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RUC-4 Compound

Phase 1

Coronary Disease | Small molecule | Cardiovascular |Precision BioSciences, Inc.|Last Updated: Aug 27, 2024

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment44
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03844191A Randomized Phase 1 Dose-Escalation Study of Subcutaneously(SC) Administered RUC-4PHASE1 COMPLETED 44Feb 18, 2019Dec 1, 2019Aug 27, 20241 United States
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Study Endpoints
Primary Endpoints
Platelet Inhibition
5 minutes

inhibition of platelet aggregation

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Study Design & Arms
AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Part 1 Cohort 1EXPERIMENTALCohort 1: 0.05 mg/kg RUC-4/placebo 7 subjects will be enrolled: 6 subjects will receive a single subcutaneous dose of RUC-4 and 1 subject will receive matched placebo.
Part 1 Cohort 2EXPERIMENTALCohort 2: 0.075 mg/kg RUC-4/placebo 7 subjects will be enrolled: 6 subjects will receive a single subcutaneous dose of RUC-4 and 1 subject will receive matched placebo.
Part 2 Cohort 1EXPERIMENTALCohort 1: initial dose to be selected by the Safety Review Committee (SRC) after completion of Part 1 (the same initial dose used in Part 1 or one of the previously studied higher doses that is lower than the overall RUC-4 BED) 7 subjects will be enrolled: 6 subjects will receive a single subcutaneous dose of RUC-4 and 1 subject will receive matched placebo.
Part 2 Cohorts 2-3EXPERIMENTAL7 subjects (6 receiving RUC-4, 1 receiving placebo) will be enrolled in each dose cohort, with a safety evaluation performed after 2 subjects in a dose cohort receive RUC 4 and at the completion of dosing for all subjects in the dose cohort. Dose escalation to be determined by the SRC charter and will continue until identification of the overall RUC-4 BED or MTD
Part 2 Dose Expansion Cohort 1EXPERIMENTAL14 subjects will receive a selected dose of RUC-4 based on SRC review of dose escalation data. In the expansion cohort, 7 subjects weighing 55 to 65 kg and 7 subjects weighing 100 to 120 kg will be enrolled; 12 subjects will receive a single subcutaneous dose of RUC-4 and 2 will receive matched placebo
Interventions
NameTypeDescription
RUC-4 CompoundDRUGsingle subcutaneous administration of RUC-4
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersYes
Study Sites1

Main Inclusion Criteria (all subjects) * weight between 55-120 kg, inclusive, and BMI between 18-38 kg/m2 * females must be non-pregnant, non-lactating, and of non-childbearing potential. * good general health as determined by no acute illness and no clinically significant abnormal findings on medi...

Countries:United States
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