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GEN-001

Phase 2

Gastric Cancer | Small molecule | Oncology |Merck & Company, Inc.|Last Updated: Dec 16, 2025

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment42

FDA Designations

No designations recorded

Clinical trial landscape

GEN-001 · 2 trials · 6 indications

Phase 2 1Phase 1 1
NCT05419362GEN-001 in Combination With Avelumab for Patients With PD-L1 Positive Gastric CancerGastric Cancer
COMPLETED42 Analytics
PHASE2COMPLETED
GEN-001 in Combination With Avelumab for Patients With PD-L1 Positive Gastric Cancer
Gastric CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

To assess the anti-tumor activity of GEN-001, when administered as combined with avelumab
1 years

Objective Response (OR) per Response Evaluation Criteria in Solid Tumors (RECIST) v1.1

Dose Escalation: Incidence of Adverse Events
1 years

Assessed as per CTCAE v5.0

Dose Escalation: Incidence of Laboratory abnormalities
1 years

Assessed as per CTCAE v5.0

Dose Escalation: Incidence of dose-limiting toxicity (DLT)
1 Cycle (one cycle = 28 days)

To evaluate the safety and tolerability of GEN-001 in combination with avelumab

Dose Expansion: To assess objective response (OR) of GEN-001 in patients with advanced or metastatic solid tumors, when administered as combined with avelumab.
2 years

Confirmed OR per RECIST v1.1 by the Investigator

Secondary Endpoints

Incidence of Adverse Events
1 years
Incidence of Laboratory abnormalities
1 years
Duration of response (DoR)
1 years
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
GEN-001 with avelumabEXPERIMENTAL42 patients in total with metastatic GC/Gastroesophageal Junction Adenocarcinoma who have progressed after 2 prior systemic treatments and confirmed PD-L1 positive expression will be enrolled in this study.

Interventions

NameTypeDescription
GEN-001DRUGThe capsules taken by mouth once a daily. Each capsule will contain ≥ 3x10\^11 colony-forming units (CFU)
AvelumabDRUG800 mg given by intravenous (IV) infusion once every 2 weeks
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Eligibility Criteria

Age Range19 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: * Histologically confirmed unresectable, recurrent, locally advanced or metastatic GC/Gastroesophageal Junction Adenocarcinoma * Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1 * Have adequate organ functions as defined in the protocol * Negative childbear...

Countries:South KoreaUnited States
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Competitive Landscape -Gastric Cancer 112 trials

Top 20 of 45 competitors

CompanyTickerTrialsLead PhaseDrugs
AstraZeneca PLCAZN16PHASE3AZD0901, Ramucirumab, paclitaxel, Paclitaxel, Docetaxel
BeOne Medicines Ltd. Sponsored ADRONC4PHASE3Tislelizumab, Cisplatin, Leucovorin, 5-fluorouracil, Oxaliplatin
Jazz Pharmaceuticals Public Limited CompanyJAZZ3PHASE3Zanidatamab, Tislelizumab, Trastuzumab, Capecitabine, Oxaliplatin
Arcus Biosciences, Inc.RCUS2PHASE3Domvanalimab, Zimberelimab, Capecitabine, Fluorouracil, Leucovorin
Bristol-Myers Squibb CompanyBMY6PHASE2Pumitamig, Folfox, Capox, Nivolumab
Pfizer Inc.PFE7PHASE2disitamab vedotin, tucatinib
Agenus Inc.AGEN2PHASE3Balstilimab, Botensilimab, Folfox Protocol, XELOX, Nivolumab
AbbVie, Inc.ABBV2PHASE2Telisotuzumab Adizutecan, Budigalimab, Fluorouracil, Leucovorin, Oxaliplatin
Eli Lilly and CompanyLLY2PHASE2Ramucirumab, Paclitaxel
Compass Therapeutics, Inc.CMPX1PHASE2CTX-009, Paclitaxel
ALX Oncology Holdings, Inc.ALXO1PHASE2Evorpacept, Trastuzumab, Ramucirumab, Paclitaxel
GE Healthcare Technologies Inc.GEHC1PHASE2GEH300079 Positron-Emission Tomography/Computed Tomography
ImmunityBio IncIBRX1PHASE2N-803, Pembrolizumab
Apollomics Inc. Class AAPLM1PHASE2APL-101
Exelixis, Inc.EXEL2PHASE1cabozantinib, atezolizumab
Tango Therapeutics, Inc.TNGX2PHASE2Trifluridine/Tipiracil, Oxaliplatin, FOLFOX regimen, Nivolumab
Inhibrx Biosciences, Inc.INBX1PHASE1INBRX-106- Hexavalent OX40 agonist antibody, pembrolizumab, Carboplatin AUC-5, Pemetrexed/m2, Cisplatin/m2
Incyte CorporationINCY1PHASE2Capecitabine, Oxaliplatin, Retifanlimab
I-Mab Biopharma US LimitedIMAB2PHASE2Givastomig, Nivolumab, 5Fluorouracil, Leucovorin, Oxaliplatin
Enliven Therapeutics, Inc.ELVN1PHASE1ELVN-002, Trastuzumab, 5-Fluorouracil, Oxaliplatin, Capecitabine
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Frequently asked questions about GEN-001

What is GEN-001 used for?

GEN-001 is an investigational live biotherapeutic product being studied in oncology. It is being evaluated in combination with avelumab for patients with solid tumors who have progressed on anti-PD-(L)1 therapy, and for patients with PD-L1 positive gastric cancer and gastroesophageal junction adenocarcinoma.

Who is developing GEN-001?

GEN-001 is being developed by Merck & Company, Inc., which trades under the ticker MRK. The drug is a small molecule modality in the oncology therapeutic area.

What phase is GEN-001 in?

GEN-001 is in Phase 2 clinical development. It has completed a Phase 1 trial and a Phase 2 trial, both of which are listed as completed. The drug remains investigational and has not been approved.

What clinical trials is GEN-001 in?

GEN-001 has been studied in two completed trials. NCT04601402 was a Phase 1 study of GEN-001 with avelumab in solid tumors, non small cell lung cancer, squamous cell carcinoma of the head and neck, and urothelial carcinoma. NCT05419362 was a Phase 2 study in gastric cancer and gastroesophageal junction adenocarcinoma.

Is GEN-001 being studied in biomarker-selected patients?

Yes, GEN-001 is being studied in biomarker-selected patients. The Phase 2 trial NCT05419362 enrolled patients with PD-L1 positive gastric cancer, indicating that biomarker selection is part of the development strategy.

What is the enrollment status of GEN-001 trials?

GEN-001 has completed two clinical trials with a total enrollment of 42 patients across both studies. The Phase 1 trial enrolled 11 patients, and the Phase 2 trial enrolled 42 patients. Both trials were uncontrolled and not randomized or double-blinded.