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Molidustat

Phase 3

Anemia | Small molecule | Hematology |Bayer AG|Last Updated: Jan 29, 2021

Success Probability

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Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLEDDMC
Total Trials8
Total Enrollment1,086

FDA Designations

No designations recorded

Clinical trial landscape

Molidustat · 10 trials · 3 indications

Phase 3 5Phase 2 3Phase 1 2
NCT03543657Maintenance Treatment of Renal Anemia in Dialysis SubjectsAnemia
COMPLETED229 Analytics
NCT03418168A Study of Molidustat for Treatment of Renal Anemia in Peritoneal Dialysis SubjectsAnemia
COMPLETED51 Analytics
NCT03351166A Study of Molidustat for Correction of Renal Anemia in Dialysis SubjectsAnemia
COMPLETED25 Analytics
NCT03350347A Study of Molidustat for Maintenance Treatment of Renal Anemia in Non-dialysis SubjectsAnemia
COMPLETED164 Analytics
NCT03350321A Study of Molidustat for Correction of Renal Anemia in Non-dialysis SubjectsAnemia
COMPLETED162 Analytics
PHASE3COMPLETED
Maintenance Treatment of Renal Anemia in Dialysis Subjects
AnemiaUnlock trial analytics
PHASE3COMPLETED
A Study of Molidustat for Treatment of Renal Anemia in Peritoneal Dialysis Subjects
AnemiaUnlock trial analytics
PHASE3COMPLETED
A Study of Molidustat for Correction of Renal Anemia in Dialysis Subjects
AnemiaUnlock trial analytics
PHASE3COMPLETED
A Study of Molidustat for Maintenance Treatment of Renal Anemia in Non-dialysis Subjects
AnemiaUnlock trial analytics
PHASE3COMPLETED
A Study of Molidustat for Correction of Renal Anemia in Non-dialysis Subjects
AnemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

The mean Hb level during the evaluation period
From week 33 to 36
The change in mean Hb level during the evaluation period from baseline
Baseline and week 33 to 36
Responder rate: proportion of responders among the subjects
Week 30 to 36

Responder is defined as meeting all of the following criteria: (i) Mean of the Hb levels in the target range (ii) ≥ 50% of the Hb levels in the target range (iii) No rescue treatment

Rate of rise in Hb (Hemoglobin) level (g/dL/week)
Up to 8 weeks
Mean Hb (Hemoglobin) level
From week 30 to 36
Change in hemoglobin level from baseline to the average during the evaluation period
Baseline and week 30 to 36
Change in local laboratory hemoglobin level from baseline
Baseline up to 36 months
Number of participants with serious adverse events (SAEs) and adjucated adverse events as a measure of safety and tolerability
Up to 36 months
Number of participants with liver function-related AEs including abnormal liver function tests and any hospitalization
Up to 36 months
Number of participants with serious adverse events as a measure of safety and tolerability
Up to 36 months
Change in local laboratory hemoglobin level from baseline to the average during the last 4 weeks treatment period
Baseline and weeks 14 to 17
Pharmacokinetics characterized by Cmax of Molidustat
Up to 96 hours post dose

Cmax: maximum drug concentration in plasma after single dose administration

Pharmacokinetics characterized by AUC of Molidustat
Up to 96 hours post dose

AUC: area under the plasma concentration vs time curve from zero to infinity

Pharmacokinetics characterized by Cmax,norm of Molidustat
Up to 96 hours post dose

Cmax,norm;maximum drug concentration in plasma after single dose administration divided by dose (milligrams) per kilogram body weight

Pharmacokinetics characterized by (AUCnorm) of Molidustat
Up to 96 hours post dose

AUCnorm; area under the plasma concentration vs time curve divided by dose per kg body weight

Number of participants with adverse events
Approximately 9 weeks
Blood pressure
Approximately 9 weeks

Systolic, diastolic, mean blood pressure

Heart rate
Approximately 9 weeks
Cmax
Pre-dose and up to 48 h post-dose

Maximum observed drug concentration in measured matrix after single dose administration

Cmax/D
Pre-dose and up to 48 h post-dose

Cmax divided by dose

AUC
Pre-dose and up to 48 h post-dose

Area under the concentration vs time curve from zero to infinity after single dose

AUC/D
Pre-dose and up to 48 h post-dose

AUC divided by dose

Heart rate over 1 min
Pre-dose and up to 24 h post-dose
Standing blood pressure procedure
Starting from 2 h post-dose and up to 4 h post-dose
Impedance cardiography
Pre-dose and up tp 8 h post-dose

Stroke volume, heart rate, cardiac index, cardiac output, and total peripheral resistance

Secondary Endpoints

Responder rate: proportion of responders among the subjects
From week 33 to 36
Proportion of subjects who meet each component of the response
From week 33 to 36
Hb level
Up to 52 weeks
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Molidustat groupEXPERIMENTALSubjects in the molidustat group will receive molidustat and darbepoetin alfa placebo.
Darbepoetin alfa groupACTIVE_COMPARATORSubjects in the darbepoetin alfa group will receive molidustat placebo and darbepoetin alfa.
Molidustat (BAY85-3934)EXPERIMENTALMolidustat group
Darbepoetin alfaACTIVE_COMPARATORDarbepoetin alfa group
BAY85-3934EXPERIMENTAL -
DarbepoetinACTIVE_COMPARATOR -
Epoetin alfa/betaACTIVE_COMPARATOR -
Molidustat (BAY 85-3934)(25mg)EXPERIMENTALStarting dose of 25 mg of BAY85-3934 as once-daily oral tablets. Regular titrations at dose control visits. Titration occuring every 4-weeks will be based on the subject's Hb response and tolerability of the prior dose. Total treatment time is 16 weeks. Planned doses include 15, 25, 50, 75, 100,150 and 200 mg once daily.
Molidustat (BAY 85-3934)(50mg)EXPERIMENTALStarting dose of 50 mg of BAY85-3934 as once-daily oral tablets. Regular titrations at dose control visits Titration occuring every 4-weeks will be based on the subject's Hb response and tolerability of the prior dose. Total treatment time is 16 weeks. Planned doses include 15, 25, 50, 75, 100,150 and 200 mg once daily.
Molidustat (BAY 85-3934) (75mg)EXPERIMENTALStarting dose of 75 mg of BAY85-3934 as once-daily oral tablets. Regular titrations at dose control visits Titration occuring every 4-weeks will be based on the subject's Hb response and tolerability of the prior dose. Total treatment time is 16 weeks. Planned doses include 15, 25, 50, 75, 100,150 and 200 mg once daily.,
Molidustat (BAY 85-3934) (150mg)EXPERIMENTALStarting dose of 150 mg of BAY85-3934 as once-daily oral tablets. Regular titrations at dose control visits Titration occuring every 4-weeks will be based on the subject's Hb response and tolerability of the prior dose. Total treatment time is 16 weeks. Planned doses include 15, 25, 50, 75, 100, 150 and 200 mg once daily
Arm 1EXPERIMENTALSingle oral dose of 75 mg molidustat (fasted) in subjects on hemodialysis (at start of hemodialysis and on a hemodialysis free day,respectively)
Arm 2EXPERIMENTALSingle oral dose of 75 mg molidustat (fasted) in subjects on peritoneal dialysis (after start of peritoneal dialysis intervall and, optionally, after the start of a peritoneal dialysis-free intervall,respectively)
Arm 3EXPERIMENTALSingle oral dose of 75 mg molidustat (fasted) in healthy subjects
Molidustat, 80 mgEXPERIMENTALSubjects received a single oral dose of 80 mg BAY 85-3934 in the first period and placebo in the second period, separated by a wash-out period of at least 1 week.
Molidustat, 120 mgEXPERIMENTALSubjects received a single oral dose of 120 mg BAY 85-3934 in the first period and placebo in the second period, separated by a wash-out period of at least 1 week.
Molidustat, 40 mgEXPERIMENTALSubjects received a single oral dose of 40 mg BAY 85-3934 in the first period and placebo in the second period, separated by a wash-out period of at least 1 week. This is an optional dose escalation step.
Molidustat, 160 mgEXPERIMENTALSubjects received a single oral dose of 160 mg BAY 85-3934 in the first period and placebo in the second period, separated by a wash-out period of at least 1 week. This is an optional dose escalation step.

Interventions

NameTypeDescription
Molidustat (BAY85-3934)DRUGStarting dose of molidustat will be titrated based on the subject's Hb (Hemoglobin) response. Administrated orally once daily (OD).
Darbepoetin alfaDRUGStarting dose of darbepoetin alfa will be titrated based on the subject's Hb (Hemoglobin) response. Administrated weekly or once every two weeks by intravenous injection.
Placebo of Molidustat (BAY85-3934)DRUGMatching placebo of Molidustat.
Placebo of Darbepoetin alfaDRUGMatching placebo of Darbepoetin alfa.
DarbepoetinBIOLOGICALDarbepoetin will be administered according to the local label and titrated at the scheduled dose by intravenous injection. Treatment will be for a minimum of 6 months to up to a maximum of 36 months.
Epoetin alfa/betaBIOLOGICALSubjects will continue with the same treatment they were receiving in the parent study (16208). Epoetin alfa / beta will be administered as intravenous (IV) or subcutaneous (SC) injections per individual subject regimen according to the local label. Dose assessments will be made every 4 (± 1) weeks. At the scheduled visits,dose may be titrated on an individualized basis taking into account the subject's Hb response and the tolerability of the previous dose.Total treatment time is up to 36 months.
Molidustat (BAY 85-3934)DRUGOral doses of BAY85-3934 will be available in multiples of 25,50,75 and 150 mg tablets
Molidustat(BAY85-3934)DRUGTwo single oral doses of 75 mg molidustat tablet in subjects on hemodialysis and peritoneal dialysis
PlaceboDRUGSingle oral dose of matching placebo will be given in each treatment arm
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Eligibility Criteria

Age Range20 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites53

Inclusion Criteria: * Subject with ESKD (end-stage kidney disease) on regular dialysis (including, hemodiafiltration, hemofiltration, hemodialysis, and other modalities except for peritoneal dialysis) weekly or more than weekly for at least 12 weeks prior to randomization * Body weight (after dialy...

Countries:JapanAustraliaBulgariaFranceGermanyHungaryIsraelItalyPolandRomaniaSouth KoreaSpainTurkey (Türkiye)United KingdomUnited States
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Frequently asked questions about Molidustat

What is Molidustat used for?

Molidustat is an investigational small molecule being developed for the treatment of anemia associated with chronic kidney disease and renal insufficiency. It is intended for patients with these conditions, including those on hemodialysis. The drug is currently in Phase 3 clinical development and has not been approved by regulatory authorities.

Who is developing Molidustat?

Molidustat is being developed by Bayer AG, a multinational pharmaceutical company. Bayer's stock is traded under the ticker symbol BAYRY on the OTC market. The company has conducted multiple clinical trials to evaluate the drug's safety and efficacy in patients with anemia related to chronic kidney disease.

What phase is Molidustat in?

Molidustat is in Phase 3 clinical development. It is an investigational drug, meaning it has not yet received regulatory approval. The drug has completed earlier phase trials, including Phase 1 and Phase 2 studies, and is being evaluated for the treatment of anemia associated with chronic kidney disease.

What clinical trials has Molidustat been in?

Molidustat has been studied in several clinical trials, including NCT01679587, a Phase 1 dose escalation study in patients with kidney disease, and NCT01975818, a Phase 2 trial comparing Molidustat to epoetin alfa/beta in hemodialysis patients with anemia. Other completed trials include NCT02055482 and NCT02064426, both long-term extension studies.

Is Molidustat the same as BAY85-3934?

Yes, Molidustat is also known as BAY85-3934. In clinical trial records, the drug is often referred to by this alternative name. Researchers and medical professionals may use either name when discussing the drug, which is being developed for anemia associated with chronic kidney disease.