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RP-3500

Phase 1

Solid Tumor | Small molecule | Oncology |Repare Therapeutics Inc.|Last Updated: Dec 17, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment49
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05566574A Study of RP-3500 in Combination With Standard Radiation Therapy in People With Solid Tumor CancerPHASE1 ACTIVE NOT_RECRUITING 49Sep 30, 2022Sep 30, 2026Dec 17, 20257 United States
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Study Endpoints
Primary Endpoints
Phase I - Safety and Tolerability of RP-3500 in combination with radiation therapy
2 years

by assessing the grade and frequency of adverse events and serious adverse events. A dose limiting toxicity (DLT) will be graded according to NCI CTCAE v5.0.

Phase II - Assess 6 month local control rate of patients with pathogenic ATM who received RP-3500 and palliative RT
2 years

Imaging per discretion of treating physician, and may include PET, CT and MRI imaging.

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Study Design & Arms
AllocationNA
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
RP-3500 in Combination With Standard Radiation TherapyEXPERIMENTALPatients with metastatic cancers with identified mutations in ATM will be enrolled. All patients will receive a standard palliative RT (4Gy x 5 fractions) on Days 1-5 in combination with RP-3500 on Days 1-5. In the first phase of the study, a 3+3 study design will be used to identify a safe dose of RP-3500 (starting at 80 mg QD) in combination with palliative RT.
Pilot subcohortEXPERIMENTALThe primary objective is to assess 6 month local control rate of patients of new metastatic lesions with pathogenic ATM who haves received prior RP-3500 and palliative RT.
Interventions
NameTypeDescription
RP-3500DRUGRP-3500 on Days 1-5.
External Beam Radiotherapy (EBRT)RADIATIONPalliative radiation therapy (4Gy x 5 fractions) to a metastatic site on Days 1-5
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites7

Inclusion Criteria: * Histologically confirmed malignancy with at least one metastatic lesion amenable to radiotherapy. Bone, visceral, and soft tissue are eligible. * Mutation in ATM (deleterious or VUS; somatic or germline; monoallelic or biallelic) * Note: Homozygous Deletion in the ATM gene ...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT05566574studyFirstPostDate: changed