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Sargramostim

Phase 2

Covid19 | Small molecule | Infectious Disease |United Therapeutics Corporation|Last Updated: Feb 6, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment600
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04707664Sargramostim Use in COVID-19 to Recover Patient HealthPHASE2 COMPLETED 600Apr 27, 2021Jan 31, 2022Feb 6, 202337 United States, Argentina
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Study Endpoints
Primary Endpoints
Number of Participants With an Emergency Room Visit or Hospitalization, or Death by Day 28
28 days

Percentage of patients who experience any emergency room visit or hospitalization, or death

Secondary Endpoints
Disease Progression Based on NIAID Score
Day 28 and Day 60
Time to Disease Progression Based on NIAID Score
Day 28 and Day 60
Change From Baseline in Overall Symptom Scores
Day 7, 14, and 28
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Sargramostim ArmEXPERIMENTALDay 1 - 5: Sargramostim treatment in addition to standard of care for COVID-19
Placebo ArmPLACEBO_COMPARATORDay 1 - 5: Placebo treatment in addition to standard of care for COVID-19
Interventions
NameTypeDescription
SargramostimDRUGAll patients randomized to the sargramostim treatment arm will be treated with 250 mcg inhaled sargramostim administered via a vibrating mesh nebulizer once daily for 5 days.
PlaceboDRUGAll patients in the control arm will receive an equivalent volume of inhaled placebo diluent administered via a vibrating mesh nebulizer once daily for 5 days.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites37

Inclusion Criteria: 1. Patients with a positive laboratory diagnosis of SARS-CoV-2 infection by an antigen or a molecular test ≤5 days prior to randomization. The test should have been authorized by the relevant regulatory authority. 2. Have one or more of the following mild or moderate COVID-19 sy...

Countries:United StatesArgentina
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