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SPN-817

Phase 2

Epilepsy | Small molecule | Neurology |Supernus Pharmaceuticals, Inc.|Last Updated: Jun 1, 2026

Target and mechanism

Molecular targetAChE
Target classEnzyme
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment60

FDA Designations

No designations recorded

Clinical trial landscape

SPN-817 · 3 trials · 3 indications

Phase 2 3
NCT07141329SPN-817 Open-Label Extension Study in Adults With Focal Onset SeizuresFocal Onset Seizures
RECRUITING100 Analytics
NCT06798896RENAISSANCE 2: SPN-817 Phase 2, Double-Blind, Placebo-Controlled Study in Adults With Focal Onset SeizuresFocal Onset Seizures
RECRUITING216 Analytics
NCT05518578Safety and Tolerability Study of SPN-817 in Adult Patients With Treatment Resistant EpilepsyEpilepsy
RECRUITING60 Analytics
PHASE2RECRUITING
SPN-817 Open-Label Extension Study in Adults With Focal Onset Seizures
Focal Onset SeizuresUnlock trial analytics
PHASE2RECRUITING
RENAISSANCE 2: SPN-817 Phase 2, Double-Blind, Placebo-Controlled Study in Adults With Focal Onset Seizures
Focal Onset SeizuresUnlock trial analytics
PHASE2RECRUITING
Safety and Tolerability Study of SPN-817 in Adult Patients With Treatment Resistant Epilepsy
EpilepsyUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence of treatment-emergent adverse events
Week 1-Week 52

The percent of participants who took at least one dose of SPN-817 and reported at least one adverse event during the 1-year SPN-817 Treatment Period

Percent change (PCH) from baseline in focal onset seizure frequency per 28 days over the Maintenance Period
Baseline and Maintenance Period (Maintenance Week 1-14)

Percent change in 28-day frequency of focal seizures during the 14 week Maintenance Period relative to baseline

Effects of SPN-817 on safety and tolerability
72 weeks

The incidence of adverse events.

Secondary Endpoints

Percent change (PCH) from baseline in quantifiable focal onset seizure frequency per 28 days over the 1-year SPN-817 Treatment Period
Baseline and Treatment Period (Week 1-52)
Proportion of participants experiencing ≥50% reduction in focal seizure frequency per 28 days from baseline
Baseline and Treatment Period (Week 1-52)
Proportion of participants experiencing seizure freedom
Baseline and Treatment Period (Week 1-52)
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
SPN-817EXPERIMENTALSPN-817, bid
PlaceboPLACEBO_COMPARATORPlacebo, bid
Open-Label TreatmentEXPERIMENTAL0.25 mg to 4 mg SPN-817 taken orally twice daily

Interventions

NameTypeDescription
SPN-817DRUGSPN-817 starting at 0.25 mg bid up to 4.00 mg bid
PlaceboDRUGPlacebo, bid
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: 1. Completed antecedent SPN-817 double-blind study 2. Taking a stable dosage regimen (maintained during the antecedent study) of at least one antiseizure medication (ASM) and no more than 4 ASMs Exclusion Criteria: 1. Has current nonepileptic events that could be confused by t...

Countries:United StatesAustralia
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Frequently asked questions about SPN-817

What is SPN-817 used for?

SPN-817 is an investigational small molecule being developed for epilepsy, including focal onset seizures and treatment-resistant epilepsy. It is currently in Phase 2 clinical development and is not yet approved by the FDA. The drug is being studied in adult patients with these seizure disorders.

What does SPN-817 target?

SPN-817 targets acetylcholinesterase (AChE), an enzyme involved in neurotransmission. By inhibiting this enzyme, the drug may modulate cholinergic signaling in the brain, which is being investigated as a potential mechanism for reducing seizure activity in epilepsy patients.

Who makes SPN-817?

SPN-817 is being developed by Supernus Pharmaceuticals, Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol SUPN. The company is conducting Phase 2 clinical trials to evaluate the drug's safety and efficacy in treating epilepsy and focal onset seizures.

What phase is SPN-817 in?

SPN-817 is currently in Phase 2 clinical development. It is being evaluated in multiple Phase 2 trials, including a double-blind, placebo-controlled study in adults with focal onset seizures and an open-label extension study. The drug is investigational and has not received FDA approval.

What clinical trials is SPN-817 in?

SPN-817 is being studied in several clinical trials. NCT05518578 is a Phase 2 safety and tolerability study in adults with treatment-resistant epilepsy. NCT06798896 is a Phase 2 double-blind, placebo-controlled study in focal onset seizures. NCT07141329 is an open-label extension study in focal onset seizures. A Phase 1 bioavailability study (NCT05102552) has been completed.

Is SPN-817 the same as other epilepsy drugs?

SPN-817 is a distinct investigational compound with a unique mechanism of action targeting acetylcholinesterase. It is not the same as other marketed epilepsy drugs, which typically work through different pathways such as sodium channels or GABA receptors. SPN-817 is being developed specifically for treatment-resistant epilepsy and focal onset seizures.