (VS-6766) + Defactinib in Recurrent Low-Grade Serous Ovarian Cancer With and Without a KRAS MutationPHASE2 ACTIVE NOT_RECRUITING 225Dec 21, 2020Dec 1, 2026Jan 29, 202547 United States, Belgium +5
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Study Endpoints
Primary Endpoints
Part A: Determine optimal regimen of avutometinib (VS-6766) monotherapy or in combination with defactinib
From start of treatment to confirmation of response; 24 weeks

Confirmed overall response rate per RECIST 1.1

Part B: To determine the efficacy of the optimal regimen identified from Part A
From start of treatment to confirmation of response; 24 weeks

Confirmed overall response rate per RECIST 1.1

Part C: To evaluate additional efficacy parameters for the optimal regimen identified in Part A
From start of treatment to confirmation of response; 24 weeks

Confirmed overall response rate per RECIST 1.1

Part D:To evaluate additional efficacy parameters for a lower dose of avutometinib in combination with defactinib
From start of treatment to confirmation of response; 24 weeks

Confirmed ORR defined according to RECIST 1.1

Secondary Endpoints
Overall Response Rate as assessed by Investigator
From start of treatment to confirmation of response; 24 weeks
Duration of Response (DOR)
Time from the first documentation of response to first documentation of progressive disease or death due to any cause, greater than or equal to 6 months
Disease Control Rate (DCR)
Greater than or equal to 8 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Part AEXPERIMENTALTo determine the optimal regimen, either avutometinib(VS-6766) monotherapy or avutometinib (VS-6766) in combination with defactinib, for subsequent evaluation for efficacy in the Expansion Phase (Part B)
Part BEXPERIMENTALTo determine the efficacy of the optimal regimen identified from Part A
Part C:EXPERIMENTALTo evaluate additional efficacy parameters for the optimal regimen identified in Part A.
Part DEXPERIMENTALTo evaluate additional efficacy parameters for a lower dose of avutometinib in combination with defactinib
Interventions
NameTypeDescription
avutometinib (VS-6766)DRUGavutometinib (VS-6766) monotherapy
avutometinib (VS-6766) and defactinibDRUGavutometinib (VS-6766) and defactinib combination
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Eligibility Criteria
Age Range18 Years — N/A
SexFEMALE
Healthy VolunteersNo
Study Sites47

Inclusion Criteria: * Histologically proven LGSOC (ovarian, peritoneal) * Progression or recurrence of LGSOC after at least one prior systemic therapy for metastatic disease. * Measurable disease according to RECIST 1.1 * An Eastern Cooperative Group (ECOG) performance status ≤ 1. * Adequate organ ...

Countries:United StatesBelgiumCanadaFranceItalySpainUnited Kingdom
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT04625270primaryCompletionDate: changed
LOWMay 24, 2026NCT04625270studyFirstPostDate: changed