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XTX501

Phase 1

Metastatic NSCLC - Non-Small Cell Lung Cancer | Small molecule | Oncology |Xilio Therapeutics, Inc.|Last Updated: Jul 7, 2026

Target and mechanism

Molecular targetPD-1
Target classImmune Checkpoint
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment140

FDA Designations

No designations recorded

Clinical trial landscape

XTX501 · 1 trial · 2 indications

Phase 1 1
NCT07688577XTX501 in Patients With Metastatic Non-Small Cell Lung Cancer and Advanced Solid TumorsMetastatic NSCLC - Non-Small Cell Lung Cancer
NOT YET_RECRUITING140 Analytics
PHASE1NOT YET_RECRUITING
XTX501 in Patients With Metastatic Non-Small Cell Lung Cancer and Advanced Solid Tumors
Metastatic NSCLC - Non-Small Cell Lung CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence of Dose Limiting Toxicities (DLTs) in Part 1A
Cycle 1 Day 1 up to just prior to the second dose of study drug (approximately 21 days)
Incidence of treatment-emergent adverse events (Phase 1 and Phase 2)
Up to Safety Follow Up Period (90 [+7] days after the last dose)
Incidence of serious adverse events (Phase 1 and Phase 2)
Up to Safety Follow Up Period (90 [+7] days after the last dose)
Incidence of significant change from baseline in clinical laboratory values (Phase 1 and Phase 2)
Up to Safety Follow Up Period (90 [+7] days after the last dose)
Investigator-assessed objective response rate (ORR) per RECIST v1.1 (Phase 2)
Up to Safety Follow Up Period (90 [+7] days after the last dose)

Secondary Endpoints

Investigator-assessed objective response rate (ORR) per RECIST v1.1 (Phase 1)
Up to Safety Follow Up Period (90 [+7] days after the last dose)
Investigator-assessed duration of response (DOR) per RECIST v1.1 (Phase 1 and Phase 2)
Up to Safety Follow Up Period (90 [+7] days after the last dose)
Investigator-assessed disease control rate (DCR) per RECIST v1.1 (Phase 2)
Up to Safety Follow Up Period (90 [+7] days after the last dose)
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Phase 1 - XTX501 Monotherapy Dose Escalation and BackfillEXPERIMENTALPart 1A will examine XTX501 monotherapy in a Bayesian Optimal Interval design to determine the maximum tolerated dose up to 10 dose regimens. Part 1B will further evaluate the safety and antitumor activity of XTX501 at dose regimens under consideration for the recommended Phase 2 dose(s).
Phase 2- XTX501 Monotherapy Dose Expansion in metastatic NSCLCEXPERIMENTALPhase 2 will further evaluate the efficacy of the selected recommended Phase 2 dose(s) in participants with metastatic NSCLC.

Interventions

NameTypeDescription
XTX501DRUGXTX501 monotherapy
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo

Inclusion Criteria: * Measurable disease at baseline per RECIST v1.1 * ECOG performance status of 0 or 1 * Adequate organ function * Metastatic NSCLC: * Must have histologically confirmed metastatic NSCLC. * Tumor must have been assessed for EGFR and ALK per local standard of practice; patient...

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Recent Changes (Last 90 Days)

LOWJul 7, 2026NCT07688577NEW_TRIAL: changed
LOWJul 7, 2026NCT07688577NEW_TRIAL: changed

Frequently asked questions about XTX501

What is XTX501 used for in metastatic NSCLC?

XTX501 is an investigational small molecule being studied for the treatment of metastatic non-small cell lung cancer (NSCLC) and advanced solid tumors. It is currently in Phase 1 clinical development and has not been approved by regulatory authorities.

What does XTX501 target?

XTX501 targets PD-1, an immune checkpoint protein. By targeting PD-1, the drug is designed to modulate the immune system's response against cancer cells. It is being evaluated in a Phase 1 clinical trial for metastatic NSCLC and advanced solid tumors.

Who is developing XTX501?

XTX501 is being developed by Xilio Therapeutics, Inc., a biopharmaceutical company. The company is conducting a Phase 1 clinical trial to evaluate the drug's safety and efficacy in patients with metastatic non-small cell lung cancer and advanced solid tumors.

What phase is XTX501 in?

XTX501 is in Phase 1 clinical development. It is an investigational drug and has not yet been approved by the FDA or other regulatory agencies. The ongoing Phase 1 trial is designed to assess the drug's safety, tolerability, and preliminary efficacy.

What clinical trials is XTX501 in?

XTX501 is being evaluated in a Phase 1 clinical trial with the identifier NCT07688577. This trial is studying the drug in patients with metastatic non-small cell lung cancer and advanced solid tumors. The trial is not yet recruiting and aims to enroll approximately 140 participants.

Is XTX501 the same as any other drug?

No alternative names for XTX501 have been disclosed. The drug is identified solely by its code name XTX501 in clinical trial registrations and is being developed by Xilio Therapeutics, Inc. for the treatment of metastatic non-small cell lung cancer and advanced solid tumors.