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GWP42006

Phase 2

Epilepsy | Small molecule | Neurology |Jazz Pharmaceuticals plc|Last Updated: Dec 20, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials3
Total Enrollment260
FDA Designations
No designations recorded
Clinical Trials (3)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02365610A Study of GWP42006 in People With Focal Seizures - Part BPHASE2 COMPLETED 162Mar 1, 2016Sep 1, 2017Dec 20, 202226 Czechia, Hungary +4
NCT02369471A Study of GWP42006 in People With Focal Seizures - Part APHASE2 COMPLETED 32Mar 1, 2015Nov 1, 2015Dec 20, 20229 Czechia, Spain +1
NCT01918735A Study of the Safety and Tolerability of GWP42006 in Healthy SubjectsPHASE1 COMPLETED 66Aug 1, 2013Dec 1, 2013Dec 20, 20221 United Kingdom
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Study Endpoints
Primary Endpoints
Percentage change from baseline to the end of treatment in focal seizure frequency in subjects taking GWP42006 compared to placebo.
Day -28 to Day 57
Pharmacokinetic parameters of GWP42006 and metabolites: Cmax, Cmin, tmax, AUC(0-t), AUC(0-inf) and t1/2, in the presence of other AEDs.
Day 1 to Day 18
The incidence of adverse events as measure of subject safety
Day 0 - Day 10

The number of subjects who experienced an adverse event during each arm of the study is presented.

Secondary Endpoints
Number of subjects considered treatment responders.
Day -28 to Day 57
Change from baseline in seizure subtypes frequency.
Day -28 to Day 57
Change from baseline in composite seizure score.
Day -28 to Day 57
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Study Design & Arms
AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
GWP42006EXPERIMENTALGWP42006
Placebo controlPLACEBO_COMPARATORPlacebo
Group 1aEXPERIMENTALSubjects on inducer AEDs will administer GWP42006.
Group 2aACTIVE_COMPARATORSubjects on inhibitor AEDs will administer GWP42006.
Group 3aEXPERIMENTALSubjects on AEDs that are neither inducers nor inhibitors will administer GWP42006.
Group 1bPLACEBO_COMPARATORMatching placebo control for Group 1a.
Group 2bPLACEBO_COMPARATORMatching placebo control for Group 2a.
Group 3bPLACEBO_COMPARATORMatching placebo control for Group 3a.
Group/dose level 1aEXPERIMENTAL25 mg GWP42006 oral solution. As a safety precaution, subjects will be split into two sub-groups for sentinel dosing. On the first day of dosing , only two subjects will be dosed (randomisation schedule designed so that one placebo one active will be dosed on first day). Following a review of the safety data for the first set of subjects, the remaining subjects will be dosed.
Group/dose level 1bPLACEBO_COMPARATORMatching placebo for Group/dose level 1a. As a safety precaution, subjects will be split into two sub-groups for sentinel dosing. On the first day of dosing , only two subjects will be dosed (randomisation schedule designed so that one placebo one active will be dosed on first day). Following a review of the safety data for the first set of subjects, the remaining subjects will be dosed.
Group/dose level 2aEXPERIMENTAL75 mg GWP42006 oral solution. As a safety precaution, subjects will be split into two sub-groups for sentinel dosing. On the first day of dosing , only two subjects will be dosed (randomisation schedule designed so that one placebo one active will be dosed on first day). Following a review of the safety data for the first set of subjects, the remaining subjects will be dosed.
Group/dose level 2bPLACEBO_COMPARATORMatching placebo for Group/dose level 2a. As a safety precaution, subjects will be split into two sub-groups for sentinel dosing. On the first day of dosing , only two subjects will be dosed (randomisation schedule designed so that one placebo one active will be dosed on first day). Following a review of the safety data for the first set of subjects, the remaining subjects will be dosed.
Group/dose level 3aEXPERIMENTAL200 mg GWP42006 oral solution (single dose) followed by an intravenous administration of 5 mg GWP42006 after the oral dose
Group/dose level 3bPLACEBO_COMPARATORMatching placebo for Group/dose level 3a
Group/dose level 4aEXPERIMENTAL400 mg GWP42006 oral solution
Group/dose level 4bPLACEBO_COMPARATORMatching placebo for Group/dose level 4a
GWP42006 1, 2, or 3 times dailyEXPERIMENTALSubjects will receive the selected dose of GWP42006 once, twice or three times daily (the number of daily doses and actual dose will be decided upon based on results from Part 1 of the study) for a total of 5 days, with the final dose given on the morning of Day 5.
Placebo 1, 2, or 3 times dailyPLACEBO_COMPARATORSubjects will receive placebo once, twice or three times daily (the number of daily doses and actual dose will be decided upon based on results from Part 1 of the study) for a total of 5 days, with the final dose given on the morning of Day 5.
Interventions
NameTypeDescription
GWP42006DRUG -
Placebo ControlDRUG -
PlaceboDRUG -
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Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersNo
Study Sites26

For inclusion in Part B of the study patients must fulfil ALL of the following criteria: * Male or female aged between 18 and 65 years, inclusive. * Well-documented history of focal epilepsy, compatible electroencephalogram and clinical history. * Documented computerized tomography / magnetic reson...

Countries:CzechiaHungaryItalyPolandSpainUnited Kingdom
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