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Posiphen

Phase 1

Alzheimer Disease | Small molecule | Neurology |Annovis Bio, Inc.|Last Updated: May 9, 2023

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment75

FDA Designations

No designations recorded

Clinical trial landscape

Posiphen · 2 trials · 3 indications

Phase 1 2
NCT04524351Posiphen® Dose-Finding, Biomarker Study in Early Alzheimer's and Parkinson's PatientsAlzheimer Disease
COMPLETED75 Analytics
NCT02925650Safety, Tolerability, PK and PD of Posiphen® in Subjects With Early Alzheimer's DiseaseAlzheimer's Disease
COMPLETED18 Analytics
PHASE1COMPLETED
Posiphen® Dose-Finding, Biomarker Study in Early Alzheimer's and Parkinson's Patients
Alzheimer DiseaseUnlock trial analytics
PHASE1COMPLETED
Safety, Tolerability, PK and PD of Posiphen® in Subjects With Early Alzheimer's Disease
Alzheimer's DiseaseUnlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of Participants With Treatment-Emergent Adverse Events
25±2 days

Percent of patients with AEs in the Posiphen treatment arms compared to the Placebo group

Safety and Tolerability of Multiple Ascending Doses of Posiphen: Reports of Adverse Events or Study Discontinuations
Up to 25 days

Number of adverse events or study discontinuations, broken down by dose arm (i.e. Low vs. Medium vs. High vs. Placebo), and further broken down by relatedness to Posiphen (Definitely Related, Probably Related, Possibly Related, Unlikely Related, Unrelated)

The Levels of Posiphen and Its Metabolites Will be Determined in Plasma
The confinement visit occurred following 21-23 days of treatment with either Posiphen or placebo, while also allowing a +/- 2-day visit window. Plasma was collected at 0, 2, 4, 8, 12, 16, 20, and 24hrs during the confinement visit.

Mean plasma concentrations of levels of posiphen tartrate, N1 desmethyl posiphen, and N8 desmethyl Posiphen metabolite were determined for each of the three dose cohorts (Low Dose, Medium Dose, High Dose) by a protein precipitation extraction method using a high performance liquid chromatographic mass spectrometric detection method, with a linear weighted regression to determine their concentrations.

The Levels of Posiphen and Its Metabolites Will be Determined in Cerebrospinal Fluid (CSF)
The confinement visit occurred following 21-23 days of treatment with either Posiphen or placebo, while also allowing a +/- 2-day visit window. Plasma was collected at 0, 2, 4, 8, 12, 16, 20, and 24hrs during the confinement visit.

Mean CSF concentrations of levels of posiphen tartrate, N1 desmethyl posiphen, and N8 desmethyl Posiphen metabolite were determined for each of the three dose cohorts (Low Dose, Medium Dose, High Dose) by a protein precipitation extraction method using a high performance liquid chromatographic mass spectrometric detection method, with a linear weighted regression to determine the concentrations.

Fractional Synthesis Rate of Aβ40 in CSF Using the SILK™ Technique With Multiple Doses of Posiphen
The confinement visit occurred following 21-23 days of treatment with either Posiphen or placebo, while also allowing a +/- 2-day visit window. CSF was collected between 6 and 16hrs during the confinement visit.

The fractional synthesis rate (FSR) of Aβ40 was measured in the CSF using the SILK™ technique. FSR is a measure of the rate of Aβ synthesis in the brain. During 13C6-leucine infusion, 13C6-leucine is incorporated into newly synthesized proteins throughout the body, including the brain, in proportion to the available 13C6-leucine. This FSR is calculated as the rate of change of the ratio of 13C6-leucine-labeled Aβ proteins to unlabeled Aβ proteins in the lumbar CSF between 6 to 16 hours, normalized to the ratio of labeled to unlabeled leucine amino acid in plasma. It is reported as a fraction of 13C6-leucine-labeled to unlabeled Aβ proteins per hour. The ratio of Aβ in CSF containing 13C6-leucine to that containing unlabeled leucine is measured using mass spectrometry.

Secondary Endpoints

Concentration of Posiphen in Plasma
Samples collected over a 6 hour timeframe
Feasibility of CSF Catheter Study With SILK™ Technology to Evaluate Rates of Enrollment
Up to 25 days
Feasibility of CSF Catheter Study With SILK™ Technology to Evaluate %CSF Samples With Enough Volume for Testing
Up to 25 days
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Posiphen, 80mg (Parkinson's Participants)ACTIVE_COMPARATORPosiphen Oral Capsule, 80mg, taken once per day for 25±2 days.
Posiphen, 40mg (Parkinson's Participants)ACTIVE_COMPARATORPosiphen Oral Capsule, 40mg, taken once per day for 25±2 days.
Posiphen, 20mg (Parkinson's Participants)ACTIVE_COMPARATORPosiphen Oral Capsule, 20mg, taken once per day for 25±2 days.
Posiphen, 10mg (Parkinson's Participants)ACTIVE_COMPARATORPosiphen Oral Capsule, 10mg, taken once per day for 25±2 days.
Posiphen, 5mg (Parkinson's Participants)ACTIVE_COMPARATORPosiphen Oral Capsule, 5mg, taken once per day for 25±2 days.
Placebo (Parkinson's Participants)PLACEBO_COMPARATORPlacebo Oral Capsule, taken once per day for 25±2 days.
Placebo (Alzheimer's Participants)PLACEBO_COMPARATORPlacebo Oral Capsule, taken once per day for 25±2 days.
Posiphen, 80mg (Alzheimer's Participants)ACTIVE_COMPARATORPosiphen Oral Capsule, 80mg, taken once per day for 25±2 days.
Low DoseEXPERIMENTALThe study drug Posiphen dosage of 60mg is to be taken orally in divided doses, three times per day for a total 23-25 days.
Medium DoseEXPERIMENTALThe study drug Posiphen dosage of 120mg is to be taken orally in divided doses, three times per day for a total 23-25 days.
High DoseEXPERIMENTALThe study drug Posiphen dosage of 180mg is to be taken orally in divided doses, three times per day for a total 23-25 days.
PlaceboPLACEBO_COMPARATORThe Placebo comparator is to be taken orally in divided doses, three times per day for a total 23-25 days.

Interventions

NameTypeDescription
PosiphenDRUGSolid oral dosage form, capsule
PlaceboDRUGSolid oral dosage form, capsule
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Eligibility Criteria

Age Range45 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites13

Inclusion Criteria Subjects must meet the following criteria: 1. Male or female aged 45 years and over. 2. Female participants must be of non-childbearing potential or post-menopausal for at least 2 consecutive years or surgically sterile (bilateral tubal ligation, hysterectomy or bilateral oophor...

Countries:United States
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Frequently asked questions about Posiphen

What is Posiphen used for?

Posiphen is an investigational small molecule being developed for Alzheimer's Disease. It is being studied in early Alzheimer's patients to evaluate its safety, tolerability, and effects on biomarkers. The drug is not approved and remains in clinical development.

Who makes Posiphen?

Posiphen is being developed by Annovis Bio, Inc., a biopharmaceutical company traded on the NYSE American under the ticker symbol ANVS. The company is conducting clinical trials to evaluate the drug's potential in treating Alzheimer's Disease.

What phase is Posiphen in?

Posiphen is in Phase 1 clinical development. Two Phase 1 trials have been completed, both in the United States. The drug is investigational and has not received FDA approval for any indication.

What clinical trials is Posiphen in?

Posiphen has been studied in two completed Phase 1 trials: NCT02925650, a safety and tolerability study in early Alzheimer's patients, and NCT04524351, a dose-finding biomarker study in early Alzheimer's and Parkinson's patients. Both trials were conducted in the United States.

Is Posiphen the same as other Alzheimer's drugs?

Posiphen is a distinct small molecule being developed by Annovis Bio. It is not the same as other marketed Alzheimer's treatments. Its mechanism of action is not disclosed in available clinical trial information, and it remains under investigation for early Alzheimer's disease.