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BIVV020

Phase 1

Autoimmune Haemolytic Anaemia | Small molecule | Hematology |Sanofi|Last Updated: Sep 22, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment12
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04269551A Safety and Tolerability Study of BIVV020 in Adults With Cold Agglutinin DiseasePHASE1 COMPLETED 12Jun 15, 2020Jan 6, 2022Sep 22, 202510 United States, Germany +4
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Study Endpoints
Primary Endpoints
Assessment of adverse events (AEs)
Screening to Day 106

Number of participants with adverse events (AEs)

Secondary Endpoints
Mean change from baseline in bilirubin over time
Day 1 to Day 106
Mean change from baseline in hemoglobin over time
Day 1 to Day 106
Complement System Classical Pathway Levels as Measured by WIESLAB Assay
Day 1 to Day 106
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
BIVV020 IVEXPERIMENTALSingle administration dose 1, plus two optional doses of BIVV020 administered intravenously.
Interventions
NameTypeDescription
BIVV020DRUGPharmaceutical form:solution for injection Route of administration: intravenous
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites10

Inclusion criteria : * Male and/or female patients, ≥ 18 years of age with cold agglutinin disease as defined by: 1. Chronic hemolysis per Investigator's judgement, 2. Polyspecific direct antiglobulin test (DAT) positive, 3. Monospecific DAT strongly positive for C3d, 4. Cold agglutinin (C...

Countries:United StatesGermanyItalyNetherlandsNorwayUnited Kingdom
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