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ION775

Phase 2

Hypertriglyceridemia | Small molecule | Other |Ionis Pharmaceuticals, Inc.|Last Updated: Jun 1, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDDMC
Total Trials1
Total Enrollment72
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07604974A Study to Assess the Safety, Tolerability and Efficacy of ION775PHASE2 RECRUITING 72May 1, 2026Mar 1, 2028Jun 1, 20268 United States
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Study Endpoints
Primary Endpoints
Percent Change From Baseline in Fasting Triglyceride (TG)
Baseline, Month 6
Secondary Endpoints
Number of Participants With at Least One Treatment-Emergent Adverse Events (TEAEs)
Up to 12 Months
Number of Participants who Experience Abnormalities in Clinical Laboratory Evaluations
Up to 12 Months
Percent Change From Baseline in Fasting Apolipoprotein C-III (apoC-III)
Baseline, Month 6
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
ION775: Cohot AEXPERIMENTALParticipants will be randomized to receive ION775 by subcutaneous (SC) injection.
ION775: Cohot BEXPERIMENTALParticipants will be randomized to receive ION775 by SC injection.
ION775: Cohot CEXPERIMENTALParticipants will be randomized to receive ION775 by SC injection.
Interventions
NameTypeDescription
ION775DRUGION775 will be administered by SC injection.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites8

Key Inclusion Criteria: 1. Adult males and females with HTG (fasting TG more than or equal to (≥) 350 milligrams per deciliter (mg/dL) \[3.95 millimoles per liter (mmol/L)\] or with sHTG (fasting TG ≥ 500 mg/dL \[5.65 mmol/L\]). 2. Participants should be on standard of care lipid-lowering medicatio...

Countries:United States
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Recent Changes (Last 90 Days)
LOWJun 2, 2026NCT07604974lastUpdatePostDate: changed
LOWJun 2, 2026NCT07604974lastUpdatePostDate: changed
LOWJun 2, 2026NCT07604974lastUpdatePostDate: changed