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Abemaciclib

Phase 2

CDK Gene Mutation | Small molecule | Oncology |Kazia Therapeutics Limited|Last Updated: Apr 13, 2026

Target and mechanism

Molecular targetCDK6, CDK4
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment50

FDA Designations

No designations recorded

Clinical trial landscape

Abemaciclib · 1 trial · 7 indications

Phase 2 1
NCT03994796Genetic Testing in Guiding Treatment for Patients With Brain MetastasesCDK Gene Mutation
ACTIVE NOT_RECRUITING50 Analytics
PHASE2ACTIVE NOT_RECRUITING
Genetic Testing in Guiding Treatment for Patients With Brain Metastases
CDK Gene MutationUnlock trial analytics

Study Endpoints

Primary Endpoints

Objective response rate in the brain
Up to 5 years

Assessed per Response Assessment in Neuro-Oncology (RANO) criteria for brain metastases. The response rate is defined as the number of patients who have achieved complete response (CR) or partial response (PR) per RANO for brain metastases criteria during treatment with CDK, PI3K, NTRK/ROS, or KRAS G12C inhibitors divided by total number of evaluable patients. The response rate and associated exact confidence interval will be estimated within each cohort defined by the targeted agent and histology.

Secondary Endpoints

Systemic response for extracranial disease
Up to 5 years
Clinical benefit rate for central nervous system (CNS)
Up to 5 years
Clinical benefit rate for extracranial disease
Up to 5 years
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Arm I (CDK gene mutation)EXPERIMENTALPatients receive abemaciclib PO BID on days 1-28. Cycles repeat every 28 days in the absence of disease progression or unacceptable toxicity.
Arm II (PI3K gene mutation)EXPERIMENTALPatients receive PI3K inhibitor paxalisib PO QD on days 1-28. Cycles repeat every 28 days in the absence of disease progression or unacceptable toxicity.
Arm III (NTRK/ROS1 gene mutation)EXPERIMENTALPatients receive entrectinib PO QD on days 1-28. Cycles repeat every 28 days in the absence of disease progression or unacceptable toxicity.
Arm IV (KRAS G12C mutation)EXPERIMENTALPatients receive adagrasib (MRTX849) PO BID on days 1-28. Cycles repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Interventions

NameTypeDescription
AbemaciclibDRUGGiven PO
PI3K Inhibitor paxalisibDRUGGiven PO
EntrectinibDRUGGiven PO
AdagrasibDRUGGiven PO
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites435

Inclusion Criteria: PRE-REGISTRATION ELIGIBILITY CRITERIA (ALL PATIENTS) • Tissue available for biomarker testing (any brain metastasis tissue and extracranial site from any prior resection or biopsy). REGISTRATION ELIGIBILITY CRITERIA (ALL PATIENTS) * Participants must have histologically confir...

Countries:United States
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Competitive Landscape -Genetic Mutations 6 trials (matched to "CDK Gene Mutation")

Frequently asked questions about Abemaciclib

What is Abemaciclib used for in CDK Gene Mutation?

Abemaciclib is an investigational small molecule being studied for use in patients with CDK gene mutations, including those with brain metastases and metastatic solid neoplasms. It is currently in Phase 2 clinical development for this oncology indication.

What does Abemaciclib target?

Abemaciclib targets CDK4 and CDK6, which are cyclin-dependent kinases involved in cell cycle regulation. As a CDK inhibitor, it is designed to interfere with the activity of these targets in cancer cells.

Who is developing Abemaciclib?

Abemaciclib is being developed by Kazia Therapeutics Limited, a biopharmaceutical company listed on the NASDAQ under the ticker symbol KZIA. The company is conducting clinical trials to evaluate the drug's potential in oncology.

What phase is Abemaciclib in?

Abemaciclib is currently in Phase 2 clinical development. It is an investigational drug and has not yet been approved by regulatory authorities. The ongoing Phase 2 trial is active but not recruiting participants.

What clinical trials is Abemaciclib in?

Abemaciclib is being evaluated in the clinical trial NCT03994796, titled 'Genetic Testing in Guiding Treatment for Patients With Brain Metastases.' This Phase 2 study is enrolling approximately 50 patients in the United States with CDK gene mutations and other genetic alterations.

Is Abemaciclib the same as any other drug?

Abemaciclib is also known by the ChEMBL identifier CHEMBL3301610. This identifier is used in chemical and biological databases to track the compound. No other alternative names have been established for this drug.