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Chimeric Fibril-Reactive Monoclonal Anti-body 11-1F4

Phase 1

AL Amyloidosis | Small molecule | Rare Disease |AstraZeneca PLC|Last Updated: Feb 7, 2025

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment30

FDA Designations

No designations recorded

Clinical trial landscape

Chimeric Fibril-Reactive Monoclonal Anti-body 11-1F4 · 1 trial · 1 indication

Phase 1 1
NCT02245867Study of Chimeric Fibril-Reactive Monoclonal Antibody 11-1F4 in Patients With AL AmyloidosisAL Amyloidosis
COMPLETED30 Analytics
PHASE1COMPLETED
Study of Chimeric Fibril-Reactive Monoclonal Antibody 11-1F4 in Patients With AL Amyloidosis
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Study Endpoints

Primary Endpoints

Maximum Tolerated Dose (MTD) of Ch mAb 11-1F4
2 years approximately

The MTD of a single application of Ch mAb 11-1F4 is defined as the highest safely-tolerated dose (mg/m2) where 0 patients experiences Dose Limiting Toxicity.

Secondary Endpoints

Number of subjects with positive amyloid-related organ response
12 weeks
Estimated mean area under the curve (AUC) for Ch mAb 11-1F4
Phase 1a: 1, 2, 24 hours post start of infusion; then post-infusion week 1, 2, 3, 4, 8. Phase 1b: pretreatment, 1, 2, 24 hours post start of infusion; then post-infusion week 5, 8, 12.
Number of participants with adverse events
2 years approximately
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Phase IaEXPERIMENTALAdministration of Chimeric Fibril-Reactive Monoclonal Anti-body 11-1F4: A 1-patient cohort will be infused with 0.5 mg/m2 of Ch 11-1F4 and, if tolerated, the doses in the next patients will be increased to 5, 10, 50, 100, 250, and finally, 500 mg/m2. All individuals will be evaluated prior to treatment, after infusion weekly for four weeks, as well as at 8 weeks.
Phase IbEXPERIMENTALAdministration of Chimeric Fibril-Reactive Monoclonal Anti-body 11-1F4: Subjects will receive four weekly infusions of the monoclonal anti-body at Dose Level 1 (0.5 mg/m2). If tolerated, the doses in the next patients will be increased to 5, 10, 50, 100, 250, and finally, 500 mg/m2. When the highest tolerated dose is reached without toxicity in 2 patients, an additional 4 patients will be enrolled and infused at that dose. Escalation or de-escalation will continue until we have determined the highest dose level at which less than 2 patients experience toxicity. All individuals will be evaluated prior to each course of treatment, as well as at weeks 5, 8, and 12.

Interventions

NameTypeDescription
Chimeric Fibril-Reactive Monoclonal Anti-body 11-1F4DRUGThe antibody binds to the pathologic material and initiates a neutrophil/macrophage response
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Eligibility Criteria

Age Range21 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Patients must have a confirmed diagnosis of AL amyloidosis based on accepted clinical and laboratory criteria. * Patients are greater than 21 years old. * Female patients are not of child bearing potential or if they are of child bearing potential, they must not be pregnant...

Countries:United States
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