Recent Updates
Recently added Catalysts

Sargramostim

Phase 2

Bilateral Breast Carcinoma | Monoclonal antibody | Oncology |United Therapeutics Corporation|Last Updated: Jun 30, 2026

Target and mechanism

Molecular targetCSF2RA, CSF2RB
Target classAgonist
ModalityMonoclonal antibody

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment280

FDA Designations

No designations recorded

Clinical trial landscape

Sargramostim · 3 trials · 16 indications

Phase 2 3
NCT04707664Sargramostim Use in COVID-19 to Recover Patient HealthCovid19
COMPLETED600 Analytics
NCT04411680Study of Sargramostim in Patients With COVID-19COVID-19
COMPLETED123 Analytics
NCT03012100Multi-epitope Folate Receptor Alpha Peptide Vaccine, GM-CSF, and Cyclophosphamide in Treating Patients With Triple Negative Breast CancerBilateral Breast Carcinoma
ACTIVE NOT_RECRUITING280 Analytics
PHASE2COMPLETED
Sargramostim Use in COVID-19 to Recover Patient Health
Covid19Unlock trial analytics
PHASE2COMPLETED
Study of Sargramostim in Patients With COVID-19
COVID-19Unlock trial analytics
PHASE2ACTIVE NOT_RECRUITING
Multi-epitope Folate Receptor Alpha Peptide Vaccine, GM-CSF, and Cyclophosphamide in Treating Patients With Triple Negative Breast Cancer
Bilateral Breast CarcinomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants With an Emergency Room Visit or Hospitalization, or Death by Day 28
28 days

Percentage of patients who experience any emergency room visit or hospitalization, or death

Change in Oxygenation Parameter of P(A-a)O2 Gradient by Day 6
1-6 days

The P(A-a)O2 gradient is a measure of how well the oxygen moves from the lungs into the bloodstream. Patients with a high gradient have less oxygen in the bloodstream.

Number of Patients Who Have Been Intubated by Day 14
1-14 days

Secondary Endpoints

Disease Progression Based on NIAID Score
Day 28 and Day 60
Time to Disease Progression Based on NIAID Score
Day 28 and Day 60
Change From Baseline in Overall Symptom Scores
Day 7, 14, and 28
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Sargramostim ArmEXPERIMENTALDay 1 - 5: Sargramostim treatment in addition to standard of care for COVID-19
Placebo ArmPLACEBO_COMPARATORDay 1 - 5: Placebo treatment in addition to standard of care for COVID-19
Control ArmACTIVE_COMPARATORStandard of care for COVID-19
Arm I (FRalpha peptide vaccine, sargramostim)EXPERIMENTALPatients receive cyclophosphamide PO BID on days 1-7 and 15-21 of cycle 1 only. Starting cycle 2, patients receive multi-epitope folate receptor alpha peptide vaccine with sargramostim ID on day 1. Treatment repeats every 28 days for cycles 2-7 and every 6 months for cycles 8-14 in the absence of disease progression or unacceptable toxicity.
Arm II (placebo, sargramostim)PLACEBO_COMPARATORPatients receive cyclophosphamide as in Arm I. Starting cycle 2, patients receive placebo vaccine with sargramostim ID on day 1. Treatment repeats every 28 days for cycles 2-7 and every 6 months for cycles 8-14 in the absence of disease progression or unacceptable toxicity.

Interventions

NameTypeDescription
SargramostimDRUGAll patients randomized to the sargramostim treatment arm will be treated with 250 mcg inhaled sargramostim administered via a vibrating mesh nebulizer once daily for 5 days.
PlaceboDRUGAll patients in the control arm will receive an equivalent volume of inhaled placebo diluent administered via a vibrating mesh nebulizer once daily for 5 days.
Standard of careDRUGStandard of care for COVID-19
CyclophosphamideDRUGGiven PO
Laboratory Biomarker AnalysisOTHERCorrelative studies
Multi-epitope Folate Receptor Alpha Peptide VaccineBIOLOGICALGiven ID
Placebo AdministrationOTHERGiven ID
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites37

Inclusion Criteria: 1. Patients with a positive laboratory diagnosis of SARS-CoV-2 infection by an antigen or a molecular test ≤5 days prior to randomization. The test should have been authorized by the relevant regulatory authority. 2. Have one or more of the following mild or moderate COVID-19 sy...

Countries:United StatesArgentina
Unlock Eligibility Criteria

Frequently asked questions about Sargramostim

What is Sargramostim used for?

Sargramostim is an investigational drug being studied for COVID-19 and breast cancer, including bilateral breast carcinoma and triple-negative breast cancer. It is in Phase 2 clinical development for these indications. Sargramostim is not approved by the FDA and remains under clinical investigation.

Who makes Sargramostim?

Sargramostim is being developed by United Therapeutics Corporation, a publicly traded company listed on the NASDAQ under the ticker symbol UTHR. The company is conducting clinical trials to evaluate the drug's safety and efficacy in patients with COVID-19 and certain breast cancers.

What phase is Sargramostim in?

Sargramostim is currently in Phase 2 clinical development. It is an investigational drug and has not received FDA approval. Clinical trials are ongoing or completed to assess its effectiveness in treating COVID-19 and breast cancer conditions.

What clinical trials is Sargramostim in?

Sargramostim is being studied in three Phase 2 clinical trials. NCT03012100 evaluates a vaccine with GM-CSF in triple-negative breast cancer. NCT04411680 and NCT04707664 study Sargramostim in COVID-19 patients. These trials are conducted in the United States and Argentina.

Is Sargramostim the same as GM-CSF?

Sargramostim is a monoclonal antibody, not GM-CSF itself. In clinical trials, it is studied alongside GM-CSF as a vaccine adjuvant. The drug is being tested for its potential role in treating COVID-19 and breast cancer, but it is distinct from GM-CSF.