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Brigatinib

Phase 2

Neurofibromatosis Type 2 | Small molecule | Other |Incyte Corporation|Last Updated: May 6, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment109
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04374305Innovative Trial for Understanding the Impact of Targeted Therapies in NF2-Related Schwannomatosis (INTUITT-NF2)PHASE2 RECRUITING 109Jun 20, 2020Dec 1, 2030May 6, 20266 United States
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Study Endpoints
Primary Endpoints
Radiographic response rate (for each drug substudy)
2 years

Radiographic response rates in target tumors according to tumor-associated criteria: * VS, non-VS, and meningiomas: Dombi criteria (2013) * Ependymomas: RECIST 1.12

Secondary Endpoints
Incidence of Treatment-Emergent Adverse Events [Safety and Tolerability
2 years
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Sub-study A (brigatinib) - CLOSED TO ENROLLMENTEXPERIMENTALSubjects treated in this arm will receive brigatinib 90 mg by mouth daily for 7 days and then increased to 180 mg by mouth daily if the drug is tolerated.
Sub-study B (neratinib)EXPERIMENTALThe first three participants treated in this arm will receive neratinib 200 mg mg by mouth daily. If these participants tolerate the medication well, subsequent participants will receive neratinib 240 mg by mouth daily.
Experimental: sub-study C (retifanlimab plus bevacizumab)EXPERIMENTALSubjects on this arm will receive retifanlimab by IV infusion at a dose of 375 mg every 3 weeks on a continuous schedule for 48 weeks. Subjects will also receive bevacizumab by IV infusion at a dose of 7.5 mg/kg every 3 weeks on an intermittent schedule. One cycle last 42 days and the study will last for 52 total weeks (48 treatment weeks and 4 follow-up weeks).
Interventions
NameTypeDescription
BrigatinibDRUGOral daily per predetermined dosage per protocol.
NeratinibDRUGOral daily per predetermined dosage per protocol.
RetifanlimabDRUGEvery 3 weeks by IV per predetermined dose in protocol.
BevacizumabDRUGEvery 3 weeks by IV per predetermined dose in protocol.
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Eligibility Criteria
Age Range12 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites6

Eligibility Specific For MASTER PROTOCOL: Inclusion Criteria: \- Patients must have a pathogenic variant in the NF2 gene (either in the germline or in two NF2-related tumors) OR a confirmed diagnosis of NF2 by fulfilling National Institute of Health (NIH) criteria or Manchester criteria: The NIH ...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT04374305primaryCompletionDate: changed
LOWMay 24, 2026NCT04374305studyFirstPostDate: changed