Recent Updates
Recently added Catalysts

NL-201

Phase 1

Solid Tumor | Small molecule | Oncology |Neurogene Inc.|Last Updated: Oct 1, 2024

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

CONTROLLEDDMC
Total Trials1
Total Enrollment59

FDA Designations

No designations recorded

Clinical trial landscape

NL-201 · 1 trial · 2 indications

Phase 1 1
NCT04659629NL-201 Monotherapy and in Combination With Pembrolizumab in Patients With Relapsed or Refractory CancerSolid Tumor
COMPLETED59 Analytics
PHASE1COMPLETED
NL-201 Monotherapy and in Combination With Pembrolizumab in Patients With Relapsed or Refractory Cancer
Solid TumorUnlock trial analytics

Study Endpoints

Primary Endpoints

Recommended phase 2 dose (RP2D) for NL-201 (Parts 1 and 2)
Up to Day 33

Evaluation of tolerability of NL-201 as measured by number of subjects with dose limiting toxicities (DLTs)

Recommended dose schedule for NL-201 (Parts 1 and 2)
Up to Day 33

Evaluation of tolerability of NL-201 as measured by number of subjects with dose limiting toxicities (DLTs)

Recommended phase 2 dose (RP2D) for NL-201 in combination with Pembrolizumab (Parts 3 and 4)
Up to Day 33

Evaluation of tolerability of NL-201 in combination with Pembrolizumab as measured by number of subjects with dose limiting toxicities (DLTs)

Recommended dose schedule for NL-201 in combination with Pembrolizumab (Parts 3 and 4)
Up to Day 33

Evaluation of tolerability of NL-201 in combination with Pembrolizumab as measured by number of subjects with dose limiting toxicities (DLTs)

Incidence of treatment-emergent adverse events
Up to Day 33

Rate of adverse events in patients with advanced solid tumors

Severity of treatment-emergent adverse events
Up to Day 33

Rate of adverse event grades in patients with advanced solid tumors

Secondary Endpoints

Best Objective Response according to RECIST version 1.1
Up to 36 months
Objective Response Rate (ORR) according to RECIST version 1.1
Up to 36 months
Progression-Free Survival (PFS) according to RECIST version 1.1
Up to 36 months
Unlock Study Endpoints

Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Part 1: NL-201 Monotherapy Dose EscalationEXPERIMENTALNL-201 given as monotherapy by intravenous administration testing ascending doses and two different schedules.
Part 2: NL201 Monotherapy Expansion CohortsEXPERIMENTALNL-201 given as monotherapy by intravenous administration in indication specific cohorts at a dose and schedule determined in Part 1.
Part 3: NL-201 in Combination with Pembrolizumab Dose EscalationEXPERIMENTALNL-201, in combination with a set Pembrolizumab dose, testing ascending doses and two different schedules
Part 4: NL-201 in Combination with Pembrolizumab Expansion CohortsEXPERIMENTALNL-201 in combination with Pembrolizumab in indication specific cohorts at a dose and schedule determined in Part 3

Interventions

NameTypeDescription
NL-201DRUGNL-201 is a de novo protein therapeutic.
Pembrolizumab Injection [Keytruda]DRUGA programmed death receptor-1 (PD-1)-blocking antibody
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites8

Inclusion Criteria: * Patients with measurable disease * Patients with Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1 * At least 6 weeks from any prior nitrosurea or mitomycin C therapy; at least 4 weeks from any other prior chemotherapy or checkpoint inhibitor; at least 2 w...

Countries:United StatesAustraliaCanada
Unlock Eligibility Criteria

Competitive Landscape -Other Solid Tumors 9 trials (matched to "Solid Tumor")

Frequently asked questions about NL-201

What is NL-201 used for?

NL-201 is an investigational small molecule being developed for the treatment of solid tumors, including advanced solid tumors. It is studied in patients with relapsed or refractory cancer. The drug is currently in clinical development and is not approved by the FDA.

Who makes NL-201?

NL-201 is developed by Neurogene Inc., a biopharmaceutical company. Neurogene's stock is traded under the ticker symbol NGNE. The company is conducting clinical trials to evaluate the safety and efficacy of NL-201 in patients with solid tumors.

What phase is NL-201 in?

NL-201 is in Phase 1 clinical development. It is an investigational drug, meaning it has not been approved by regulatory authorities. The Phase 1 trial has been completed, and the drug is no longer in active clinical trials.

What clinical trials is NL-201 in?

NL-201 was studied in a Phase 1 clinical trial with the identifier NCT04659629. The trial evaluated NL-201 as a monotherapy and in combination with pembrolizumab in patients with relapsed or refractory cancer. The study enrolled 59 participants and has been completed.

Is NL-201 the same as pembrolizumab?

No, NL-201 is not the same as pembrolizumab. NL-201 is an investigational small molecule developed by Neurogene Inc., while pembrolizumab is an approved immunotherapy drug. In the clinical trial NCT04659629, NL-201 was studied both alone and in combination with pembrolizumab.