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Fimepinostat

Phase 1

Diffuse Intrinsic Pontine Glioma | Small molecule | Oncology |Curis, Inc.|Last Updated: Jul 11, 2025

Target and mechanism

Molecular targetHDAC1, HDAC3, HDAC6, HDAC2, HDAC5, HDAC7, HDAC8, HDAC11, HDAC4, HDAC9, HDAC10, PIK3CA, PIK3CB, PIK3CD
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment30

FDA Designations

No designations recorded

Clinical trial landscape

Fimepinostat · 2 trials · 16 indications

Phase 1 1Early Phase 1 1
NCT01742988Study to Assess the Safety, Tolerability and Pharmacokinetics of Fimepinostat (CUDC-907) in Patients With LymphomaLymphoma
COMPLETED106 Analytics
PHASE1COMPLETED
Study to Assess the Safety, Tolerability and Pharmacokinetics of Fimepinostat (CUDC-907) in Patients With Lymphoma
LymphomaUnlock trial analytics

Study Endpoints

Primary Endpoints

To determine the maximum tolerated dose (MTD) and recommended Phase 2 dose (RP2D) of oral fimepinostat (CUDC-907) in combination with venetoclax and rituximab
At the end of cycle 1 or 2 (each cycle is 21 days)

To be evaluated in patients with relapsed and/or refractory (R/R) diffuse large B-cell lymphoma (DLBCL) or high-grade B-cell lymphoma (HGBL). Within any given study arm, the highest dose level studied at which fewer than 2 out of 6 subjects (\< 33%) experience a dose limiting toxicity (DLT).

To assess the safety and tolerability of fimepinostat in combination with anti-cancer regimens by evaluating the number of participants with adverse events assessed using the NCI Common Terminology Criteria for Adverse Events (CTCAE, v4.0).
18 months

Number of participants with adverse events assessed using the NCI Common Terminology Criteria for Adverse Events (CTCAE, v4.0).

To evaluate the efficacy of fimepinostat in combination with anti-cancer regimens by evaluating ORR
24 months

ORR assessments as measured using Lugano criteria.

To evaluate the efficacy of fimepinostat in combination with anti-cancer regimens by evaluating DOR
24 months

DOR assessments as measured using Lugano criteria.

Penetration of fimepinostat across the blood brain barrier (BBB)
During surgery or biopsy

Will be analyzed using descriptive statistics from results of fimepinostat concentrations measured within the tumor tissue collected at the time of a standard of care surgery or biopsy. Within each strata, Simon's two-stage design will be used.

Secondary Endpoints

To assess pharmacokinetics (PK) of fimepinostat when administered in combination with anti-cancer regimens as measured by area under the concentration-time curve (AUC).
Pre-dose to 21 - 28 days post dose
To assess pharmacokinetics (PK) of fimepinostat when administered in combination with anti-cancer regimens as measured by maximum plasma concentration (Cmax).
Pre-dose to 21 - 28 days post dose
To assess pharmacokinetics (PK) of fimepinostat when administered in combination with anti-cancer regimens as measured by half-life (T1/2).
Pre-dose to 21 - 28 days post dose
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Fimepinostat - Continuous Once DailyEXPERIMENTALFimepinostat 30-60 mg/day
Fimepinostat - 2x/weekEXPERIMENTALFimepinostat 60-240 mg/day
Fimepinostat - 3x/weekEXPERIMENTALFimepinostat 60-180 mg/day
Fimepinostat - 4x/weekEXPERIMENTALFimepinosta 60-180 mg/day
Fimepinostat - 5x/weekEXPERIMENTALFimepinostat 60-180 mg/day
Fimepinostat - Expansion 5x/weekEXPERIMENTALFimepinostat 60 mg on the 5 days on/2 days off
Fimepinostat - Expansion 3x/weekEXPERIMENTALFimepinostat 120 mg 3 days on/4 days off
Fimepinostat 60 mg - Combination w/ rituximabEXPERIMENTALFimepinostat 60 mg 5 days on.2 days off plus rituximab
Fimepinostat 120 mg - Combination w/ rituximabEXPERIMENTALFimepinostat 120 mg 3x/week plus rituximab
Fimepinostat - Biocomparability ArmEXPERIMENTALBiocomparability Arm
Fimepinostat 30 mg - Combination w/ venetoclaxEXPERIMENTALFimepinostat 30 mg 5 days on/2 days off plus venetoclax. Different combinations of dose levels for venetoclax will be explored
Fimepinostat 60 mg - Combination w/ venetoclaxEXPERIMENTALFimepinostat 60 mg 5 days on/2 days off plus venetoclax. Different combinations of dose levels for venetoclax will be explored
Fimepinostat - Combination w/ venetoclax and rituximabEXPERIMENTALFimepinostat and venetoclax dosed at dose levels determined for that combination. Rituximab dosed at 375 mg/m2 IV on Day 1 of each 21 day cycle
Treatment (fimepinostat, tumor resection)EXPERIMENTALPatients receive fimepinostat by mouth once daily, on Days -2 to 0. Within 2 hours of receiving fimepinostat on Day 0, patients undergo tumor resection or biopsy as part of their standard of care. MAINTENANCE PHASE: Patients receive fimepinostat by mouth, once daily for days 1-5 each week. Cycles repeat every 28 days in the absence of disease progression or unacceptable toxicity for up to 12 months from the time treatment begins. Should patients continue to derive clinical benefit, and not experience excess toxicity or progression, patients can continue to receive drug for up to 24 months or longer pending discussion with study chairs and study sponsor.

Interventions

NameTypeDescription
fimepinostatDRUG -
RituximabDRUG -
venetoclaxDRUG -
Therapeutic Conventional SurgeryPROCEDUREUndergo surgery
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: * Patients ≥ 18 years of age with any of the following: Histopathologically confirmed DLBCL or HGBL (i.e., HGBL with MYC, BCL2, and/or BCL6 rearrangements, HGBL, not otherwise specified \[NOS\], or DLBCL, NOS) that is refractory to, or has relapsed after, treatment with at least...

Countries:United StatesSwitzerland
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Recent Changes (Last 90 Days)

LOWMay 26, 2026NCT03893487primaryCompletionDate: changed
LOWMay 24, 2026NCT03893487studyFirstPostDate: changed

Frequently asked questions about Fimepinostat

What is Fimepinostat used for?

Fimepinostat is an investigational small molecule being studied for the treatment of lymphoma and diffuse intrinsic pontine glioma (DIPG). It is in Phase 1 clinical development for these oncology indications.

What does Fimepinostat target?

Fimepinostat is an inhibitor that targets multiple HDAC enzymes, including HDAC1, HDAC2, HDAC3, HDAC4, HDAC5, HDAC6, HDAC7, HDAC8, HDAC9, HDAC10, and HDAC11, as well as PIK3CA, PIK3CB, and PIK3CD.

Who makes Fimepinostat?

Fimepinostat is being developed by Curis, Inc., a biopharmaceutical company traded on NASDAQ under the ticker symbol CRIS.

What phase is Fimepinostat in?

Fimepinostat is in Phase 1 clinical development. It is an investigational drug and has not been approved by the FDA. Clinical trials are ongoing or completed to assess its safety and efficacy.

What clinical trials is Fimepinostat in?

Fimepinostat has been studied in two clinical trials. NCT01742988, a completed Phase 1 study in patients with lymphoma, enrolled 106 participants. NCT03893487, an early Phase 1 study in children and young adults with brain tumors including DIPG, is active but not recruiting.

Is Fimepinostat the same as CUDC-907?

Yes, Fimepinostat is also known as CUDC-907. In clinical trial NCT01742988, the drug is referred to as Fimepinostat (CUDC-907), confirming that these names refer to the same compound.