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BAX 826

Phase 1

Hemophilia A | Monoclonal antibody | Hematology |Takeda Pharmaceutical Company Limited|Last Updated: May 25, 2021

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDBiomarker
Total Trials1
Total Enrollment40

FDA Designations

No designations recorded

Clinical trial landscape

BAX 826 · 1 trial · 1 indication

Phase 1 1
NCT02716194BAX 826 Dose-Escalation Safety StudyHemophilia A
COMPLETED40 Analytics
PHASE1COMPLETED
BAX 826 Dose-Escalation Safety Study
Hemophilia AUnlock trial analytics

Study Endpoints

Primary Endpoints

Serious AEs (SAEs) and Non-serious AEs Occurring After Infusion With BAX 826
Up to 6 weeks ± 4 days post infusion with BAX826.

Serious Adverse Events and non-serious Adverse Events the occurred after infusion with BAX 826.

Immediate Tolerability (Vital Signs and Clinical Laboratory Assessments)
Screening (Day -30 to -2); Advate Administration (Study Day 1) pre & postdose, and Day 4; Advate washout 96 hours to 4 weeks; BAX826 Administration Day 1 pre & postdose, Post BAX826 Day 4, 8, 14, and 23; and study termination visit, week 6 ± 4 days

Clinically significant results after treatment with investigational product that constitute an AE are counted. Vital signs include body temperature, respiratory rate, pulse rate, and blood pressure. Clinical laboratory results include: Hematology (hemoglobin, hematocrit, red blood cell count, white blood cell count with differential (i.e. basophils, eosinophils, lymphocytes, monocytes and neutrophils), international normalized ratio (INR), mean corpuscular volume (MCV), mean corpuscular hemoglobin concentration (MCHC), platelet count. Clinical Chemistry: sodium, potassium, chloride, bicarbonate, total protein, albumin, alanine aminotransferase (ALT), aspartate aminotransferase (AST), total bilirubin, alkaline phosphatase, gamma-glutamyltransferase (GGT), blood urea nitrogen (BUN), creatinine, glucose. Lipid panel: cholesterol, very-low-density lipoprotein (VLDL), low-density lipoprotein (LDL), high-density lipoprotein (HDL), triglycerides

Immunogenicity: Inhibitory Antibodies to Factor VIII (FVIII)
Screening visit (Day -30 to -2); Advate Administration (Study Day 1) predose; ADVATE wash out period 96 hours to 4 weeks; BAX826 Administration Day 1 predose, and Post BAX826 Day 8; and study termination visit, week 6 ± 4 days

Inhibition of FVIII activity by antibodies binding to FVIII were measured using the Nijmegen modification of the Bethesda inhibitor assay.

Immunogenicity: Binding Antibodies to PSA-FVIII (ie BAX 826)
Screening visit (Day -30 to -2); Advate Administration (Study Day 1) predose; ADVATE wash out period 96 hours to 4 weeks; BAX826 Administration Day 1 predose, and Post BAX826 Day 8; and study termination visit, week 6 ± 4 days

Binding antibodies to PSA FVIII (ie BAX 826) IgG and IgM

Immunogenicity: Binding Antibodies to Factor VIII (FVIII)
Screening visit (Day -30 to -2); Advate Administration (Study Day 1) predose; ADVATE wash out period 96 hours to 4 weeks; BAX826 Administration Day 1 predose, and Post BAX826 Day 8; and study termination visit, week 6 ± 4 days

Binding antibodies to FVIII IgG and IgM

Immunogenicity: Anti-polysialic Acid (Anti-PSA) Antibodies
Screening visit (Day -30 to -2); Advate Administration (Study Day 1) predose; ADVATE wash out period 96 hours to 4 weeks; BAX826 Administration Day 1 predose, and Post BAX826 Day 8; and study termination visit, week 6 ± 4 days

Binding antibodies to PSA (IgG and IgM)

Immunogenicity: Anti-Chinese Hamster Ovary (Anti-CHO) Antibodies
Screening visit (Day -30 to -2); Advate Administration (Study Day 1) predose; ADVATE wash out period 96 hours to 4 weeks; BAX826 Administration Day 1 predose, and Post BAX826 Day 8; and study termination visit, week 6 ± 4 days

Binding antibodies to CHO

Immunogenicity: Human Anti-murine Antibodies (HAMA)
Screening visit (Day -30 to -2); Advate Administration (Study Day 1) predose; ADVATE wash out period 96 hours to 4 weeks; BAX826 Administration Day 1 predose, and Post BAX826 Day 8; and study termination visit, week 6 ± 4 days

Binding antibodies HAMA (IgG)

Secondary Endpoints

Pharmacokinetics: Area Under the Concentration-time Curve From 0 to Infinity (AUC0-∞)
Pre-infusion within 30 minutes; and post-infusion at 15 and 30 minutes, and 1, 3, 6, 9, 12, 24, 32, 48, 56, and 72 hours for both BAX 826 and ADVATE. BAX 826 will also include post-infusion at 96, 120, 144, and 168 hours.
Pharmacokinetics: Terminal Half-life (t1/2)
Pre-infusion within 30 minutes; and post-infusion at 15 and 30 minutes, and 1, 3, 6, 9, 12, 24, 32, 48, 56, and 72 hours for both BAX 826 and ADVATE. BAX 826 will also include post-infusion at 96, 120, 144, and 168 hours.
Pharmacokinetics: Mean Residence Time (MRT)
Pre-infusion within 30 minutes; and post-infusion at 15 and 30 minutes, and 1, 3, 6, 9, 12, 24, 32, 48, 56, and 72 hours for both BAX 826 and ADVATE. BAX 826 will also include post-infusion at 96, 120, 144, and 168 hours.
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelCROSSOVER
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Cohort 1 - Low doseEXPERIMENTALThe study is comprised of 3 dose cohorts and two dose escalation steps \[Cohort 1: 10 evaluable participants; Cohort 2: 10 evaluable participants; Cohort 3: 10 evaluable participants\]. Participants will be recruited to the next dose level only after short-term safety has been reviewed and subject to approval by a Safety Review Committee at the preceding dose level.
Cohort 2 - Medium doseEXPERIMENTALThe study is comprised of 3 dose cohorts and two dose escalation steps \[Cohort 1: 10 evaluable participants; Cohort 2: 10 evaluable participants; Cohort 3: 10 evaluable participants\]. Participants will be recruited to the next dose level only after short-term safety has been reviewed and subject to approval by a Safety Review Committee at the preceding dose level.
Cohort 3 - High doseEXPERIMENTALThe study is comprised of 3 dose cohorts and two dose escalation steps \[Cohort 1: 10 evaluable participants; Cohort 2: 10 evaluable participants; Cohort 3: 10 evaluable participants\]. Participants will be recruited to the next dose level only after short-term safety has been reviewed and subject to approval by a Safety Review Committee at the preceding dose level.

Interventions

NameTypeDescription
BAX 826BIOLOGICAL -
Octocog alfaBIOLOGICAL -
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Eligibility Criteria

Age Range18 Years to 65 Years
SexMALE
Healthy VolunteersNo
Study Sites28

Inclusion Criteria: 1. Previously treated male participants aged 18 to 65 years (inclusive) at the time of screening 2. Diagnosis of severe hemophilia A (Factor VIII level \<1%) 3. Previously treated with FVIII concentrates for ≥150 documented Exposure Days (EDs) 4. Karnofsky performance score of ≥...

Countries:BulgariaGermanyHungaryItalyNetherlandsPolandRussiaSpainUnited Kingdom
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Frequently asked questions about BAX 826

What is BAX 826 used for?

BAX 826 is an investigational monoclonal antibody being developed for the treatment of Hemophilia A. It is currently in Phase 1 clinical development and has not been approved by regulatory authorities.

What does BAX 826 target?

BAX 826 is a monoclonal antibody, but its specific molecular target has not been disclosed in available information. The drug is being studied for its potential role in managing Hemophilia A.

Who makes BAX 826?

BAX 826 is being developed by Takeda Pharmaceutical Company Limited, which is publicly traded under the ticker symbol TAK.

What phase is BAX 826 in?

BAX 826 is in Phase 1 clinical development. It is an investigational drug and has not yet received FDA approval.

What clinical trials is BAX 826 in?

BAX 826 has one completed Phase 1 clinical trial, identified as NCT02716194, titled 'BAX 826 Dose-Escalation Safety Study.' The trial enrolled 40 male participants aged 18 years and older with Hemophilia A across multiple countries.

Is BAX 826 the same as any other drug?

No alternative names for BAX 826 have been disclosed. It is referred to solely as BAX 826 in available clinical trial information.