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efzofitimod

Phase 2

Interstitial Lung Disease | Small molecule | Respiratory |aTyr Pharma, Inc.|Last Updated: May 7, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment25
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05892614Study to Evaluate the Efficacy, Safety, and Tolerability of Efzofitimod in Patients With Systemic Sclerosis (SSc)-Related Interstitial Lung Disease (ILD) (SSc-ILD)PHASE2 RECRUITING 25Oct 26, 2023Apr 1, 2026May 7, 202515 United States
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Study Endpoints
Primary Endpoints
Absolute change from baseline in forced vital capacity (FVC) in mL
24 weeks
Annual rate of decline in FVC in mL
24 weeks
Annual rate of decline in FVC in percent predicted
24 weeks
Change in HRCT fibrosis score
Baseline to Week 24
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Study Design & Arms
AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
efzofitimod 450 mgEXPERIMENTALAdministered IV infusion
efzofitimod 270 mgEXPERIMENTALAdministered IV infusion
PlaceboPLACEBO_COMPARATORAdministered IV infusion
Interventions
NameTypeDescription
efzofitimod 450 mgDRUGIV infusion over approximately 60 minutes every 4 weeks
efzofitimod 270 mgDRUGIV infusion over approximately 60 minutes every 4 weeks
PlaceboDRUGIV infusion over approximately 60 minutes every 4 weeks
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites15

Inclusion Criteria: 1. Diagnosis of SSc based on ACR/ EULAR criteria (2013) 2. Overall duration of SSc \< 84 months from the first non-Raynaud symptom manifestation prior to Day 1 3. HRCT obtained at the Screening Visit or within the 3 months prior to Screening consistent with SSc-ILD (adjudicated ...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT05892614primaryCompletionDate: changed
LOWMay 24, 2026NCT05892614studyFirstPostDate: changed