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Gluten- and casein-free diet

Phase 2

Autism | Unknown | Psychiatry |United Therapeutics Corporation|Last Updated: Oct 1, 2010

Success Probability

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Market & Valuation

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Trial Design

RandomizedNO_TREATMENT_CONTROLLED
Total Trials1
Total Enrollment72

FDA Designations

No designations recorded

Clinical trial landscape

Gluten- and casein-free diet · 1 trial · 2 indications

Phase 2 1
NCT00614198ScanBrit Dietary Intervention in AutismAutism
COMPLETED72 Analytics
PHASE2COMPLETED
ScanBrit Dietary Intervention in Autism
AutismUnlock trial analytics

Study Endpoints

Primary Endpoints

Change in Diet Groups Scores on One of Several Measures Used Against Pre-defined Statistical Thresholds as Evidence of Improvement.
Baseline - 8 months - 12 months - 24 months

ADOS (Autism Diagnostic Observation Schedule): module 1 cutoff scores (communication+social): autism=12, autism spectrum (AS)=7; module 2 cutoffs: autism=12, AS=8; module 3 cutoffs: autism=10; AS=7. GARS (Gilliam Autism Rating Scale): \<80 low probability of autism, 81-90 below average, 91-110 average, \>110 above average probability of autism. VABS (Vineland Adaptive Behaviour Scale): \<69 (low ability), 70-84 (moderate/low), 85-115 (adequate), 116-130 (moderate/high), \>130 (high). ADHD-IV: 0=no problems indicated. \>11 attention \& \>11 hyperactivity = ADHD diagnosis.

Secondary Endpoints

Changes to Appearance of Multiple Compounds in Urine Samples
Baseline - 8 months -12 months - 24 months
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Study Design & Arms

AllocationRANDOMIZED
MaskingSINGLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Gluten- and casein-free dietEXPERIMENTALStage 1: Gluten- and casein-free dietary intervention for first 8 or 12 months. 8 or 12 months: Interim analysis based on surpassing statistical thresholds. If showed group significant improvements then progressed to stage 2 (continued on a gluten- and casein-free diet for a further 12 months).
No dietary interventionNO_INTERVENTIONStage 1: No special dietary intervention for first 8 or 12 months. 8 or 12 months: Interim analysis based on surpassing statistical thresholds. If gluten- and casein-free dietary group showed group significant improvements then progressed to stage 2 (introduction of a gluten- and casein-free diet for 12 months).

Interventions

NameTypeDescription
Gluten- and casein-free dietOTHERRemoval of foods containing gluten (cereal produce) and casein (dairy produce)
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Eligibility Criteria

Age Range4 Years to 11 Years
SexALL
Healthy VolunteersNo

Inclusion Criteria: * Autism Spectrum Disorder (ASD) * Diagnosis received at Centre for Autism or a psychiatric clinic * Abnormal urinary peptide profile Exclusion Criteria: * Medical treatment * Epilepsy

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Frequently asked questions about Gluten- and casein-free diet

What is the gluten- and casein-free diet used for in autism?

The gluten- and casein-free diet is an investigational dietary intervention being studied for autism and autism spectrum disorder (ASD). It involves removing gluten and casein from the diet. It is currently in Phase 2 clinical development and is not approved by the FDA.

Who is developing the gluten- and casein-free diet?

United Therapeutics Corporation (NASDAQ: UTHR) is the developer of the gluten- and casein-free diet for autism. The company is conducting clinical research on this dietary approach as a potential intervention for autism spectrum disorder.

What phase is the gluten- and casein-free diet in?

The gluten- and casein-free diet is in Phase 2 clinical development for autism. It is an investigational dietary intervention and has not received FDA approval. One Phase 2 trial has been completed, with no active trials currently ongoing.

What clinical trials is the gluten- and casein-free diet in?

The gluten- and casein-free diet was studied in the ScanBrit Dietary Intervention in Autism trial, registered as NCT00614198. This Phase 2 study enrolled 72 participants aged 4 years and older with autism or autism spectrum disorder. The trial was completed and was randomized but not double-blind.

Is the gluten- and casein-free diet the same as a standard autism treatment?

No, the gluten- and casein-free diet is an investigational dietary intervention, not a standard or approved treatment for autism. It is being studied as a potential approach to manage autism symptoms, but it has not been established as a conventional therapy.