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1. Intranasal oxytocin

Phase 2

Autism Spectrum Disorder | Small molecule | Psychiatry |United Therapeutics Corporation|Last Updated: Mar 2, 2026

Success Probability
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment96
FDA Designations
No designations recorded
Clinical trial landscape

1. Intranasal oxytocin · 1 trial · 2 indications

Phase 2 1
NCT05754073Oxytocin Effects on Bone in Children With Autism Spectrum DisorderAutism Spectrum Disorder
RECRUITING96 Analytics
PHASE2RECRUITING
Oxytocin Effects on Bone in Children With Autism Spectrum Disorder
Autism Spectrum DisorderUnlock trial analytics
Study Endpoints
Primary Endpoints
Difference between IN OXT vs placebo in 12-month change in whole body less head BMD Z-scores.
12 months
Secondary Endpoints
Difference between IN OXT vs placebo in 12-month change in areal BMD Z-score at the femoral neck.
12 months
Difference between IN OXT vs placebo in 12-month change in radial and tibial cortical area and radial trabecular thickness.
12 months
Difference between IN OXT vs placebo in 12-month change in radial and tibial failure load.
12 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposePREVENTION
Treatment Arms
ArmTypeDescription
1. Intranasal OxytocinEXPERIMENTALIntranasal oxytocin spray (30 IU twice daily) for 12 months in the double-blinded phase followed by intranasal oxytocin spray (30 IU twice daily) for 6-months in the open-label phase
2. PlaceboPLACEBO_COMPARATORIntranasal placebo spray (30 IU twice daily (total 60 IU per day) for 12 months followed by intranasal oxytocin spray (30 IU twice daily) for 6-months in the open-label phase
Interventions
NameTypeDescription
1. Intranasal oxytocin sprayDRUG30 IU, twice daily for 12 months in the experimental arm in double-blinded phase
2. Intranasal placebo sprayDRUG30 IU, twice daily for 12 months in the placebo comparator arm in double-blinded phase
3. Intranasal Oxytocin sprayDRUG30 IU, twice daily for 6 months in both experimental and placebo comparator arm in open-label phase
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Eligibility Criteria
Age Range6 Years to 18 Years
SexALL
Healthy VolunteersNo
Study Sites2

Inclusion Criteria: 1. Ages 6 to 18 years old at Randomization 2. BMI greater than or equal to the 5th percentile 3. Expert clinical diagnosis of ASD 4. Availability of parent/guardian to provide informed consent Exclusion Criteria: 1. Fragile X, tuberous sclerosis, William's syndrome, Angelman's...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT05754073studyFirstPostDate: changed