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PAS-004

Phase 1

RAS Mutation | Small molecule | Oncology |Pasithea Therapeutics Corp.|Last Updated: Dec 4, 2025

Success Probability
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Market & Valuation
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Trial Design
CONTROLLED
Total Trials1
Total Enrollment48
FDA Designations
FAST_TRACKRARE_PEDIATRIC_DISEASEORPHAN_DRUG
Clinical trial landscape

PAS-004 · 2 trials · 8 indications

Phase 1 2
NCT06961565PAS-004 in Adults Who Have Neurofibromatosis Type 1 With Plexiform NeurofibromasNF1 Mutation
RECRUITING56 Analytics
NCT06299839PAS-004 in Patients With Advanced Solid TumorsRAS Mutation
RECRUITING48 Analytics
PHASE1RECRUITING
PAS-004 in Adults Who Have Neurofibromatosis Type 1 With Plexiform Neurofibromas
NF1 MutationUnlock trial analytics
PHASE1RECRUITING
PAS-004 in Patients With Advanced Solid Tumors
RAS MutationUnlock trial analytics
Study Endpoints
Primary Endpoints
Part A: To evaluate the safety and tolerability of PAS-004 when administered for one 28-day treatment cycle
Part A from enrollment (Day 1) through Day 28 (completion of Cycle 1)

Endpoint/Outcome Measures: Number of participants with dose-limiting toxicities (DLTs), with Adverse Events (AEs), AEs leading to interruption or discontinuation of study drug, with clinically significant findings on clinical laboratory tests, with abnormal cardiac and visual function exams using the Common Terminology Criteria for Adverse Events (CTCAE Version 5).

Part B: To evaluate the safety and tolerability of PAS-004 when administered for six 28-day treatment cycle
Part B from enrollment (Day 1) through Day 168 (completion of Cycle 6) [each cycle is 28 days]

Endpoint/Outcome Measures: Number of participants with dose-limiting toxicities (DLTs), with Adverse Events (AEs), AEs leading to interruption or discontinuation of study drug, with clinically significant findings on clinical laboratory tests, with abnormal cardiac and visual function exams using the Common Terminology Criteria for Adverse Events (CTCAE Version 5).

Evaluation of dose limiting toxicities (DLTs)
Day 1 through Day 35 (Cycle 1)

Pre-defined DLTs will be assessed for dose escalation and expansion determinations.

Evaluation of adverse events (AEs)
Screening through Day 1 through Day 35 (Cycle 1), and 30 days after discontinuation of study drug

The number and severity of AEs will be evaluated for dosing cohorts to inform dose escalation and expansion decisions, and support selection of a preliminary recommended phase 2 dose (RP2D).

Evaluation of AEs leading to discontinuation of investigational product (IP), PAS-004.
Screening through Day 1 through Day 35 (Cycle 1), and 30 days after discontinuation of study drug

The number and severity of AEs leading to discontinuation of study drug will be evaluated for dosing cohorts to inform dose escalation and expansion decisions, and support selection of a preliminary recommended phase 2 dose (RP2D).

Evaluation of hematology laboratory parameters
Screening through Day 1 through Day 35 (Cycle 1), and 30 days after discontinuation of study drug

Lab parameters will be evaluated for to assess the safety profile of the study drug, and support selection of a preliminary recommended phase 2 dose (RP2D).

Evaluation of clinical chemistry laboratory parameters
Screening through Day 1 through Day 35 (Cycle 1), and 30 days after discontinuation of study drug

Lab parameters will be evaluated for to assess the safety profile of the study drug, and support selection of a preliminary recommended phase 2 dose (RP2D).

Secondary Endpoints
Peak Plasma Concentration (Cmax)
Day 28 (predose, and 1 , 3 , 6 , and 24 hours post-dose) [end of Cycle 1]
Plasma predose or trough concentration (Ctau/Ctrough)
Day 28 (predose, and 1 , 3 , 6 , and 24 hours post-dose) [end of Cycle 1]
Time of maximum plasma concentration (Tmax)
Day 28 (predose, and 1 , 3 , 6 , and 24 hours post-dose) [end of Cycle 1]
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Part AEXPERIMENTALSequential dose escalation: 4 mg, 8 mg, 12 mg, and 18 mg
Part BEXPERIMENTALTwo parallel cohorts dosing at 2 levels selected based on Part A safety results
PAS-004 CapsulesEXPERIMENTALSequential dose escalation: 2 mg, 4 mg, 8 mg, 15 mg, 22 mg, 30 mg, 37 mg, and 45 mg
PAS-004 TabletsEXPERIMENTALA single cohort at the 4mg dose using tablet formulation of PAS-004
Interventions
NameTypeDescription
PAS-004 TabletsDRUGA mitogen-activated protein kinase/extracellular signal-regulated kinase kinase (MAPK/ERK kinase, or MEK) 1/2 inhibitor presented in 1m and 4mg strength tablets, intended for oral administration once daily.
PAS-004 CapsulesDRUGA mitogen-activated protein kinase/extracellular signal-regulated kinase kinase (MAPK/ERK kinase, or MEK) 1/2 inhibitor presented in 1 mg, 4mg, and 10 mg strength capsules, intended for oral administration once daily.
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Eligibility Criteria
Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: 1. Participant is capable of providing informed consent, which includes compliance with the requirements, prohibitions and restrictions listed in the informed consent form. 2. Participant has been informed both verbally and in writing about the objectives of the clinical study, ...

Countries:United StatesAustraliaSouth KoreaBulgariaRomania
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Competitive Landscape -Genetic Mutations 6 trials (matched to "RAS Mutation")
Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT06299839primaryCompletionDate: changed
LOWMay 26, 2026NCT06961565primaryCompletionDate: changed
LOWMay 24, 2026NCT06961565studyFirstPostDate: changed
LOWMay 24, 2026NCT06299839studyFirstPostDate: changed