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ARN-75039

Phase 1

Healthy Adult Participants | Small molecule | Other |United Therapeutics Corporation|Last Updated: May 1, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment94

FDA Designations

No designations recorded

Clinical trial landscape

ARN-75039 · 1 trial · 1 indication

Phase 1 1
NCT05735249A Study to Assess the Safety, Tolerability, and Pharmacokinetics of Oral ARN-75039 in Healthy Adult SubjectsHealthy Adult Participants
COMPLETED94 Analytics
PHASE1COMPLETED
A Study to Assess the Safety, Tolerability, and Pharmacokinetics of Oral ARN-75039 in Healthy Adult Subjects
Healthy Adult ParticipantsUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence of Treatment-Emergent Adverse Events (TEAEs)
From first dose through the End-of-Study (EOS) visit: Part 1 (SAD), through Day 15/EOS; Food-effect cohort, through the second treatment period and Day 29/EOS; Part 2 (MAD), from Day 1 through Day 39/EOS.

A treatment-emergent adverse event (TEAE) was defined as any adverse event that began or worsened after administration of the study drug (ARN-75039 or placebo) through the End-of-Study visit.

Incidence of Treatment-Emergent Serious Adverse Events (TESAEs)
From first dose through the End-of-Study (EOS) visit: Part 1 (SAD), through Day 15/EOS; Food-effect cohort, through the second treatment period and Day 29/EOS; Part 2 (MAD), from Day 1 through Day 39/EOS.

Number of participants with at least one treatment-emergent Serious adverse event (TESAE). A TESAE is any adverse event that starts or worsens after administration of study drug (ARN-75039 or placebo).

Secondary Endpoints

Part 1-SAD: Cmax
Day 1 predose and at 0.25 (15 minutes), 0.5 (30 minutes), 1, 2, 4, 6, 12, 24 (Day 2), 48 (Day 3), 72 (Day 4), 168 (Day 8), and 336 (Day 15/EOS) hours postdose.
Part 1-SAD: Tmax
Day 1 predose and at 0.25 (15 minutes), 0.5 (30 minutes), 1, 2, 4, 6, 12, 24 (Day 2), 48 (Day 3), 72 (Day 4), 168 (Day 8), and 336 (Day 15/EOS) hours postdose.
Part 1-SAD: Terminal Half-life
Derived from plasma samples collected from Day 1 predose through 336 hours (Day 15/EOS) postdose.
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
ARN-75039 oral capsulesEXPERIMENTALEscalating single or multiple doses of ARN-75039 oral capsules
Placebo (microcrystalline cellulose)PLACEBO_COMPARATORSpecified weight of placebo (microcrystalline cellulose) corresponding to the dose of ARN-75039 within the same cohort and encapsulating it in a HPMC capsule prior to dosing.

Interventions

NameTypeDescription
ARN-75039 oral capsulesDRUGactive oral study drug prepared and administered as oral capsules
PlaceboDRUGGiven at frequency and amounts matching ARN- 75039 dosing regimen
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Eligibility Criteria

Age Range18 Years to 55 Years
SexALL
Healthy VolunteersYes
Study Sites1

Inclusion Criteria: 1. Is male or female, age 18 to 55 years, inclusive, at Screening. 2. Body mass index (BMI) between 18.5 and 35 kg/m2, inclusive, at Screening. 3. In good general health, determined by no clinically significant findings in the opinion of the Investigator from medical history, ph...

Countries:United States
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Frequently asked questions about ARN-75039

What is ARN-75039 used for?

ARN-75039 is an investigational small molecule being studied for use in healthy adult participants. It is currently in Phase 1 clinical development, with a completed trial assessing its safety, tolerability, and pharmacokinetics in healthy subjects.

Who makes ARN-75039?

ARN-75039 is being developed by United Therapeutics Corporation, a biopharmaceutical company traded on the NASDAQ under the ticker symbol UTHR.

What phase is ARN-75039 in?

ARN-75039 is in Phase 1 clinical development. The single trial for this drug, NCT05735249, has been completed, and the drug remains investigational and is not approved for any use.

What clinical trials is ARN-75039 in?

ARN-75039 has one completed Phase 1 clinical trial, NCT05735249, titled "A Study to Assess the Safety, Tolerability, and Pharmacokinetics of Oral ARN-75039 in Healthy Adult Subjects." The trial enrolled 94 participants in the United States.

Is ARN-75039 FDA approved?

ARN-75039 is not FDA approved. It is an investigational drug that has completed a Phase 1 trial in healthy volunteers, but it is still in clinical development and has not been approved for any medical use.