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APL-3007

Phase 2

Geographic Atrophy Secondary to Age-related Macular Degeneration | Small molecule | Ophthalmology |Apellis Pharmaceuticals, Inc.|Last Updated: Jun 24, 2026

Target and mechanism

Molecular targetC3
ModalitySmall molecule

Also known as APL-3007, pegcetacoplan (APL-2), APL-3007, pegcetacoplan

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment240

FDA Designations

No designations recorded

Clinical trial landscape

APL-3007 · 1 trial · 1 indication

Phase 2 1
NCT07215390A Phase 2, Randomized, Placebo Controlled, Multicenter, Masked Study to Evaluate the Efficacy, Safety, Tolerability, and Pharmacodynamics of Multidose APL 3007 in Combination With Syfovre/Pegcetacoplan (APL-2) in Patients Diagnosed With Geographic Atrophy Secondary to Age Related Macular DegeneratioGeographic Atrophy Secondary to Age-related Macular Degeneration
RECRUITING240 Analytics
PHASE2RECRUITING
A Phase 2, Randomized, Placebo Controlled, Multicenter, Masked Study to Evaluate the Efficacy, Safety, Tolerability, and Pharmacodynamics of Multidose APL 3007 in Combination With Syfovre/Pegcetacoplan (APL-2) in Patients Diagnosed With Geographic Atrophy Secondary to Age Related Macular Degeneratio
Geographic Atrophy Secondary to Age-related Macular DegenerationUnlock trial analytics

Study Endpoints

Primary Endpoints

Change from baseline (CFB) in the area of artificial intelligence (AI)-based SD-OCT assessment of RPE lesion in the study eye
At month 12

Secondary Endpoints

CFB in the area of AI-based OCT assessment of photoreceptor degeneration in the study eye
At month 12
Safety & tolerability based on adverse event (AE) reporting
At month 12
Safety as assessed by Best Corrected Visual Acuity (BCVA)
At Month 12
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Group 1 (APL-3007 Dose/Frequency 1 )EXPERIMENTALAPL-3007 SC + pegcetacoplan (APL-2)
Group 2 (APL-3007 Dose/Frequency 2)EXPERIMENTALAPL-3007 + pegcetacoplan (APL-2)
Group 3 (placebo)PLACEBO_COMPARATORPlacebo SC + pegcetacoplan (APL-2)

Interventions

NameTypeDescription
APL-3007, pegcetacoplan (APL-2)DRUGComplement C3 inhibitor
Placebo, SyfovreOTHERComplement C3 Inhibitor
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Eligibility Criteria

Age Range60 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites78

Inclusion Criteria: * The study eye must meet all inclusion criteria. If both eyes meet the inclusion criteria, the eye with better normal luminance visual acuity at the screening visit will be designated as the study eye. If both eyes have the same visual acuity, the right eye will be used as the ...

Countries:United States
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Recent Changes (Last 90 Days)

LOWJun 24, 2026NCT07215390primaryCompletionDate: changed
LOWJun 24, 2026NCT07215390primaryCompletionDate: changed
MEDIUMJun 22, 2026NCT07215390primaryCompletionDate: changed
MEDIUMJun 22, 2026NCT07215390primaryCompletionDate: changed

Frequently asked questions about APL-3007

What is APL-3007 used for in Geographic Atrophy Secondary to Age-related Macular Degeneration?

APL-3007 is an investigational small molecule being studied for the treatment of Geographic Atrophy Secondary to Age-related Macular Degeneration. It is currently in Phase 2 clinical development and is not yet approved by regulatory authorities.

What does APL-3007 target?

APL-3007 targets complement component C3, a protein involved in the complement cascade. By targeting C3, APL-3007 is designed to modulate the complement system, which is implicated in the progression of Geographic Atrophy Secondary to Age-related Macular Degeneration.

Who makes APL-3007?

APL-3007 is being developed by Apellis Pharmaceuticals, Inc., a biopharmaceutical company traded on the stock exchange under the ticker symbol APLS.

What phase is APL-3007 in?

APL-3007 is currently in Phase 2 clinical development. It is an investigational drug and has not been approved by the FDA or any other regulatory agency.

What clinical trials is APL-3007 in?

APL-3007 is being evaluated in a Phase 2 clinical trial with the identifier NCT07215390. This is a randomized, double-blind, placebo-controlled study enrolling approximately 240 patients with Geographic Atrophy Secondary to Age-related Macular Degeneration in the United States.

Is APL-3007 the same as pegcetacoplan?

APL-3007 is also known as pegcetacoplan (APL-2). The drug is being studied in combination with Syfovre/pegcetacoplan (APL-2) in the ongoing Phase 2 clinical trial.