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Daunorubicin

Phase 3

Acute Myeloid Leukemia | Small molecule | Oncology |Jazz Pharmaceuticals plc|Last Updated: Jul 17, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment882
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT03897127Study of Standard Intensive Chemotherapy Versus Intensive Chemotherapy With CPX-351 in Adult Patients With Newly Diagnosed AML and Intermediate- or Adverse GeneticsPHASE3 ACTIVE NOT_RECRUITING 882Sep 4, 2019Jun 1, 2027Jul 17, 202562 Austria, Germany
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Study Endpoints
Primary Endpoints
Overall survival (OS) in the restricted set of de novo patients
2 years
Secondary Endpoints
Overall survival (OS) in the extended set of patients
2 years
Event-free survival (EFS) with CRi considered as response to induction therapy in both, the restricted set of de novo patients and the extended set of patients
2 years
Event-free survival (EFS) with CRi considered as failure of induction therapy in the restricted set of de novo patients
2 years
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Standard armACTIVE_COMPARATOR -
Investigational armEXPERIMENTAL -
Interventions
NameTypeDescription
CytarabineDRUGInduction therapy: 200 mg/m2 i.v. (continuously) d1-7 Consolidation therapy: * Patients age 18-60 years o Intermediate-dose cytarabine 1500 mg/m2 i.v. q12h (3 hrs) d1-3 * Patients age \>60 years o Intermediate-dose cytarabine 1000 mg/m2 i.v. q12h (3 hrs) d1-3
DaunorubicinDRUGInduction therapy: 60 mg/m2 i.v. (1 hr) d1-3
CPX-351DRUGInduction 1: o CPX-351 44 mg/m2 daunorubicin / 100 mg/m2 cytarabine \[100 U/m²\] i.v. (90 min) d1,3,5 Induction 2: o CPX-351 44 mg/m2 daunorubicin / 100 mg/m2 cytarabine \[100 U/m²\] i.v. (90 min) d1,3 Consolidation therapy: o CPX-351 29 mg/m2 daunorubicin / 65 mg/m2 cytarabine \[65 U/m²\] i.v. (90 min) d1,3
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites62

Patient Inclusion Criteria: 1. Patients with newly diagnosed AML and intermediate- or adverse-risk genetics (according to 2017 ELN criteria \[Appendix B\]), including AML with myelodysplasia-related changes (AML-MRC) and therapy-related AML according to the World Health Organization (WHO) classific...

Countries:AustriaGermany
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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT03897127studyFirstPostDate: changed