Recent Updates
Recently added Catalysts

Low Dose ARD-501

Phase 2

Autism Spectrum Disorder | Small molecule | Psychiatry |Aardvark Therapeutics, Inc.|Last Updated: May 9, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment5
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06126653A Study to Evaluate ARD-501 in Patients With Autism Spectrum DisorderPHASE2 COMPLETED 5Aug 1, 2024Jan 13, 2025May 9, 20251 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Assessment of the incidence of Treatment-Emergent Adverse Events (TEAE)
Baseline to Week 5

To measure the efficacy evaluation of safety in subjects with autism spectrum disorder (ASD) by assessment of the incidence of Treatment-Emergent Adverse Events (TEAE).

Secondary Endpoints
Assessment of change in the Clinical Global Impression - Severity/Improvement (CGI-S/I) scale
Baseline to Week 5
Assessment of change on the Social Responsiveness Scale, Second Edition (SRS™-2, version-adjusted for age)
Baseline to Week 5
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelCROSSOVER
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Phase 1: Low DoseEXPERIMENTALARD-501 for 7 days at 0.2 mg/kg
Phase 2: PlaceboPLACEBO_COMPARATORPlacebo for 7 days
Phase 2: High DoseEXPERIMENTALARD-501 for 7 days at 0.5 mg/kg
Phase 2: Crossover Placebo to High DoseEXPERIMENTALARD-501 for 7 days at 0.5 mg/kg
Phase 2: Crossover High Dose to PlaceboPLACEBO_COMPARATORPlacebo for 7 days
Interventions
NameTypeDescription
Low Dose ARD-501DRUGTitratable, liquid formulation, taken orally. The intervention is given relative to the body weight of the individual. 0.2 mg/kg dosing.
High Dose ARD-501DRUGTitratable, liquid formulation, taken orally. The intervention is given relative to the body weight of the individual. 0.5 mg/kg dosing.
PlaceboDRUGTitratable, liquid formulation, taken orally.
Unlock Study Design Details
Eligibility Criteria
Age Range17 Years — 30 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion Criteria: Subjects must meet all the following criteria to be eligible for participation in this study: * Male and female subjects, 17-30 years of age * Able and willing to sign consent and comply with study protocol * Diagnostic confirmation of ASD as confirmed by gold standard clinical...

Countries:United States
Unlock Eligibility Criteria
Competitive Landscape -Autism Spectrum Disorder 17 trials