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Terlipressin continuous infusion

Phase 2

Cirrhosis | Small molecule | Gastrointestinal |BioVie Inc.|Last Updated: Jul 13, 2021

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment6
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03107091Continuous Infusion Terlipressin for Patients With Cirrhosis and Refractory AscitesPHASE2 COMPLETED 6Jul 15, 2017Apr 25, 2019Jul 13, 20211 United States
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Study Endpoints
Primary Endpoints
Clinical Safety of Terlipressin Infusion in Cirrhotic Patients With Refractory Ascites
28 day treatment period and 28 day post-treatment

Rate of treatment emergent adverse events assessed by physical examination and laboratory safety

Steady State Plasma Levels of Terlipressin and 8-lysine Vasopressin During Terlipressin Continuous Infusion at 2 mg/Day in Cirrhotic Patients With Refractory Ascites
7 day treatment

Serial sampling for determination of Terlipressin concentration and metabolite 8-lysine vasopressin in plasma at steady state (Css)

Secondary Endpoints
Change in Requirement of Large Volume Paracentesis With Continuous Infusion of Terlipressin
28 day post-treatment
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Terlipressin acetate continuous infusionEXPERIMENTALContinuous infusion of terlipressin starting at 2 mg/day over 7 days in-house and if tolerated continue treatment in the ambulatory setting for 21 days
Interventions
NameTypeDescription
Terlipressin acetate continuous infusionDRUGLow-dose continuous infusion of Terlipressin administered via ambulatory pump over 28 days
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Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: * Patients with cirrhosis and refractory ascites who required 3 or more large volume (4 liters and more) paracenteses in the previous 60 days Exclusion Criteria: * Ascites with causes other than cirrhosis such as nephrogenic ascites or malignant ascites due to peritoneal carci...

Countries:United States
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