Recent Updates
Recently added Catalysts

HMB-002

Phase 1

Von Willebrand Disease (VWD) | Small molecule | Hematology |Hemab Therapeutics Holdings, Inc.|Last Updated: Dec 9, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment108
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06754852A Study Assessing HMB-002 in Participants With Von Willebrand DiseasePHASE1 RECRUITING 108Feb 6, 2025Jul 1, 2027Dec 9, 20254 Australia, United Kingdom
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Incidence of Treatment emergent adverse events (TEAE)
up to Day 113
Secondary Endpoints
Pharmacokinetic Parameter: Maximum observed plasma concentration (Cmax)
Day 1 to Day 113
Pharmacokinetic Parameter: Area under the curve from time zero to last quantifiable concentration (AUClast)
Day 1 to Day 113
Pharmacokinetic Parameter: Area under the curve from time zero to extrapolated infinite time (AUCinf)
Day 1 to Day 113
Unlock Study Endpoints
Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Part A Single Ascending Dose DesignEXPERIMENTALA multicenter study to evaluate the safety, tolerability, PK, and PD effect of single dose HMB-002 in participants with Type 1 VWD.
Part B Multiple Dose AssessmentEXPERIMENTALA multicenter study to evaluate the safety, tolerability, PK, and PD effect of 3 repeat doses of HMB-002, as well as the preliminary prophylactic effects on bleeding events.
Interventions
NameTypeDescription
HMB-002 (Part A)DRUGHMB-002 will be administered subcutaneously. Part A will utilize sentinel dosing. The planned duration of study participants in Part A is approximately 12 weeks.
HMB-002 (Part B)DRUGHMB-002 will be administered subcutaneously. Part B dosing intervals will be determined following evaluation of Part A results. The planned duration of study participants in Part B will be approximately 21 weeks.
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — 64 Years
SexALL
Healthy VolunteersNo
Study Sites4

Inclusion Criteria: 1. Has the ability to provide informed consent to participate in the study, in accordance with applicable regulations. 2. Has an understanding, ability, and willingness to comply with study procedures and restrictions. 3. ≥18 and \<65 years. 4. Weight 50 to 110 kg, inclusive. 5....

Countries:AustraliaUnited Kingdom
Unlock Eligibility Criteria
Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT06754852primaryCompletionDate: changed
LOWMay 24, 2026NCT06754852studyFirstPostDate: changed