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KSI-301

Phase 3

Macular Edema | Small molecule | Ophthalmology |Kodiak Sciences Inc|Last Updated: Jul 3, 2024

Success Probability

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLEDDMC
Total Trials1
Total Enrollment568

FDA Designations

No designations recorded

Clinical trial landscape

KSI-301 · 2 trials · 3 indications

Phase 3 2
NCT04964089A Study to Evaluate the Efficacy and Safety of Intravitreal KSI-301 Compared With Intravitreal Aflibercept in Participants With Neovascular (Wet) Age-related Macular Degeneration (wAMD)Wet Age-related Macular Degeneration
COMPLETED557 Analytics
NCT04592419A Study to Evaluate the Efficacy, Durability, and Safety of KSI-301 Compared to Aflibercept in Patients With Macular Edema Due to Retinal Vein Occlusion (RVO)Macular Edema
COMPLETED568 Analytics
PHASE3COMPLETED
A Study to Evaluate the Efficacy and Safety of Intravitreal KSI-301 Compared With Intravitreal Aflibercept in Participants With Neovascular (Wet) Age-related Macular Degeneration (wAMD)
Wet Age-related Macular DegenerationUnlock trial analytics
PHASE3COMPLETED
A Study to Evaluate the Efficacy, Durability, and Safety of KSI-301 Compared to Aflibercept in Patients With Macular Edema Due to Retinal Vein Occlusion (RVO)
Macular EdemaUnlock trial analytics

Study Endpoints

Primary Endpoints

Mean Change in Best Corrected Visual Acuity (BCVA) From Day 1 to the Average of Non-missing BCVA Values of Weeks 40, 44 and 48.
Day 1 to Week 48

Best Corrected Visual Acuity (BCVA) was measured on the Early Treatment Diabetic Retinopathy Study (ETDRS) chart at a starting distance of 4 meters. The BCVA letter score ranges from 0 to 100 (best score), and a gain in BCVA letter score from baseline indicates an improvement in visual acuity.

Mean Change in Best Corrected Visual Acuity (BCVA) From Day 1 to Week 24 in BRVO Participants.
Day 1 to Week 24

BCVA as a continuous variable measured at each study visit using the Early Treatment Diabetic Retinopathy Study (ETDRS) BCVA approach.

Mean Change in Best Corrected Visual Acuity (BCVA) From Day 1 to Week 24 in All RVO Patients.
Day 1 to Week 24

BCVA as a continuous variable measured at each study visit using the Early Treatment Diabetic Retinopathy Study (ETDRS) BCVA approach.

Secondary Endpoints

Mean Change in Best Corrected Visual Acuity (BCVA) by Visit Over Time
Day 1 to Week 48
Proportion of Patients Who Gain ≥ 5, ≥10 and ≥15 Letters From Baseline Over Time
Day 1 to Week 48
Proportion of Patients Who Lost ≥ 5, ≥10 and ≥15 Letters From Baseline Over Time
Day 1 to Week 48
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Study Design & Arms

AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
KSI-301 (Treatment Group A)EXPERIMENTALIntravitreal injection of KSI-301 (5 mg) at Day 1 once every 4 weeks via intravitreal injection through Week 44.
Aflibercept (Treatment Group B)ACTIVE_COMPARATORIntravitreal injection of aflibercept (2 mg) once every 4 weeks for 3 monthly doses followed by intravitreal injection of aflibercept (2 mg) once every 8 weeks from Week 16 to Week 44. Sham injections will be administered at each monthly visit where an active treatment is not administered.
KSI-301 (Arm A)EXPERIMENTALIntravitreal injection of KSI-301 (5 mg) at Day 1, Week 4, and once every 8 weeks through Week 20 followed by an individualized dosing regimen of Intravitreal injection of KSI-301 (5 mg) from Week 24 to Week 44. In the Extension Phase, participants randomized to KSI-301 (5 mg) in the Primary Study will continue to receive KSI-301 (5 mg) based on protocol-defined disease activity criteria.
Aflibercept (Arm B)ACTIVE_COMPARATORIntravitreal injection of aflibercept (2 mg) once every 4 through Week 20 followed by an individualized dosing regimen of Intravitreal injection of Aflibercept (2 mg) once every 4 weeks from Week 24 to Week 44. In the Extension Phase, participants randomized to aflibercept in the Primary Study will cross over to treatment with KSI-301 (5 mg). They will receive their first dose of KSI-301 (5 mg) at Week 48 and will receive additional treatment with KSI-301 (5 mg) based on protocol-defined disease activity criteria.

Interventions

NameTypeDescription
KSI-301DRUGIntravitreal Injection
AfliberceptDRUGIntravitreal Injection
Sham ProcedureOTHERThe sham is a procedure that mimics an intravitreal injection. It involves pressing the blunt end of an empty syringe (without a needle) against the anesthetized eye. It will be administered to participants in both treatments arms at applicable visits to maintain masking.
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Eligibility Criteria

Age Range50 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites66

Inclusion Criteria: * Signed informed consent prior to participation in the study. * Treatment-naïve choroidal neovascularization (CNV) secondary to AMD. * BCVA ETDRS score between 83 and 25 letters, inclusive, in the Study Eye. * Decrease in vision in the Study Eye determined by the Investigator t...

Countries:United StatesPuerto RicoCzechiaFranceGermanyHungaryIsraelItalyLatviaPolandSlovakiaSpain
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Frequently asked questions about KSI-301

What is KSI-301 used for?

KSI-301 is an investigational small molecule being developed for ophthalmology indications, specifically macular edema and wet age-related macular degeneration. It is being studied in patients with macular edema due to retinal vein occlusion and in participants with neovascular (wet) age-related macular degeneration.

Who makes KSI-301?

KSI-301 is being developed by Kodiak Sciences Inc, a biopharmaceutical company traded on the NASDAQ under the ticker symbol KOD. The company is conducting clinical trials to evaluate the drug's efficacy and safety in ophthalmology indications.

What phase is KSI-301 in?

KSI-301 is in Phase 3 clinical development. Two Phase 3 trials have been completed, one in macular edema due to retinal vein occlusion and one in wet age-related macular degeneration. The drug is investigational and has not been approved by regulatory authorities.

What clinical trials is KSI-301 in?

KSI-301 has completed two Phase 3 trials. NCT04592419 evaluated KSI-301 compared to aflibercept in 568 patients with macular edema due to retinal vein occlusion. NCT04964089 evaluated KSI-301 compared to aflibercept in 557 participants with wet age-related macular degeneration. Both trials were randomized, double-blind, and active-controlled.

Is KSI-301 the same as aflibercept?

No, KSI-301 is not the same as aflibercept. KSI-301 is an investigational drug developed by Kodiak Sciences, while aflibercept is a separate, approved therapy used as an active comparator in KSI-301's clinical trials. The trials compare KSI-301 directly against aflibercept to evaluate efficacy and safety.