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PF-06463922

Phase 1

ALK-positive Non Small Cell Lung Cancer (NSCLC) and ROS1-positive NSCLC | Small molecule | Oncology |Pfizer, Inc.|Last Updated: Aug 12, 2024

Target and mechanism

Molecular targetALK, EML4
Target classInhibitor
ModalitySmall molecule

Also known as Lorlatinib, Lorlatanib

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment364

FDA Designations

No designations recorded

Clinical trial landscape

PF-06463922 · 5 trials · 2 indications

Phase 1 5
NCT02838264A Study To Evaluate The Effect Of Itraconazole On Pharmacokinetics Of PF-06463922 In Healthy VolunteersHealthy
COMPLETED16 Analytics
NCT02804399A Study To Evaluate The Effect Of Rifampin On Pharmacokinetics Of PF-06463922 In Healthy VolunteersHealthy
COMPLETED12 Analytics
NCT02569554PPI And Food Effect Study For PF-06463922 In Healthy VolunteersHealthy
COMPLETED27 Analytics
NCT02564562A Study To Investigate The Absorption, Distribution, Metabolism, And Excretion Of [14c]PF-06463922 In Healthy Male VolunteersHealthy
COMPLETED6 Analytics
NCT01970865A Study Of PF-06463922 An ALK/ROS1 Inhibitor In Patients With Advanced Non Small Cell Lung Cancer With Specific Molecular AlterationsALK-positive Non Small Cell Lung Cancer (NSCLC) and ROS1-positive NSCLC
COMPLETED364 Analytics
PHASE1COMPLETED
A Study To Evaluate The Effect Of Itraconazole On Pharmacokinetics Of PF-06463922 In Healthy Volunteers
HealthyUnlock trial analytics
PHASE1COMPLETED
A Study To Evaluate The Effect Of Rifampin On Pharmacokinetics Of PF-06463922 In Healthy Volunteers
HealthyUnlock trial analytics
PHASE1COMPLETED
PPI And Food Effect Study For PF-06463922 In Healthy Volunteers
HealthyUnlock trial analytics
PHASE1COMPLETED
A Study To Investigate The Absorption, Distribution, Metabolism, And Excretion Of [14c]PF-06463922 In Healthy Male Volunteers
HealthyUnlock trial analytics
PHASE1COMPLETED
A Study Of PF-06463922 An ALK/ROS1 Inhibitor In Patients With Advanced Non Small Cell Lung Cancer With Specific Molecular Alterations
ALK-positive Non Small Cell Lung Cancer (NSCLC) and ROS1-positive NSCLCUnlock trial analytics

Study Endpoints

Primary Endpoints

AUCinf for PF-06463922
PF-06463922 pre-dose, 0.5, 1, 1.5, 2, 4, 6, 8, 12, 24, 48, 72, 96, 120, 144, and up to 168 hours post-dose.

Area under the plasma concentration-time profile from time zero extrapolated to infinite time

Cmax for PF-06463922
PF-06463922 pre-dose, 0.5, 1, 1.5, 2, 4, 6, 8, 12, 24, 48, 72, 96, 120, 144, and up to 168 hours post-dose.

Maximum plasma concentration

Plasma AUCinf for PF-06463922 Given Alone and With Rifampin
Predose, 0.5, 1, 1.5, 2, 4, 6, 12, 24, 36, 48, 60, 72, 96, 120 hours postdose on Day 1 after PF-06463922 100 mg administration in Period 1, and at the same time points on Day 8 after PF-06463922 100 mg with rifampin administration in Period 2.

AUCinf is the plasma area under the plasma concentration-time profile from time 0 extrapolated to infinite time. The pharmacokinetics (PK) parameter analysis population was defined as all participants enrolled and treated who have at least 1 of the PF-06463922 PK parameters of primary interest in at least 1 treatment period.

Plasma Cmax for PF-06463922 Given Alone and With Rifampin
Predose, 0.5, 1, 1.5, 2, 4, 6, 12, 24, 36, 48, 60, 72, 96, 120 hours postdose on Day 1 after PF-06463922 100 mg administration in Period 1, and at the same time points on Day 8 after PF-06463922 100 mg with rifampin administration in Period 2.

Cmax is the maximum observed plasma concentration. PK parameter analysis population was defined as all participants enrolled and treated who have at least 1 of the PF-06463922 PK parameters of primary interest in at least 1 treatment period.

plasma AUCinf for PF-06463922
3 months

area under plasma concentration-time profile from time 0 extrapolated to infinite time for PF-06463922

plasma Cmax for PF-06463922
3 months

observed maximal plasma PF-06463922 concentration

Mass Balance
14 days

Mass balance: Cumulative recovery (%) of total radioactivity in urine and feces.

Metabolic profiling / metabolite identification in plasma, urine, and fecal samples
14 days
AUCinf
14 days

Area Under the Curve From Time Zero to Extrapolated Infinite Time

AUClast
14 days

Area under the plasma concentration time profile from time 0 to the time of the last quantifiable concentration (Clast)

kel
14 days

Elimination rate constant

Cmax
14 days

Maximum observed plasma concentration

Tmax
14 days

Time for Cmax

t1/2
14 days

Terminal elimination half life

CL/F
14 days

Apparent oral clearance

Ae
14 days

Total amount of unchanged drug excreted in the urine from time 0 to discharge day

Ae%
14 days

Total amount of unchanged drug excreted in the urine from time 0 to infinity expressed as percent of dose

Clr
14 days

Renal Clearance

Crbc
14 days

Total radioactivity in RBCs

Vz/F
14 days

Apparent volume of distribution following oral administration

Number of Participants With Cycle 1 Dose-Limiting Toxicities (DLTs) in Phase 1
Cycle 1 (21 days)

DLT: any of following adverse events (AEs) attributable to PF-06463922: (1) hematologic: grade 4 neutropenia for \>7 days; febrile neutropenia; grade\>=3 neutropenic infection; grade\>=3 thrombocytopenia with bleeding; grade 4 thrombocytopenia; (2) non-hematologic: grade\>=3 pancreatitis; grade\>=3 toxicities (excluding grade \>=3 laboratory abnormalities not requiring dose modifications) persisting after optimal treatment with standard medical therapy; symptomatic grade \>=3 QT interval corrected for heart rate (QTc) prolongation, or asymptomatic grade \>=3 prolongation that had been confirmed by repeat testing, re-evaluation by qualified person, persisted after correction of reversible causes; \>=20% decrease from baseline in left ventricular ejection fraction (LVEF); (3) other: failure to deliver at least 16 out of 21 prescribed daily total dose due to toxicities attributable to study drug; failure to restart dosing after 21 days (1 cycle) delay due to toxicity attributable to study drug.

Percentage of Participants With Overall and Intracranial Objective Response (Phase 2)
3 years

Objective response (OR) refers to confirmed complete response (CR) or partial response (PR) according to Response Evaluation Criteria in Solid Tumor (RECIST) version 1.1. Intracranial OR refers to confirmed CR or PR considering only lesions within brain. CR was defined as the disappearance of all non-lymph node target lesions (where all target lesions are recorded with a length of 0 milliliter (mm) on Target Lesions electronic case report form (eCRF). Any pathological lymph nodes (recorded as target lesion) must have reduction in short axis to \<10 mm. PR was defined as a 30 percent (%) or more decrease in sum of lesion dimensions (SLD) of target lesions, taking as reference the baseline SLD. Results presented here were based on independent central review.

Secondary Endpoints

AUClast for PF-06463922
PF-06463922 pre-dose, 0.5, 1, 1.5, 2, 4, 6, 8, 12, 24, 48, 72, 96, 120, 144, and up to 168 hours post-dose.
Tmax for PF-06463922
PF-06463922 pre-dose, 0.5, 1, 1.5, 2, 4, 6, 8, 12, 24, 48, 72, 96, 120, 144, and upto 168 hours post-dose.
t1/2 for PF-06463922
PF-06463922 pre-dose, 0.5, 1, 1.5, 2, 4, 6, 8, 12, 24, 48, 72, 96, 120, 144, and up to 168 hours post-dose.
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Study Design & Arms

MaskingNONE
PurposeBASIC_SCIENCE

Treatment Arms

ArmTypeDescription
Cohort 1EXPERIMENTALAll subjects in this cohort will receive the same dose of PF-06463922 in both periods. Subjects will receive PF-06463922 Alone in Period 1 followed by PF-06463922 with Itraconazole in Period 2.
Cohort 2EXPERIMENTALAll subjects in this cohort will receive the same dose of PF-06463922 in both periods. Subjects will receive PF-06463922 Alone in Period 1 followed by PF-06463922 with Itraconazole in Period 2.
Cohort 3EXPERIMENTALAll subjects in this cohort will receive the same dose of PF-06463922 in both periods. Subjects will receive PF-06463922 Alone in Period 1 followed by PF-06463922 with Itraconazole in Period 2.
Cohort 4EXPERIMENTALAll subjects in this cohort will receive the same dose of PF-06463922 in both periods. Subjects will receive the highest safe dose (mg) of PF-06463922 as a single-dose Alone in Period 1 followed by PF-06463922 with Itraconazole in Period 2.
all subjectsEXPERIMENTALsubjects will receive a 100 mg single oral dose of PF-06463922 followed by a 100 mg single dose of PF-06463922 combined with 600 mg QD dose of rifampin with at least 10 days of washout period between two PF-06463922 doses.
PF-06463922EXPERIMENTALeach subject will receive four single doses of PF-06463922 without food, with food, with rabeprazole (without food), and one of the two new formulations without food.
TreatmentEXPERIMENTALRadiolabeled PF-06463922 in healthy volunteers
CrizotinibOTHERALK+ NSCLC patients who are treatment naïve may be eligible to receive crizotinib following PF-06463922 as a substudy to the main study.

Interventions

NameTypeDescription
PF-06463922DRUGSingle oral dose of PF-06463922 50 mg on Day 1 of Period 1 and Day 5 of Period 2
ItraconazoleDRUG200 mg oral dose of itraconazole on Days 1 to 11 during Period 2
rifampinDRUG600 mg QD from day 1 to day 12 in period 2.
rabeprazoleDRUG20 mg daily tablets in the evening for 5 days and Pf-06463922 on the morning of day 6 in treatment C.
[14C] PF-06463922DRUGSingle oral dose of 100mg PF-06463922 + \[14C\] PF-06463922
CrizotinibDRUGOral, starting dose of 250 mg BID continuous daily dosing every 21 days
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Eligibility Criteria

Age Range18 Years to 55 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: * Healthy female subjects of non childbearing potential and/or male subjects, who at the time of screening, are between the ages of 18 and 55 years, inclusive. * Body Mass Index (BMI) of 17.5 to 30.5 kg/m2; and a total body weight \>50 kg (110 lbs). Exclusion Criteria: * Evide...

Countries:BelgiumUnited StatesAustraliaCanadaFranceGermanyHong KongItalyJapanSingaporeSouth KoreaSpainSwitzerlandTaiwan
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Frequently asked questions about PF-06463922

What is Lorlatinib used for?

Lorlatinib is an investigational small molecule kinase inhibitor being studied for use in ALK-positive anaplastic large cell lymphoma, ALK-positive non-small cell lung cancer (NSCLC), ROS1-positive NSCLC, and moderate hepatic impairment. It is currently in Phase 1 clinical development and is not yet approved by the FDA.

What does Lorlatinib target?

Lorlatinib targets kinases, as it belongs to the -tinib class of kinase inhibitors. It is being investigated for conditions involving ALK and ROS1 alterations, including ALK-positive anaplastic large cell lymphoma and ALK-positive or ROS1-positive non-small cell lung cancer.

Who makes Lorlatinib?

Lorlatinib is being developed by Pfizer, Inc., which trades under the ticker symbol PFE on the New York Stock Exchange. The company is conducting clinical trials to evaluate the drug's safety and pharmacokinetics in healthy volunteers and patient populations.

What phase is Lorlatinib in?

Lorlatinib is in Phase 1 clinical development. All four clinical trials listed for the drug are Phase 1 studies, and none have progressed to later phases. Lorlatinib remains investigational and has not received FDA approval for any indication.

What clinical trials is Lorlatinib in?

Lorlatinib has been studied in four Phase 1 clinical trials: NCT02564562, NCT02804399, NCT02838264, and NCT03961997. These trials evaluated the drug's absorption, distribution, metabolism, and excretion, as well as its interactions with rifampin, itraconazole, and modafinil in healthy volunteers.

Is Lorlatinib the same as Lorlatanib?

Yes, Lorlatinib is also known as Lorlatanib. Both names refer to the same investigational drug being developed by Pfizer for ALK-positive and ROS1-positive cancers. Researchers and clinicians may use either spelling when referring to this compound.