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CERE-120: AAV2-NTN

Phase 1

Parkinson's Disease | Gene therapy | Neurology |Sangamo Therapeutics, Inc.|Last Updated: Nov 10, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDDMC
Total Trials1
Total Enrollment12
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00252850Safety of CERE-120 (AAV2-NTN) in Subjects With Idiopathic Parkinson's DiseasePHASE1 COMPLETED 12Jun 1, 2005Mar 1, 2007Nov 10, 20222 United States
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Interventions
NameTypeDescription
CERE-120: AAV2-NTNGENETIC -
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Eligibility Criteria
Age Range35 Years — 75 Years
SexALL
Healthy VolunteersNo
Study Sites2

Inclusion Criteria: * Diagnosis of bilateral idiopathic Parkinson's Disease of at least 5 years duration since diagnosis with motor fluctuations, despite adequate oral antiparkinsonian therapy. * Diagnosis of moderate to severe Parkinson's Disease based on clinical rating scales. * Males or nonpreg...

Countries:United States
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