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Patidegib, 2%

Phase 3

Basal Cell Nevus Syndrome | Small molecule | Rare Disease |Sol-Gel Technologies Ltd.|Last Updated: Jul 3, 2024

Target and mechanism

Molecular targetSMO
Target classAntagonist
ModalitySmall molecule

Also known as Patidegib Topical Gel, Patidegib

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment174

FDA Designations

No designations recorded

Clinical trial landscape

Patidegib, 2% · 1 trial · 1 indication

Phase 3 1
NCT03703310Study of Patidegib Topical Gel, 2%, for the Reduction of Disease Burden of Persistently Developing Basal Cell Carcinomas (BCCs) in Subjects With Basal Cell Nevus Syndrome (Gorlin Syndrome)Basal Cell Nevus Syndrome
COMPLETED174 Analytics
PHASE3COMPLETED
Study of Patidegib Topical Gel, 2%, for the Reduction of Disease Burden of Persistently Developing Basal Cell Carcinomas (BCCs) in Subjects With Basal Cell Nevus Syndrome (Gorlin Syndrome)
Basal Cell Nevus SyndromeUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of New BCCs Per Participant
Month 12

Secondary Endpoints

Number of New Surgically Eligible BCCs (nSEBs) Per Participant
Month 12
Percentage of Participants Developing >=2 Facial New BCCs
Month 12
Percentage of Participants Developing >=1 Facial New BCCs
Month 12
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Patidegib Topical Gel, 2%,EXPERIMENTALParticipants will be randomized to receive Patidegib Topical Gel, 2%. The Patidegib Topical Gel, 2% will be dispensed to participants at each study visit and applied topically twice daily to the face.
Patidegib Topical Gel, VehiclePLACEBO_COMPARATORParticipants will be randomized to receive Vehicle. The Patidegib Topical Gel, Vehicle will be dispensed to participants at each study visit and applied topically twice daily to the face.

Interventions

NameTypeDescription
Patidegib Topical Gel, 2%DRUGPatidegib Topical Gel, 2%
Patidegib Topical Gel, VehicleDRUGPatidegib Topical Gel, Vehicle
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites49

Inclusion Criteria: 1. The participant must be age at least 18 years of age at the Screening Visit. 2. The participant must provide written informed consent prior to any study procedures. 3. The participant must meet diagnostic criteria for the basal cell nevus (Gorlin) syndrome including major cri...

Countries:United StatesBelgiumCanadaDenmarkFranceGermanyItalyNetherlandsSpainUnited Kingdom
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Frequently asked questions about Patidegib, 2%

What is Patidegib used for?

Patidegib is an investigational topical gel being studied for the treatment of Basal Cell Nevus Syndrome, also known as Gorlin Syndrome, a rare genetic condition characterized by the development of numerous basal cell carcinomas. It is intended to reduce the disease burden of persistently developing basal cell carcinomas in affected adults.

What does Patidegib target?

Patidegib targets the Hedgehog signaling pathway, as indicated by its classification as a -degib (Hedgehog) inhibitor. By modulating this pathway, the drug aims to address the underlying mechanism driving basal cell carcinoma formation in patients with Gorlin Syndrome.

Who makes Patidegib?

Patidegib is being developed by Sol-Gel Technologies Ltd., a biopharmaceutical company traded on the NASDAQ under the ticker symbol SLGL. The company is conducting clinical trials to evaluate the safety and efficacy of this topical gel formulation for Gorlin Syndrome.

What phase is Patidegib in?

Patidegib is currently in Phase 3 clinical development. It is an investigational drug and has not been approved by regulatory authorities. Two Phase 3 trials have been conducted or are ongoing to assess its effectiveness in reducing basal cell carcinoma burden in patients with Gorlin Syndrome.

What clinical trials is Patidegib in?

Patidegib has been evaluated in two Phase 3 clinical trials. The first, NCT03703310, was a completed study with 174 participants investigating the gel's effect on disease burden in Basal Cell Nevus Syndrome. The second, NCT06050122, is an active but not recruiting trial with 140 participants focusing on preventing facial basal cell carcinomas in Gorlin Syndrome.

Is Patidegib the same as Patidegib Topical Gel?

Yes, Patidegib and Patidegib Topical Gel refer to the same drug product. The topical gel formulation is the specific dosage form being studied in clinical trials for the treatment of Gorlin Syndrome, and both names are used interchangeably in research contexts.