Recent Updates
Recently added Catalysts

Balovaptan

Phase 2

Stress Disorders, Post-Traumatic | Small molecule | Psychiatry |Roche Holding AG|Last Updated: Apr 18, 2024

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment29

FDA Designations

No designations recorded

Clinical trial landscape

Balovaptan · 5 trials · 3 indications

Phase 2 1Phase 1 4
NCT05401565Study To Evaluate The Efficacy And Safety Of Balovaptan In Adults With Post-Traumatic Stress Disorder (PTSD)Stress Disorders, Post-Traumatic
COMPLETED29 Analytics
PHASE2COMPLETED
Study To Evaluate The Efficacy And Safety Of Balovaptan In Adults With Post-Traumatic Stress Disorder (PTSD)
Stress Disorders, Post-TraumaticUnlock trial analytics

Study Endpoints

Primary Endpoints

Change From Baseline in the Clinician-Administered PTSD Total Symptom Severity Score
From Baseline up to Week 12

The Clinician-Administered PTSD Scale for DSM-5 (CAPS-5) measures the severity of PTSD where smaller scores indicate less severe PTSD and higher scores suggest more severe PTSD. Possible scores for this 30 item version range from 0 to 120. Measured 3 times over 12 weeks.

Maximum Plasma Concentration (Cmax) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Maximum plasma concentration of Balovaptan is estimated using non-compartmental methods. Observed peak analyte concentration obtained directly from the experimental data without interpolation, expressed in concentration units

Mean Area Under the Concentration-Time Curve From Time Extrapolated to Infinity (AUC (0-inf)) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Area under the plasma concentration-time curve (time 0 to infinity) of Balovaptan is estimated using non-compartmental methods from the concentration-time profiles. Percent extrapolation less than or equal to 20% is required to obtain a reliable AUC0-inf.

Area Under the Concentration-Time Curve From Time 0 to 24 Hours (AUC(0-24h)) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16 and 24 hours post dose

Area under the plasma concentration-time curve of Balovaptan from time 0 to 24 hours post-dose is estimated using non-compartmental methods from the concentration-time profiles.

Area Under the Concentration-Time Curve From Time 0 to the Time of the Last Quantifiable Concentration (AUClast) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Area under the concentration-time curve (time 0 to time of last quantifiable concentration) of Balovaptan is estimated using non-compartmental methods from the concentration-time profiles.

Time to Reach Cmax in Plasma (Tmax) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Time to maximum plasma concentration of Balovaptan is defined as first observed time to reach peak analyte concentration obtained directly from the experimental data without interpolation, expressed in time units and estimated using non-compartmental methods from the concentration-time profiles.

Last Quantifiable Concentration (Clast) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Last quantifiable concentration is estimated using non-compartmental methods from the concentration-time profiles.

Time To the Last Quantifiable Concentration (Tlast) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Time to last quantifiable concentration is based on last detectable concentration in the time curve.

Time Between Dosing and Time of First Balovaptan Plasma Concentration (Tlag)
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Time between dosing and time of first balovaptan plasma concentration is estimated using non-compartmental methods from the concentration-time profiles.

Apparent Clearance (Cl/F) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Apparent clearance is estimated using non-compartmental methods from the concentration-time profiles.

Apparent Volume of Distribution (Vd/F) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Apparent volume of distribution is estimated using non-compartmental methods from the concentration-time profiles.

Terminal Elimination Phase Half-Life (T1/2) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Terminal phase half-life expressed in time units is estimated using non-compartmental methods from the concentration-time profiles.

Terminal Phase Rate Constant (λz) of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Terminal phase rate constant is estimated using non-compartmental methods from the concentration-time profiles.

Plasma Concentrations of Balovaptan
Samples at predose, and at 0.25, 0.5, 1, 1.5, 2, 2.5, 3, 3.5, 4, 5, 6, 8, 12, 16, 24, 36, 48, 72, 96, 144, and 192 hours post dose

Amount of Balovaptan in a given volume of plasma.

Absolute Bioavailability of Oral Balovaptan at Dose Level A (Cohort 1)
Day 1 of Period 1 (Period 1 is 14 days).

Absolute oral bioavailability of a single dose A of balovaptan.

Maximum Plasma Concentration (Cmax) for Balovaptan
Day 10 of Period 1 and Day 16 of Period 2

Cmax is the observed peak analyte concentration obtained directly from the experimental data without interpolation, expressed in concentration units.

Maximum Plasma Concentration (Cmax) for M2 Metabolite
Day 10 of Period 1 and Day 16 of Period 2

Cmax is the observed peak analyte concentration obtained directly from the experimental data without interpolation, expressed in concentration units.

Maximum Plasma Concentration (Cmax) for M3 Metabolite
Day 10 of Period 1 and Day 16 of Period 2

Cmax is the observed peak analyte concentration obtained directly from the experimental data without interpolation, expressed in concentration units.

Area Under the Plasma Concentration Curve From Time 0 to 24 Hours (AUC0-24) for Balovaptan
Day 10 and 11 of Period 1; Day 16 and 17 of Period 2

AUC0-24 is the area under the plasma concentration-time curve from time 0 to 24 hours post dose.

Area Under the Plasma Concentration Curve From Time 0 to 24 Hours for M2 Metabolite
Day 10 and 11 of Period 1; Day 16 and 17 of Period 2

AUC0-24 is the area under the plasma concentration-time curve from time 0 to 24 hours post dose.

Area Under the Plasma Concentration Curve From Time 0 to 24 Hours for M3 Metabolite
Day 10 and 11 of Period 1; Day 16 and 17 of Period 2

AUC0-24 is the area under the plasma concentration-time curve from time 0 to 24 hours post dose.

Maximum Plasma Concentration (Cmax) for M2 Metabolite (as Applicable)
Day 10 of Period 1, Day 10 and Day 15 of Period 2

Cmax is the observed peak analyte concentration obtained directly from the experimental data without interpolation, expressed in concentration units.

Area Under the Concentration Vs Time Curve Over the Dosing Interval (AUC0-tau) for Balovaptan
Day 10 of Period 1, Day 10 and Day 15 of Period 2
Area Under the Concentration Vs Time Curve Over the Dosing Interval (AUC0-tau) for M2 Metabolite (as Applicable)
Day 10 of Period 1, Day 10 and Day 15 of Period 2
Area Under the Concentration Vs Time Curve Over the Dosing Interval (AUC0-tau) for M3 Metabolite
Day 10 of Period 1, Day 10 and Day 15 of Period 2
Time to Maximum Observed Plasma Concentration (Tmax) for Balovaptan
Day 10 of Period 1; Day 10 and Day 15 of Period 2
Time to Maximum Observed Plasma Concentration (Tmax) for M2 Metabolite (as Applicable)
Day 10 of Period 1; Day 10 and Day 15 of Period 2
Time to Maximum Observed Plasma Concentration (Tmax) for M3 Metabolite
Day 10 of Period 1; Day 10 and Day 15 of Period 2

Secondary Endpoints

Symptom Severity as Measured by Clinician-Global Impression of Severity (CGI-S) Scale Score
From Baseline up to Week 12
Change From Baseline at Week 12 in the Patient Health Questionnaire-9 (PHQ-9) Total Score
From Baseline up to Week 12
Percentage of Participants With Adverse Events
From Baseline up to Week 12
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
BalovaptanEXPERIMENTAL -
PlaceboPLACEBO_COMPARATOR -
Treatment sequence ABCEXPERIMENTALIn Period 1 participants will receive 1 tablet of balovaptan after high-fat, high-calorie meal. In Period 2, after 12 to 21 days wash-out, participants will receive 1 tablet of balovaptan after 10-hour fast. In Period 3 participants will receive esomeprazole administered once daily for 6 days and with a single oral dose of balovaptan in the fasted state 1 hour after the fifth esomeprazole dose
Treatment sequence BACEXPERIMENTALIn Period 1 participants will receive 1 tablet of balovaptan after 10-hour fast. In Period 2, after 12 to 21 days wash-out, participants will receive 1 tablet of balovaptan after high-fat, high-calorie meal. In Period 3 participants will receive esomeprazole administered once daily for 6 days and with a single oral dose of balovaptan in the fasted state 1 hour after the fifth esomeprazole dose
Cohort 1EXPERIMENTALParticipants received the study drug at dose level A in 2 periods. There was a minimum of a 14-day wash out period between Day 1 of Period 1 and Day 1 of Period 2.
Cohort 2EXPERIMENTALParticipants received the study drug at dose level B in 2 periods. There was a minimum of a 14-day wash out period between Day 1 of Period 1 and Day 1 of Period 2.
Balovaptan + RifampicinEXPERIMENTALParticipants received the study drugs in 2 periods. There was a minimum of a 14-day to a maximum of a 21-day washout between the last dose in Period 1 and the first dose in Period 2.
Balovaptan + ItraconzoleEXPERIMENTALDosing in Period 1 was separated by at least a 7 day washout period before dosing starts in Period 2. Participants received the study drugs in 2 periods over a total of 37 days.

Interventions

NameTypeDescription
BalovaptanDRUGIntervention of oral administration of 10mg balovaptan QD for 12 weeks followed by two weeks of follow-up period
PlaceboDRUGMatching placebo
EsomeprazoleDRUGEsomeprazole will be administered once daily for 6 days and with a single dose of balovaptan 1 hour after the fifth esomeprazole dose
Oral BalovaptanDRUGIn Period 1, balovaptan was administered as a single oral dose. In Period 2, balovaptan was administered as an oral dose once daily on Day 1 to Day 14.
IV BalovaptanDRUGIn Period 1, IV infusion of balovaptan was administered after the balovaptan oral dose. In Period 2, IV infusion of balovaptan was administered after the final oral dose of balovaptan.
RifampicinDRUGIn Period 2, 600 mg of rifampicin will be administered alone as a qd dose from Day 1 to Day 6, and as a qd dose on Days 7 to 16.
ItraconazoleDRUGIn Period 2, 200 mg itraconzole was administered bid for 4 days and qd on Days 5-20, approximately 12 hours apart. On Days 6-20, 200 mg itraconazole was administered qd.
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to 60 Years
SexALL
Healthy VolunteersNo
Study Sites15

Inclusion Criteria: * Participants who have a current diagnosis of PTSD as per DSM-5 criteria, with a score of \>/=33 on the PCL-5 at screening * The index trauma event must have occurred in adulthood, i.e., when the participant was \>/=18 years old * The index trauma event must have occurred at le...

Countries:United StatesNetherlands
Unlock Eligibility Criteria

Frequently asked questions about Balovaptan

What is Balovaptan used for?

Balovaptan is an investigational small molecule being developed by Roche Holding AG for psychiatric conditions including stress disorders, post-traumatic stress disorder, and autism spectrum disorder. It is currently in Phase 1 clinical development and has been studied in healthy volunteers to evaluate its pharmacokinetics and drug interactions.

Who makes Balovaptan?

Balovaptan is being developed by Roche Holding AG, a pharmaceutical company traded on the OTC market under the ticker RHHBY. The drug is an investigational small molecule in Phase 1 clinical development for psychiatric indications including autism spectrum disorder and stress disorders.

What phase is Balovaptan in?

Balovaptan is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. All three completed clinical trials for Balovaptan were Phase 1 studies conducted in healthy volunteers to assess pharmacokinetics and drug interactions.

What clinical trials is Balovaptan in?

Balovaptan has been studied in three completed Phase 1 clinical trials. These include NCT03579719, NCT03586726, and NCT03764449, all conducted in healthy volunteers in the Netherlands. A fourth trial, NCT04156646, investigated the effects of esomeprazole and food on Balovaptan pharmacokinetics in healthy volunteers in the United States.

Is Balovaptan FDA approved?

Balovaptan is not FDA approved. It is an investigational drug currently in Phase 1 clinical development. The completed trials for Balovaptan were early-stage studies focused on pharmacokinetics and drug interactions in healthy volunteers, and the drug remains under investigation for psychiatric conditions.

What does Balovaptan target?

Balovaptan is a small molecule being developed for psychiatric conditions, but its specific molecular target has not been disclosed in the available clinical trial information. The drug is in Phase 1 development for stress disorders, post-traumatic stress disorder, and autism spectrum disorder.