Recent Updates
Recently added Catalysts

OCU410

Phase 3

Dry Age-related Macular Degeneration | Monoclonal antibody | Ophthalmology |Ocugen, Inc.|Last Updated: Aug 19, 2026

Target and mechanism

Molecular targetRORA
ModalityMonoclonal antibody

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedNO_TREATMENT_CONTROLLEDDMC
Total Trials1
Total Enrollment237

FDA Designations

ORPHAN_DRUGRARE_PEDIATRIC_DISEASERMAT

Clinical trial landscape

OCU410 · 2 trials · 2 indications

Phase 3 1Phase 1 1
NCT07770828Phase 3 Study to Assess Efficacy, Safety & Tolerability of OCU410 For Geographic Atrophy Secondary to Dry AMDDry Age-related Macular Degeneration
RECRUITING237 Analytics
PHASE3RECRUITING
Phase 3 Study to Assess Efficacy, Safety & Tolerability of OCU410 For Geographic Atrophy Secondary to Dry AMD
Dry Age-related Macular DegenerationUnlock trial analytics

Study Endpoints

Primary Endpoints

Rate of change (slope) of square root-transformed GA lesion area from baseline to Month 12
Month 12

Rate of change (slope) of square root-transformed GA lesion area (√mm²/year) from baseline to Month 12 in treated eyes compared to control eyes as assessed by fundus autofluorescence (FAF) measurements

Safety (Participants With Ocular and Non-ocular AEs (Adverse Events) and SAEs (Serious Adverse Events))
12 months (Screening to 12 months post OCU410 administration)

The primary endpoint is safety, determined by the number of ocular and non-ocular Study Drug-related adverse events (SDAE), treatment-emergent adverse events (TEAEs) and serious adverse events (SAEs).

Change in anatomy of ocular structures using Slit Lamp Biomicroscopy
12 months (Screening to 12 months post OCU410 administration)

We will use Slit-lamp Biomicroscopy to visualize the anatomy of ocular structures before and after sub-retinal injections and follow-up visits.

Change in anatomy of ocular structures using Indirect ophthalmoscopy
12 months (Screening to 12 months post OCU410 administration)

We will use Indirect ophthalmoscopy to visualize the anatomy of ocular structures before and after sub-retinal injections and follow-up visits.

Change from baseline in BCVA (Best Corrected Visual Acuity)
12 months (Screening to 12 months post OCU410 administration)

Visual function of the study eye was assessed using the Early Treatment Diabetic Retinopathy Study (ETDRS) Best Corrected Visual Acuity (BCVA) letter score. A higher score represents better vision.

Change in Low Luminance Visual Acuity
12 months (Screening to 12 months post OCU410 administration)

Measured by letter score. A higher score represents better vision

Change in the Intraocular Pressure (mmHg)
12 months (Screening to 12 months post OCU410 administration)

Measured by applanation or rebound tonometry with confirmation with Goldmann tonometer if IOP is outside normal range (8-21mmHg).

Secondary Endpoints

Proportion of subjects experiencing a low-luminance visual acuity (LLVA) ≥15 Letter Loss from Baseline to M12
Month 12
Rate of change of ellipsoid zone (EZ) area loss at Month 12
Month 12
Humoral and cellular immune response
12 months (Screening to 12 months post OCU410 administration)
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingSINGLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
OCU410EXPERIMENTALOCU410 Single Sub Retinal Injection, 200 µL, 1×10\^10 vg/eye
Untreated Control ArmNO_INTERVENTIONControl Arm (Untreated)
Phase1 Dose Escalation- Low Dose (2.5×10E10 vg/mL):EXPERIMENTALLow Dose (2.5×10E10 vg/mL): Subjects will receive a subretinal injection of OCU410 in the low dose concentration.
Phase1 Dose Escalation- Medium Dose (5×10E10 vg/mL):EXPERIMENTALMedium Dose (5×10E10 vg/mL): Subjects will receive a subretinal injection of OCU410 in the medium dose concentration.
Phase1 Dose Escalation- High Dose (1.5×10E11 vg/mL):EXPERIMENTALHigh Dose (1.5×10E11 vg/mL): Subjects will receive a subretinal injection in the high dose concentration.
Phase 2 Dose Expansion: Maximum tolerated dose (MTD) from Phase 1-Randomized ArmEXPERIMENTALMaximum tolerated dose (MTD) from Phase 1: Subjects will receive a subretinal injection in the MTD concentration.
Phase 2 Dose Expansion: Lower Dose from Phase 1-Randomized ArmEXPERIMENTALSubjects will receive a subretinal injection of OCU410 in a Lower Dose concentration.
Control ArmNO_INTERVENTIONNo Intervention Control Arm: Subject will not receive any active study intervention

Interventions

NameTypeDescription
OCU410BIOLOGICALSubretinal Injection
Unlock Study Design Details

Eligibility Criteria

Age Range55 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites3

Inclusion Criteria: 1. Subjects 55 years of age or older at consent. 2. BCVA of ≥25 ETDRS letters or more using Early Treatment Diabetic Retinopathy Study (ETDRS) chart (20/320 Snellen Equivalent) and ≤80 ETDRS Letters (20/25 Snellen Equivalent) in the study eye. 3. Fundus autofluorescence (FAF) im...

Countries:United States
Unlock Eligibility Criteria

Recent Changes (Last 90 Days)

LOWAug 20, 2026NCT07770828lastUpdatePostDate: changed
LOWAug 20, 2026NCT07770828lastUpdatePostDate: changed
LOWAug 20, 2026NCT07770828lastUpdatePostDate: changed
LOWAug 20, 2026NCT07770828lastUpdatePostDate: changed
LOWAug 19, 2026NCT07770828NEW_TRIAL: changed
LOWAug 19, 2026NCT07770828NEW_TRIAL: changed
LOWAug 19, 2026NCT07770828NEW_TRIAL: changed
MEDIUMJul 31, 2026NCT06018558primaryCompletionDate: changed
MEDIUMJul 31, 2026NCT06018558primaryCompletionDate: changed

Frequently asked questions about OCU410

What is OCU410 used for?

OCU410 is an investigational therapy being developed for geographic atrophy and dry age-related macular degeneration. It is currently in Phase 3 clinical development and has not been approved by the FDA. The drug is being studied in patients with these retinal conditions.

What does OCU410 target?

OCU410 is a monoclonal antibody being developed by Ocugen, Inc. for geographic atrophy and dry age-related macular degeneration. As a monoclonal antibody, it is designed to bind to a specific target involved in the disease process, though the exact molecular target has not been disclosed.

Who makes OCU410?

OCU410 is being developed by Ocugen, Inc., a biopharmaceutical company. Ocugen is conducting clinical trials to evaluate the safety and efficacy of OCU410 for geographic atrophy and dry age-related macular degeneration.

What phase is OCU410 in?

OCU410 is currently in Phase 3 clinical development. It is being studied in a Phase 3 trial for dry age-related macular degeneration, and it has also completed a Phase 1 trial for geographic atrophy. OCU410 is investigational and not yet approved by the FDA.

What clinical trials is OCU410 in?

OCU410 is being evaluated in two clinical trials. NCT06018558 is a Phase 1 study in geographic atrophy with 60 participants, which is active but not recruiting. NCT07770828 is a Phase 3 study in dry age-related macular degeneration with 237 participants, which is currently recruiting.

Is OCU410 the same as any other drug?

OCU410 is a distinct investigational drug developed by Ocugen, Inc. It is not known to be the same as any other approved or marketed medication. It is being studied specifically for geographic atrophy and dry age-related macular degeneration.