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VTX2735

Phase 2

Cryopyrin Associated Periodic Syndrome | Small molecule | Rare Disease |Ventyx Biosciences, Inc.|Last Updated: May 22, 2026

Target and mechanism

Molecular targetNLRP3
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment7

FDA Designations

No designations recorded

Clinical trial landscape

VTX2735 · 2 trials · 2 indications

Phase 2 2
NCT06836232An Open-Label Pilot Study of VTX2735 in Recurrent PericarditisRecurrent Pericarditis
RECRUITING50 Analytics
NCT05812781A Study to Evaluate VTX2735 in Patients With Cryopyrin-associated Periodic SyndromeCryopyrin Associated Periodic Syndrome
COMPLETED7 Analytics
PHASE2RECRUITING
An Open-Label Pilot Study of VTX2735 in Recurrent Pericarditis
Recurrent PericarditisUnlock trial analytics
PHASE2COMPLETED
A Study to Evaluate VTX2735 in Patients With Cryopyrin-associated Periodic Syndrome
Cryopyrin Associated Periodic SyndromeUnlock trial analytics

Study Endpoints

Primary Endpoints

Safety and tolerability of VTX2735
Day 1 of treatment period through study completion, up to 26 weeks

Incidence of adverse events (AEs), serious adverse events (SAEs), and AEs leading to study treatment discontinuation

Secondary Endpoints

Effect of VTX2735 on pericardial pain
Day 1 of treatment period to Week 6 of treatment period
Effect of VTX2735 on inflammation
Day 1 of treatment period to Week 6 of treatment period
Mean change in the mean key symptom score (KSS) derived from the Daily Health Assessment Form, Second Generation (DHAF2) from baseline
From Day 1 to completion of treatment with VTX2735, up to Day 28
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort AEXPERIMENTAL -
Cohort B Treatment Group B1EXPERIMENTAL -
Cohort B Treatment Group B2EXPERIMENTAL -
Cohort C Treatment Group C1EXPERIMENTAL -
Cohort C Treatment Group C2EXPERIMENTAL -
Cohort 1EXPERIMENTAL -
Cohort 2EXPERIMENTAL -

Interventions

NameTypeDescription
VTX2735DRUGDose A, Daily
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites18

Inclusion Criteria: * Participants are male or female ≥ 18 years up to ≤ 75 years of age. * Capable of giving signed informed consent and able to comply with the protocol * Previously had an index (first) episode of pericarditis which met the criteria for an acute pericarditis event * Ongoing sympt...

Countries:United StatesCanada
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Frequently asked questions about VTX2735

What is VTX2735 used for?

VTX2735 is an investigational small molecule being developed for recurrent pericarditis and cryopyrin associated periodic syndrome, both rare diseases. It is currently in Phase 2 clinical development and has not been approved by the FDA.

What does VTX2735 target?

VTX2735 targets NLRP3, acting as an inhibitor of this protein. By inhibiting NLRP3, the drug aims to modulate the inflammatory pathway involved in the conditions it is being studied for, including recurrent pericarditis and cryopyrin associated periodic syndrome.

Who makes VTX2735?

VTX2735 is being developed by Ventyx Biosciences, Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol VTYX. The company is conducting clinical trials to evaluate the drug's safety and efficacy in patients with rare inflammatory diseases.

What phase is VTX2735 in?

VTX2735 is in Phase 2 clinical development. It is an investigational drug, meaning it has not yet received regulatory approval. Clinical trials are ongoing to assess its potential as a treatment for recurrent pericarditis and cryopyrin associated periodic syndrome.

What clinical trials is VTX2735 in?

VTX2735 is being studied in two Phase 2 trials. NCT05812781, a completed study in patients with cryopyrin associated periodic syndrome, enrolled 7 participants in the United States. NCT06836232, an open-label pilot study in recurrent pericarditis, is currently recruiting up to 50 participants in the United States and Canada.

Is VTX2735 the same as any other drug?

No alternative names for VTX2735 have been disclosed. It is identified solely by its development code, VTX2735, and is being investigated by Ventyx Biosciences for the treatment of recurrent pericarditis and cryopyrin associated periodic syndrome.