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AGEN2034

Phase 1

Advanced Cancer | Small molecule | Oncology |Agenus Inc.|Last Updated: Jul 30, 2025

Target and mechanism

Molecular targetPD-1
Target classProtein
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment211

FDA Designations

No designations recorded

Clinical trial landscape

AGEN2034 · 1 trial · 2 indications

Phase 1 1
NCT03104699A Study of AGEN2034 in Advanced Tumors and Cervical CancerAdvanced Cancer
COMPLETED211 Analytics
PHASE1COMPLETED
A Study of AGEN2034 in Advanced Tumors and Cervical Cancer
Advanced CancerUnlock trial analytics

Study Endpoints

Primary Endpoints

Phase 1: Number of Participants Experiencing Dose-limiting Toxicities (DLTs) for Balstilimab
21 days

A DLT was defined as any treatment-related toxicity that was National Cancer Institute Common Terminology Criteria for Adverse Event Grade ≥3, confirmed by the safety monitoring committee to be relevant for the study drug treatment, and that occurred during the first 3 weeks of balstilimab treatment in the dose escalation portion of the study (DLT evaluation period).

Phase 1: Number of Participants Experiencing Treatment-emergent Adverse Events (TEAEs)
Up to 3 years

An adverse event (AE) was any untoward medical occurrence in a participant or clinical investigation participant administered a pharmaceutical product, which did not necessarily have a causal relationship with the treatment. TEAEs were AEs with onset dates during the on-treatment period, or the worsening of an event during the on-treatment period. A summary of all Serious Adverse Events and Other Adverse Events (nonserious), regardless of causality, is located in the 'Reported Adverse Events' Section.

Phase 2: Objective Response Rate (ORR) as Determined by an Independent Endpoint Review Committee (IERC)
Up to 3 years

ORR was defined as percentage of participants with a best overall response (BOR) of complete response (CR) or partial response (PR), as determined by an IERC per Response Evaluation Criteria in Solid Tumors version 1.1 (RECIST 1.1). BOR was defined as the best response recorded from the start of the study treatment until the end of treatment. CR was defined as disappearance of all target lesions, and PR was defined as at least a 30% decrease in the sum of diameters of target lesions, taking as reference the baseline sum diameters.

Secondary Endpoints

Phase 1: Receptor Occupancy of Circulating T Cells
4 hours after the first dose (Cycle 1 Day 1) and immediately prior to the second dose (Cycle 2 Day 1) (2-3 weeks/cycle)
Phase 1: Maximum Observed Concentration (Cmax) of Balstilimab
Day 1 (Pre-dose up to 24 hours post dose) of Cycle 1 and Cycle 2 (2-3 weeks/cycle) (up to 3 weeks)
Phase 1: Area Under the Drug Concentration-time Curve From Time Zero to the Last Quantifiable Concentration (AUC0-last) of Balstilimab
Day 1 (Pre-dose up to 24 hours post dose) of Cycle 1 and Cycle 2 (2-3 weeks/cycle) (up to 3 weeks)
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
MonotherapyEXPERIMENTALDose of 3 mg/kg intravenous (IV) every 2 weeks for up to 24 months.

Interventions

NameTypeDescription
AGEN2034DRUGAnti-programmed cell death protein-1 (PD-1) Monoclonal Antibody
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Eligibility Criteria

Age Range18 Years to N/A
SexFEMALE
Healthy VolunteersNo
Study Sites44

Inclusion Criteria: 1. Voluntarily agree to participate by giving written informed consent. Participation in pharmacogenomics testing is optional. 2. Be ≥18 years of age. 3. Diagnosis and prior systemic treatment: 1. Phase 1: Have a histologically or cytologically confirmed diagnosis of a metas...

Countries:United StatesAustraliaBelgiumBrazilChileEstoniaFrancePolandSpain
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Competitive Landscape -Cancer 5 trials (matched to "Advanced Cancer")

Frequently asked questions about AGEN2034

What is AGEN2034 used for?

AGEN2034 is an investigational small molecule being developed for the treatment of advanced cancer, including cervical cancer. It is currently in Phase 1 clinical development and has not been approved by regulatory authorities.

What does AGEN2034 target?

AGEN2034 targets PD-1, a protein involved in immune regulation. By targeting PD-1, the drug is designed to modulate the immune system's response to cancer cells, though the exact mechanism of action is not fully detailed in available information.

Who makes AGEN2034?

AGEN2034 is being developed by Agenus Inc., a biopharmaceutical company. Agenus Inc. is publicly traded under the ticker symbol AGEN on the stock market.

What phase is AGEN2034 in?

AGEN2034 is in Phase 1 clinical development. It is an investigational drug, meaning it has not yet received regulatory approval and is still being studied for safety and efficacy in clinical trials.

What clinical trials is AGEN2034 in?

AGEN2034 has one completed clinical trial, identified as NCT03104699, titled "A Study of AGEN2034 in Advanced Tumors and Cervical Cancer." This Phase 1 trial enrolled 211 participants and was conducted across multiple countries, including the United States, Australia, and several European nations.