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RFB002

Phase 2

Diabetic Macular Edema | Small molecule | Ophthalmology |Novartis AG|Last Updated: Mar 3, 2017

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment83
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00901186Efficacy and Safety of Ranibizumab (Intravitreal Injections) Versus Laser Treatment in Patients With Visual Impairment Due to Diabetic Macular EdemaPHASE2 COMPLETED 83Nov 1, 2009Aug 1, 2012Mar 3, 201717 Spain
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Study Endpoints
Primary Endpoints
Mean Change From Baseline in Best Corrected Visual Acuity (BCVA)
Baseline, 12 months

Visual acuity (VA) was assessed on the study eye during every study visit using best correction determined from protocol refraction. VA measurements were performed with the patient in a sitting position using Early Treatment Diabetic Retinopathy Study (ETDRS)-like visual acuity testing charts at a testing distance of 4 meters.

Secondary Endpoints
Percentage of Participants With Improvement in BCVA
12 months
Evolution of Mean Change From Baseline in BCVA by Study Visit
Baseline, Months 1, 2, 3, 4, 5, 6, 7, 8, 9, 10, 11, 12
Percentage of Participants With VA > 73 Letters With Ranibizumab (0.5 mg) vs Laser.
12 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
RFB002EXPERIMENTALRFB002 0.5 mg was administered to the study eye with a single monthly intravitreal injection on day 1, day 30 and day 60. After day 90, if stable vision was not achieved, a monthly injection of RFB002 0.5 mg was administered until stable vision was achieved.
Laser photocoagulationACTIVE_COMPARATORAt least one treatment of laser photocoagulation was applied on day 1. The maximum number of laser photocoagulation treatments was 4.
Interventions
NameTypeDescription
RFB002DRUG0.5 mg
Laser photocoagulationPROCEDURE -
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites17

Inclusion Criteria: 1. Diabetes mellitus 1 or 2, HbA1c \< 11.0%, With: Clinically significant Diabetic Macular Edema in at least one eye. 2. Previous treatment with macular photocoagulation only should be considered if the investigator believes that the study eye may possibly benefit from additiona...

Countries:Spain
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