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Pirfenidone

Phase 2

Idiopathic Pulmonary Fibrosis | Small molecule | Respiratory |PureTech Health plc|Last Updated: Oct 15, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLED
Total Trials1
Total Enrollment240
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05321420LYT-100 in Patients With Idiopathic Pulmonary Fibrosis (IPF)PHASE2 ACTIVE NOT_RECRUITING 240Jul 1, 2022Dec 1, 2025Oct 15, 2025 -
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Study Design & Arms
Interventions
NameTypeDescription
PlaceboDRUGplacebo
PirfenidoneDRUGpirfenidone 801 mg TID
DeupirfenidoneDRUGDeupirfenidone
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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT05321420studyFirstPostDate: changed