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Paliperidone IR

Phase 1

Schizophrenia | Small molecule | Psychiatry |Johnson & Johnson|Last Updated: Sep 18, 2017

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDBiomarker
Total Trials1
Total Enrollment328
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01559272A Study to Assess the Pharmacokinetics, Safety, and Tolerability of Paliperidone Palmitate in Patients With SchizophreniaPHASE1 COMPLETED 328Feb 21, 2008May 24, 2014Sep 18, 201736 United States, Belgium +9
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Study Endpoints
Primary Endpoints
Plasma concentration of Paliperidone (Period 1)
14 time points over 96 hours
Plasma concentration of Paliperidone (Period 2)
29 time points over 544 days
Secondary Endpoints
The change from baseline in Positive and Negative Syndrome Scale for Schizophrenia (PANSS) (Period 1)
Baseline and 96 hours
Changes in Positive and Negative Syndrome Scale for Schizophrenia (PANSS) observed across multiple time points between baseline and 544 days (Period 2)
Baseline and 544 days
The change from baseline in Clinical Global Impression (CGI-S) (Period 1)
Baseline and 96 hours
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Panel AEXPERIMENTALPanel A consists of 2 treatment groups
Panel BEXPERIMENTALPanel B consists of 5 treatment groups
Panel CEXPERIMENTALPanel C consists of 1 treatment group
Panel DEXPERIMENTALPanel D consists of 4 treatment groups
Interventions
NameTypeDescription
Paliperidone IR (Period 1)DRUGType= exact number, unit= mg, number=1, form= injection, route= intramuscular use. Single injection with 1 mg paliperidone IR in the gluteal or deltoid muscle.
Paliperidone palmitate F015 (Panel A: treatment group 1)DRUGType= exact number, unit= mg, number=300, form= injection, route= intramuscular use. Single injection with 300 mg eq. 3-month formulation paliperidone palmitate F015 manufactured by milling technique A, in the gluteal muscle.
Paliperidone palmitate F015 (Panel A: treatment group 2)DRUGType= exact number, unit= mg, number=300, form= injection, route= intramuscular use. Single injection with 300 mg eq. 3-month formulation paliperidone palmitate F015 manufactured by milling technique B, in the gluteal muscle.
Paliperidone palmitate F015 (Panel B: treatment group 1)DRUGType= exact number, unit= mg, number= 75, form= injection, route= intramuscular use. Single injection with 75 mg eq. 3-month formulation paliperidone palmitate F015 in the gluteal muscle.
Paliperidone palmitate F015 (Panel B: treatment group 2)DRUGType= exact number, unit= mg, number=150, form= injection, route= intramuscular use. Single injection with 150 mg eq. 3-month formulation paliperidone palmitate F015 in the gluteal muscle.
Paliperidone palmitate F015 (Panel B: treatment group 3)DRUGType= exact number, unit= mg, number=450, form= injection, route= intramuscular use. Single injection with 450 mg eq. 3-month formulation paliperidone palmitate F015 in the gluteal muscle.
Paliperidone palmitate F015 (Panel B: treatment group 4)DRUGType= exact number, unit= mg, number=300, form= injection, route= intramuscular use. Single injection with 300 mg eq. 3-month formulation paliperidone palmitate F015 in the deltoid muscle.
Paliperidone palmitate F015 (Panel B: treatment group 5)DRUGType= exact number, unit= mg, number=450, form= injection, route= intramuscular use. Single injection with 450 mg eq. 3-month formulation paliperidone palmitate F015 in the deltoid muscle.
Paliperidone palmitate F016DRUGType= exact number, unit= mg, number=150, form= injection, route= intramuscular use. Single injection with 150 mg eq. 3-month formulation paliperidone palmitate F016 in the gluteal muscle.
Paliperidone palmitate F015 (Panel D: treatment group 1)DRUGType= exact number, unit= mg, number=525, form= injection, route= intramuscular use. Single injection with 525 mg eq. 3-month formulation paliperidone palmitate F015 in the gluteal muscle.
Paliperidone palmitate F015 (Panel D: treatment group 2)DRUGType= exact number, unit= mg, number=525, form= injection, route= intramuscular use. Single injection with 525 mg eq. 3-month formulation paliperidone palmitate F015 in the deltoid muscle.
Paliperidone palmitate F015 (Panel D: treatment group 3)DRUGType= exact number, unit= mg, number=350, form= injection, route= intramuscular use. Single injection with 350 mg eq. 3-month formulation paliperidone palmitate F015 in the gluteal muscle.
Paliperidone palmitate F015 (Panel D: treatment group 4)DRUGType= exact number, unit= mg, number=175, form= injection, route= intramuscular use. Single injection with 175 mg eq. 3-month formulation paliperidone palmitate F015 in the deltoid muscle.
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Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersNo
Study Sites36

Inclusion Criteria: * Patients diagnosed with schizophrenia or schizoaffective disorder, for at least 1 year before screening * Clinically stable with no hospitalizations for schizophrenia exacerbation or change in current antipsychotic medications for 3 months prior to screening * Stabilized on an...

Countries:United StatesBelgiumBulgariaCroatiaIsraelMalaysiaSlovakiaSouth AfricaSouth KoreaSpainTaiwan
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