Recent Updates
Recently added Catalysts

Telitacicept

Phase 3

Generalized Myasthenia Gravis | Monoclonal antibody | Neurology |Vor Biopharma Inc.|Last Updated: Aug 27, 2026

Target and mechanism

Molecular targetBLyS/APRIL
ModalityMonoclonal antibody

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment180

FDA Designations

No designations recorded

Clinical trial landscape

Telitacicept · 2 trials · 2 indications

Phase 3 2
NCT07404865Phase 3 Study of Telitacicept in Active Primary Sjögren's DiseasePrimary Sjogren's Disease
RECRUITING250 Analytics
NCT06456580A Study of Telitacicept for the Treatment of Generalized Myasthenia Gravis (UPSTREAM MG)Generalized Myasthenia Gravis
RECRUITING180 Analytics
PHASE3RECRUITING
Phase 3 Study of Telitacicept in Active Primary Sjögren's Disease
Primary Sjogren's DiseaseUnlock trial analytics
PHASE3RECRUITING
A Study of Telitacicept for the Treatment of Generalized Myasthenia Gravis (UPSTREAM MG)
Generalized Myasthenia GravisUnlock trial analytics

Study Endpoints

Primary Endpoints

To evaluate the efficacy of telitacicept versus placebo at Week 48 in the change from baseline in the EULAR Sjögren's Syndrome Disease Activity Index (ESSDAI) score at Week 48.
Week 48

Change from baseline in the EULAR Sjögren's Syndrome Disease Activity Index (ESSDAI) score at Week 48.

Change from baseline in Myasthenia Gravis-Activities of Daily Living (MG-ADL) score at Week 24
Week 24

The MG-ADL is an 8-item patient-reported outcome measure assessing MG symptoms and their effects on daily activities. Each item in the scale is scored on a 0 to 3 (0=normal, 3=severe disease) point scale. The total score is the sum of all individual item scores ranging from 0 to 24. Higher scores indicate more severe disability due to MG. A decrease from Baseline score indicates improvement.

Secondary Endpoints

To evaluate the efficacy of telitacicept versus placebo at Week 48 in the treatment of adult participants with pSD.
Week 48
To evaluate the efficacy of telitacicept versus placebo in improving glandular function during the trial.
Week 48
To evaluate the effect of telitacicept versus placebo in improving patient-reported outcomes (i.e., how participants feel and function) during the trial.
Week 48
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
TelitaciceptEXPERIMENTALTelitacicept
PlaceboPLACEBO_COMPARATORPlacebo

Interventions

NameTypeDescription
TelitaciceptBIOLOGICALSubcutaneous injection
PlaceboDRUGSubcutaneous injection
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites43

Inclusion Criteria: 1. Male or female aged 18 to 75 years of age (both inclusive) at screening 2. Participants must meet the 2016 American College of Rheumatology (ACR)/EULAR classification criteria for primary Sjogren's Syndrome at the time of screening. 3. ESSDAI ≥5 at screening (score calculated...

Countries:United StatesArgentinaAustraliaBelgiumBrazilCanadaChinaCzechiaFranceGeorgiaItalyJapanPolandSpain
Unlock Eligibility Criteria

Recent Changes (Last 90 Days)

LOWAug 27, 2026NCT07404865lastUpdatePostDate: changed
LOWAug 27, 2026NCT07404865lastUpdatePostDate: changed
LOWAug 11, 2026NCT07404865lastUpdatePostDate: changed
LOWAug 11, 2026NCT07404865lastUpdatePostDate: changed
LOWAug 11, 2026NCT07404865lastUpdatePostDate: changed
LOWJul 15, 2026NCT07404865lastUpdatePostDate: changed
LOWJul 15, 2026NCT07404865lastUpdatePostDate: changed
LOWJun 18, 2026NCT06456580lastUpdatePostDate: changed
LOWJun 18, 2026NCT06456580lastUpdatePostDate: changed
LOWJun 18, 2026NCT06456580lastUpdatePostDate: changed

Frequently asked questions about Telitacicept

What is Telitacicept used for?

Telitacicept is an investigational monoclonal antibody being studied for the treatment of generalized myasthenia gravis and primary Sjogren's disease. It is currently in Phase 3 clinical development for both indications.

What does Telitacicept target?

Telitacicept targets BLyS and APRIL, two proteins involved in B-cell survival and activity. By targeting these molecules, the drug aims to modulate the immune response in autoimmune conditions like generalized myasthenia gravis and primary Sjogren's disease.

Who is developing Telitacicept?

Telitacicept is being developed by Vor Biopharma Inc., a company traded under the ticker symbol VOR. The company is conducting Phase 3 trials for the drug in generalized myasthenia gravis and primary Sjogren's disease.

What phase is Telitacicept in?

Telitacicept is in Phase 3 clinical development. It is not yet approved by regulatory authorities and remains an investigational drug being studied for generalized myasthenia gravis and primary Sjogren's disease.

What clinical trials is Telitacicept in?

Telitacicept is being studied in two Phase 3 trials. NCT07404865 is a placebo-controlled study in primary Sjogren's disease with 250 participants in the United States. NCT06456580, known as UPSTREAM MG, is a placebo-controlled trial in generalized myasthenia gravis with 180 participants across multiple countries.

Is Telitacicept being studied in a randomized double-blind trial?

Yes, Telitacicept is being evaluated in randomized, double-blind, placebo-controlled Phase 3 trials. These trials are designed to assess the drug's efficacy and safety in patients with generalized myasthenia gravis and primary Sjogren's disease.